RecruitingPhase 4NCT04647227

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

Safety of SEVENFACT® for the Treatment of Bleeding Events in Patients With Hemophilia A or B With Inhibitors


Sponsor

American Thrombosis and Hemostasis Network

Enrollment

55 participants

Start Date

Jun 28, 2021

Study Type

INTERVENTIONAL

Conditions

Summary

Phase IV multi-center, US-centric, open-label, safety study enrolling participants with Hemophilia A or B with inhibitors, 12 years of age and older, who are either on long term prophylactic treatment (e.g., emicizumab) at risk of experiencing a breakthrough bleeding event (BE), or who are not on prophylactic treatment who may need to control a BE.


Eligibility

Min Age: 12 YearsMax Age: 100 Years

Inclusion Criteria6

  • Have a diagnosis of hemophilia A or B with inhibitors.
  • Be 12 years of age and older
  • Be capable of understanding and willing to comply with the conditions of the protocol or have a legal guardian who is capable of understanding and complying with the conditions of the protocol
  • Have read, understood, and documented written informed consent/assent
  • Be able to provide medical evidence through prior medical history of previous inhibitor levels
  • Be willing and able to use the ATHN mobile application or a paper diary to document BEs and medication usage

Exclusion Criteria9

  • Have a disorder of hemostasis in addition to Hemophilia A or B
  • Have a known or suspected intolerance or hypersensitivity to SEVENFACT® or its ingredients
  • Have a known allergy or hypersensitivity to rabbits or rabbit proteins
  • Are receiving prophylactic treatment for bleeding with a drug or biologic that is not approved for this use by the FDA
  • Have had implantation of an investigational medical device within the prior 6 months
  • Have received an investigational drug within 30 days of the baseline visit
  • Have an elective surgical procedure planned during the duration of their participation in the study*
  • Have any life-threatening disease, or other disease or condition which, in the investigator's judgment, could pose a potential hazard to the patient or interfere with study participation or study outcome (e.g., a history of non responsiveness to bypassing products or thromboembolic disease)
  • Should a participant require an unplanned surgery, the participant will not be withdrawn from the study unless the investigator deems it necessary. Instead, the participant will receive standard of care treatment as determined by the attending physician. If the participant is not withdrawn from the study, the participant's participation in the study will be paused until the investigator feels it is safe for them to continue.

Interested in this trial?

Get notified about updates and connect with the research team.

Interventions

DRUGcoagulation factor VIIa [recombinant]-jncw

a transgenically produced, activated, recombinant, human factor VII (rhFVIIa) protein with the brand name of SEVENFACT®. This protein is a clotting factor in the coagulation cascade that is produced in and purified from the milk of transgenic rabbits. SEVENFACT is approved for the treatment and control of bleeding episodes occurring in adults and adolescents (12 years of age and older) with hemophilia A or B with inhibitors.


Locations(21)

Arizona Hemophilia and Thrombosis Center at Phoenix Children's Hospital

Phoenix, Arizona, United States

Arkansas Center for Bleeding Disorders

Little Rock, Arkansas, United States

Orthopaedic Institute for Children

Los Angeles, California, United States

University of California at Davis UC Davis Hemostasis and Thrombosis Center

Sacramento, California, United States

Children's National Hemophilia Center

Washington D.C., District of Columbia, United States

Arnold Palmer Hospital for Children - The Haley Center for Children's Cancer and Blood Disorders

Orlando, Florida, United States

Hemophilia of Georgia Center for Bleeding and Clotting Disorders of Emory, Adult Division

Atlanta, Georgia, United States

Willett Children's Hospital at Memorial University Medical Center

Savannah, Georgia, United States

Massachusetts General Hospital Comprehensive Hemophilia and Thrombosis Treatment Center

Boston, Massachusetts, United States

Children's Hospital of Michigan

Detroit, Michigan, United States

Henry Ford Health System

Detroit, Michigan, United States

MSU Center for Bleeding and Clotting Disorders

Lansing, Michigan, United States

Center for Bleeding and Clotting Disorders, University of Minnesota

Minneapolis, Minnesota, United States

Mayo Comprehensive Hemophilia Center

Rochester, Minnesota, United States

Kansas City Regional Hemophilia Center

Kansas City, Missouri, United States

Northwell Health, Long Island Jewish

New Hyde Park, New York, United States

Brody School of Medicine at East Carolina University

Greenville, North Carolina, United States

University Hospitals Health System Cleveland

Cleveland, Ohio, United States

Oklahoma Center for Bleeding and Clotting Disorders

Oklahoma City, Oklahoma, United States

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Gulf States Hemophilia and Thrombophilia Center-University of Texas Health Science Center @Houston

Houston, Texas, United States

View Full Details on ClinicalTrials.gov

For the most up-to-date information, visit the official listing.

Visit

NCT04647227


Related Trials