RecruitingNCT04883905

ELEVATE, a Registry of Patients With Acute Hepatic Porphyria (AHP)

ELEVATE, a Global Observational Longitudinal Prospective Registry of Patients With Acute Hepatic Porphyria (AHP)


Sponsor

Alnylam Pharmaceuticals

Enrollment

150 participants

Start Date

Apr 26, 2021

Study Type

OBSERVATIONAL

Conditions

Summary

This global patient registry is being conducted to characterize the natural history and real-world clinical management of patients with AHP, and to further characterize the real-world safety and effectiveness of givosiran and other approved AHP therapies.


Eligibility

Min Age: 12 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a new treatment for people with acute hepatic porphyria. The study is currently recruiting participants at 30 locations. People eligible for this study include aged 12 Years and older.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Locations(30)

Clinical Trial Site

Birmingham, Alabama, United States

Clinical Trial Site

Gilbert, Arizona, United States

Clinical Trial Site

San Francisco, California, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

Clinical Trial Site

Minneapolis, Minnesota, United States

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New York, New York, United States

Clinical Trial Site

Winston-Salem, North Carolina, United States

Clinical Trial Site

Oklahoma City, Oklahoma, United States

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Philadelphia, Pennsylvania, United States

Clinical Trial Site

Galveston, Texas, United States

Clinical Trial Site

Salt Lake City, Utah, United States

Clinical Trial Site

Seattle, Washington, United States

Clinical Trial Site

Brussels, Belgium

Clinical Trial Site

Leuven, Belgium

Clinical Trial Site

Bordeaux, France

Clinical Trial Site

Paris, France

Clinical Trial Site

Toulouse, France

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Berlin, Germany

Clinical Trial Site

Chemnitz, Germany

Clinical Trial Site

Würzburg, Germany

Clinical Trial Site

Milan, Italy

Clinical Trial Site

Modena, Italy

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Madrid, Spain

Clinical Trial Site

Stockholm, Sweden

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Zurich, Switzerland

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Taichung, Taiwan

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Taipei, Taiwan

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Cardiff, United Kingdom

Clinical Trial Site

London, United Kingdom

View Full Details on ClinicalTrials.gov

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NCT04883905