RecruitingPhase 2NCT05070845

Safety and Efficacy Study of PF-06835375 in Primary Immune Thrombocytopenia

AN INTERVENTIONAL PHASE 2, OPEN-LABEL, MULTI-CENTER STUDY TO EVALUATE SAFETY AND EFFICACY OF PF-06835375 IN ADULT PARTICIPANTS WITH MODERATE TO SEVERE PRIMARY IMMUNE THROMBOCYTOPENIA


Sponsor

Pfizer

Enrollment

91 participants

Start Date

Feb 2, 2022

Study Type

INTERVENTIONAL

Summary

This is a Phase 2, open-label, multicenter, multiple subcutaneous injection, safety and efficacy study of PF-06835375 in adult participants with primary immune thrombocytopenia (ITP). This study will focus on participants with persistent (\>3 months and ≤12 months), or chronic (\>12 months) ITP


Eligibility

Min Age: 18 YearsMax Age: 70 Years

Inclusion Criteria1

  • Diagnosis of Primary ITP. Ongoing ITP (platelet counts <50 x 109/L) \[No severe bleeding within 1 month or during screening\] AND Persistent ITP (3 to 12 months) or Chronic ITP >12 months

Exclusion Criteria2

  • Bleeding event according to the WHO grading scale ≥2 occurring ≤4 weeks prior to screen OR a current bleeding event that, in the opinion of the investigator, requires treatment with standard of care therapy OR require blood or blood products during screening
  • Splenectomy within 3 months of randomization or planned during the study duration.

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Interventions

BIOLOGICALPF-06835375

CXCR5 inhibitor


Locations(31)

East Carolina University

Greenville, North Carolina, United States

Liverpool Hospital

Liverpool, New South Wales, Australia

South West Radiology

Liverpool, New South Wales, Australia

Slade Pharmacy

Mount Kuring-Gai, New South Wales, Australia

Calvary Mater Newcastle

Waratah, New South Wales, Australia

Flinders Medical Centre

Bedford Park, South Australia, Australia

ICON Cancer Centre - Kurralta Park

Kurralta Park, South Australia, Australia

The Alfred Hospital

Melbourne, Victoria, Australia

Royal Perth Hospital

Perth, Western Australia, Australia

Unity Health Toronto, St. Michael's Hospital

Toronto, Ontario, Canada

McGill University Health Centre

Montreal, Quebec, Canada

Fakultni nemocnice Hradec Kralove

Hradec Králové, Czechia

Fakultni nemocnice Ostrava

Ostrava - Poruba, Czechia

Fakultni nemocnice Kralovske Vinohrady

Prague, Czechia

Vseobecna fakultni nemocnice v Praze

Prague, Czechia

Pécsi Tudományegyetem Klinikai Központ

Pécs, Baranya, Hungary

Somogy Megyei Kaposi Mór Oktató Kórház

Kaposvár, Somogy County, Hungary

Semmelweis University

Budapest, Hungary

Petz Aladár Egyetemi Oktató Kórház

Győr, Hungary

Tolna Varmegyei Balassa Janos Korhaz

Szekszárd, Hungary

Komárom-Esztergom Vármegyei Szent Borbála Kórház

Tatabánya, Hungary

AIDPORT Sp. z o.o.

Skórzewo, Greater Poland Voivodeship, Poland

InterHem

Bialystok, Poland

Klinika Hematologii i Transplantologii Uniwersyteckie Centrum Kliniczne

Gdansk, Poland

Pratia Onkologia Katowice

Katowice, Poland

Uniwersytecki Szpital Kliniczny w Poznaniu

Poznan, Poland

Uniwersytecki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wroclawiu

Wroclaw, Poland

Addenbrooke's Hospital

Cambridge, Cambridgeshire, United Kingdom

Derriford Hospital

Plymouth, Devon, United Kingdom

The Royal Cornwall Hospital

Truro, England, United Kingdom

Hammersmith Hospital

London, United Kingdom

View Full Details on ClinicalTrials.gov

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NCT05070845