RecruitingNCT04883905

ELEVATE, a Registry of Patients With Acute Hepatic Porphyria (AHP)

ELEVATE, a Global Observational Longitudinal Prospective Registry of Patients With Acute Hepatic Porphyria (AHP)


Sponsor

Alnylam Pharmaceuticals

Enrollment

150 participants

Start Date

Apr 26, 2021

Study Type

OBSERVATIONAL

Conditions

Summary

This global patient registry is being conducted to characterize the natural history and real-world clinical management of patients with AHP, and to further characterize the real-world safety and effectiveness of givosiran and other approved AHP therapies.


Eligibility

Min Age: 12 Years

Inclusion Criteria1

  • Documented diagnosis of AHP, per physician's determination

Exclusion Criteria1

  • Currently enrolled in a clinical trial for any investigational agent

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Locations(30)

Clinical Trial Site

Birmingham, Alabama, United States

Clinical Trial Site

Gilbert, Arizona, United States

Clinical Trial Site

San Francisco, California, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Minneapolis, Minnesota, United States

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New York, New York, United States

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Winston-Salem, North Carolina, United States

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Oklahoma City, Oklahoma, United States

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Philadelphia, Pennsylvania, United States

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Galveston, Texas, United States

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Salt Lake City, Utah, United States

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Seattle, Washington, United States

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Brussels, Belgium

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Leuven, Belgium

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Bordeaux, France

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Paris, France

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Toulouse, France

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Berlin, Germany

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Chemnitz, Germany

Clinical Trial Site

Würzburg, Germany

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Milan, Italy

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Modena, Italy

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Madrid, Spain

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Stockholm, Sweden

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Zurich, Switzerland

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Taichung, Taiwan

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Taipei, Taiwan

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Cardiff, United Kingdom

Clinical Trial Site

London, United Kingdom

View Full Details on ClinicalTrials.gov

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NCT04883905