RecruitingPhase 2NCT04655118

Study of TL-895 in Subjects With Myelofibrosis or Indolent Systemic Mastocytosis

A Phase 2 Multicenter Study of TL-895 in Subjects With Relapsed/Refractory Myelofibrosis, Janus Kinase Inhibitor Intolerant Myelofibrosis, Janus Kinase Inhibitor Treatment Ineligible Myelofibrosis, or Indolent Systemic Mastocytosis


Sponsor

Telios Pharma, Inc.

Enrollment

121 participants

Start Date

Oct 22, 2020

Study Type

INTERVENTIONAL

Conditions

Summary

This study evaluates TL-895, a potent, orally-available and highly selective irreversible tyrosine kinase inhibitor for the treatment of Myelofibrosis (Cohorts 1-3) or Indolent Systemic Mastocytosis (Cohort 5). Participants must be diagnosed with Myelofibrosis and be relapsed/refractory (e.g., having failed prior therapy), intolerant, or ineligible to receive JAKi treatment, or be diagnosed with Indolent Systemic Mastocytosis.


Eligibility

Min Age: 18 Years

Inclusion Criteria10

  • Cohorts 1-3
  • Adults ≥18 years of age
  • Confirmed diagnosis of PMF, post-PV MF, or post-ET MF, as assessed by treating physician according to the World Health Organization (WHO) criteria
  • Eastern Cooperative Oncology Group (ECOG) performance status of ≤2
  • Adequate hematologic, hepatic, and renal functions
  • MF symptoms as defined by having at least 2 symptoms with an average baseline (Day -7 to Day -1) score of at least 1 for each of the 2 symptoms per MFSAF v4.0
  • Cohort 3 only: Ineligibility for JAKi treatment with a platelet count of ≥ 25 and < 50 x 10\^9/L
  • Adults ≥18 years of age
  • Confirmed diagnosis of ISM as defined by WHO diagnostic criteria based on review of bone marrow biopsy pathology report results
  • Subject must have moderate-to-severe symptoms

Exclusion Criteria7

  • Prior treatment with any BTK or BMX inhibitors
  • Prior treatment with JAKi within 28 days prior to study treatment
  • Prior splenectomy or splenic irradiation within 24 weeks prior to first dose of study treatment
  • Cohort 5
  • Prior treatment with any BTK or BMX inhibitors
  • Prior treatment with Avapritinib, bezuclastinib, or BLU-263/elenestinib
  • Diagnosis with another myeloproliferative disorder

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Interventions

DRUGTL-895

TL-895 is an experimental tyrosine kinase inhibitor drug taken by mouth.

DRUGPlacebo

Placebo to match TL-895


Locations(52)

University of Colorado - Aurora Cancer Center

Aurora, Colorado, United States

Mayo Clinic - Rochester

Rochester, Minnesota, United States

Gabrail Cancer Center

Canton, Ohio, United States

University of Cincinnati (UC) Physicians Company, LLC

Cincinnati, Ohio, United States

Ohio State University

Columbus, Ohio, United States

University of Texas, MD Anderson Cancer Center

Houston, Texas, United States

Border Medical Oncology

East Albury, Australia

Southern Oncology Specialists

Kogarah, Australia

Royal Perth Hospital

Perth, Australia

St Vincent's Hospital Sydney

Sydney, Australia

Chu De Liège

Liège, Belgium

Cliniques Universitaires Saint-Luc

Woluwe-Saint-Lambert, Belgium

Instituto de Estudos e Pesquisas Sao Lucas - IEP - Sao Lucas

São Paulo, Brazil

University Hospital "St Ivan Rilski"

Sofia, Bulgaria

Military Medical Academy

Sofia, Bulgaria

CH Le Mans

Le Mans, France

CHU de Nantes - Hôtel-Dieu

Nantes, France

CHU de Nice - Hopital L' Archet II

Nice, France

Universitaetsklinikum Carl Gustav Carus Dresden

Dresden, Germany

Marien Hospital Duesseldorf

Düsseldorf, Germany

Klinik fur Innere Medizin IV - Hamatologie/Onkologie, Universitatsklinikum Hall

Halle, Germany

Universitaetsklinikum Jena

Jena, Germany

Praxisklinik fur Hamatologie und Onkologie

Koblenz, Germany

Debreceni Egyetem Klinikai Kozpont

Debrecen, Hungary

Markhot Ferenc Oktatokorhaz es Rendelointezet

Eger, Hungary

Szabolcs-Szatmár-Bereg Megyei Önkormányzat Jósa András Oktatókórház Megyei-Városi Tüdőgondozó Intézete

Nyíregyháza, Hungary

Fejer Megyei Szent Gyorgy Egyetemi Oktato Korhaz

Székesfehérvár, Hungary

Azienda Ospedaliero Universitaria Policlinico G. Rodolico-San Marco - Presidio Ospedaliero G. Rodolico

Catania, Italy

Istituto Romagnolo per lo Studio dei Tumori Dino Amadori

Meldola, Italy

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano

Milan, Italy

ASST Grande Ospedale Metropolitano Niguarda

Milan, Italy

Azienda Ospedaliero Universitaria Maggiore Della Carita'

Novara, Italy

Azienda Ospedaliera di Perugia-Ospedale S. Maria della Misericordia

Perugia, Italy

AUSL della Romagna-Ospedale S.Maria delle Croci

Ravenna, Italy

Grande Ospedale Metropolitano Bianchi Melacrino Morelli

Reggio Calabria, Italy

Azienda Ospedaliero Universitaria Policlinico Umberto I

Roma, Italy

Szpital Uniwersytecki Nr 2 im. Dr Jana Biziela w Bydgoszczy, Klinika Hematologi

Bydgoszcz, Poland

Uniwersyteckie Centrum Kliniczne, Klinika Hematologii i Transplantologii

Gdansk, Poland

Klinika Hematologii Collegium Medicum Uniwersytetu Jagiellonskiego

Krakow, Poland

Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wroclawiu, Klinika Hematologii, Nowotworów Krwi i Transplantacji Szpiku

Wroclaw, Poland

Kyungpook National University Hospital

Daegu, South Korea

Seoul National University Hospital

Seoul, South Korea

Seoul St. Mary's Hospital, The Catholic University of Korea

Seoul, South Korea

Institut Catala d'Oncologia - L'Hospitalet

Barcelona, Spain

Hospital Germans Trias i Pujol

Barcelona, Spain

Hospital Universitario 12 de Octubre

Madrid, Spain

Salamanca University Hospital

Salamanca, Spain

Hospital Quirónsalud Zaragoza

Zaragoza, Spain

Kaohsiung Medical University Chung-Ho Memorial Hospital (KMUH)

Kaohsiung City, Taiwan

Chang Gung Memorial Hospital - Kaohsiung Branch

Kaohsiung City, Taiwan

China Medical University Hospital

Taichung, Taiwan

National Taiwan University Hospital

Taipei, Taiwan

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NCT04655118


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