RecruitingNCT04199000

Clinical and Basic Investigations Into Congenital Disorders of Glycosylation


Sponsor

Icahn School of Medicine at Mount Sinai

Enrollment

500 participants

Start Date

Oct 8, 2019

Study Type

OBSERVATIONAL

Conditions

Summary

The purpose of this research is to study the natural history of congenital disorders of glycosylation and its causes and treatments.


Eligibility

Inclusion Criteria1

  • Individuals with a genetically, enzymatically, or molecularly confirmed diagnosis of CDG or NGLY1 deficiency

Exclusion Criteria1

  • None

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Locations(12)

Rady Children's Hospital

San Diego, California, United States

Children's Hospital of Colorado

Aurora, Colorado, United States

Mayo Clinic Florida

Jacksonville, Florida, United States

Tulane University School of Medicine

New Orleans, Louisiana, United States

Boston Children's Hospital

Boston, Massachusetts, United States

University of Minnesota

Minneapolis, Minnesota, United States

Mayo Clinic in Rochester

Rochester, Minnesota, United States

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States

Baylor College of Medicine

Houston, Texas, United States

Seattle Children's Hospital

Seattle, Washington, United States

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NCT04199000


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