RecruitingNCT04003363

The United Kingdom National Registry for Myotonic Dystrophy

The UK National Registry for Myotonic Dystrophy


Sponsor

Newcastle University

Enrollment

900 participants

Start Date

May 1, 2013

Study Type

OBSERVATIONAL

Conditions

Summary

Myotonic dystrophy (dystrophia myotonica - DM) exists in two forms, usually referred to as DM1 (type 1) and DM2 (type 2). Both conditions are genetic disorders but each affects a different gene. DM1 is the most common adult-onset muscular dystrophy, and is thought to affect at least 1 in 8,000 people worldwide. The aim is to facilitate a questionnaire based research study in order to better characterise and understand the disease in the UK. By maintaining a national registry this will help identify potential participants eligible for clinical trials in the future.


Eligibility

Inclusion Criteria1

  • All patients with a confirmed Myotonic Dystrophy diagnosis (or pending diagnosis) are eligible for inclusion. Diagnosis will be confirmed via genetic testing results

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Interventions

OTHERPatient Registry

Participants who have volunteered to participate will complete various questionnaires relating to their condition.


Locations(1)

John Walton Muscular Dystrophy Research Centre

Newcastle upon Tyne, United Kingdom

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NCT04003363


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