RecruitingNCT04507997

Angelman Syndrome Natural History Study


Sponsor

Boston Children's Hospital

Enrollment

300 participants

Start Date

Aug 1, 2018

Study Type

OBSERVATIONAL

Conditions

Summary

The goal of this study is to conduct a prospective, longitudinal natural history study of children and adults with Angelman Syndrome using investigator-observed and parent-reported outcome measures to obtain data that will be useful for future clinical trials.


Eligibility

Inclusion Criteria1

  • Molecular diagnosis of Angelman syndrome

Exclusion Criteria1

  • Presence of another condition, unrelated to Angelman syndrome, that affects neurodevelopment

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Locations(11)

Cedars-Sinai Guerin Children's

Los Angeles, California, United States

Rady Children's Hospital, San Diego

San Diego, California, United States

Children's Hospital Colorado, Anschutz Medical Campus

Aurora, Colorado, United States

Emory University School of Medicine

Atlanta, Georgia, United States

Rush University Children's Hospital

Chicago, Illinois, United States

Boston Children's Hospital

Boston, Massachusetts, United States

The Carolina Institute for Developmental Disabilities

Carrboro, North Carolina, United States

Monroe Carell Jr. Children's Hospital at Vanderbilt

Nashville, Tennessee, United States

Alberta Children's Hospital

Calgary, Alberta, Canada

BC Children's Hospital

Vancouver, British Columbia, Canada

Children's Hospital of Eastern Ontario

Ottawa, Ontario, Canada

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NCT04507997


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