RecruitingPhase 3NCT05303519

SIGMA (Safusidenib in IDH1 Mutant Glioma Maintenance)

A Phase 3, Multicenter, Clinical Study to Evaluate the Efficacy and Safety of Safusidenib Erbumine in Participants With Isocitrate Dehydrogenase 1 (IDH1)-Mutant Glioma


Sponsor

Nuvation Bio Inc.

Enrollment

365 participants

Start Date

Jun 5, 2023

Study Type

INTERVENTIONAL

Conditions

Summary

This is a 3-part study. The purpose of Part 1 of the study is to evaluate the efficacy, safety, and pharmacokinetic (PK) characteristics of safusidenib in participants with recurrent/progressive IDH1-mutant World Health Organization (WHO) Grade 2 or Grade 3 glioma. The purpose of Part 2 will be to evaluate the efficacy of maintenance safusidenib treatment versus placebo in IDH1-mutant Grade 2 or Grade 3 astrocytoma with high-risk features or IDH1-mutant Grade 4 astrocytoma, following standard-of-care radiation or chemoradiation and adjuvant temozolomide. Part 2 will be randomized, double-blind, and placebo-controlled. The purpose of Part 3 will be to evaluate the efficacy of safusidenib in participants with residual or recurrent IDH1-mutant Grade 3 oligodendroglioma who have received surgery as their only treatment. Part 3 will be an open-label single-arm cohort and will enroll participants concurrently with Part 2.


Eligibility

Min Age: 18 Years

Plain Language Summary

Simplified for easier understanding

This trial (SIGMA) tests a drug called safusidenib in people with a type of brain tumor called IDH1-mutant glioma (grade 2 or 3). IDH1 is a gene mutation found in certain slow-growing brain tumors, and this drug is designed to specifically block the mutated protein. **You may be eligible if...** - You are 18 or older with a confirmed grade 2 or grade 3 glioma that has the IDH1 R132H or R132C mutation - Your tumor has recurred or is progressing after prior treatment - Your mutation has been confirmed by a certified lab test **You may NOT be eligible if...** - You do not have a confirmed IDH1 mutation - Your tumor is grade 4 (glioblastoma) - You have not had prior treatment - You have other serious medical conditions preventing participation Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGsafusidenib

safusidenib administered continuously as dosed single agent orally on Days 1 to 28 of a 28-day cycle. Subjects may continue treatment with agent safusidenib until disease progression or development of other unacceptable toxicity.

DRUGPlacebo

Placebo administered continuously as dosed single agent orally on Days 1 to 28 of a 28-day cycle. Subjects may continue treatment with placebo until disease progression or another reason for discontinuation occurs.


Locations(45)

University of Alabama

Birmingham, Alabama, United States

Mayo Clinic - Arizona

Phoenix, Arizona, United States

St. Joseph's Hospital and Medical Center

Phoenix, Arizona, United States

University of California, Los Angeles

Los Angeles, California, United States

Hoag Memorial Hospital Presbyterian

Newport Beach, California, United States

Stanford University

Palo Alto, California, United States

University of California

San Francisco, California, United States

University of Colorado Health Cancer Care

Aurora, Colorado, United States

Yale University

New Haven, Connecticut, United States

University of Florida Health

Gainesville, Florida, United States

Mayo Clinic - Florida

Jacksonville, Florida, United States

University of Miami Health

Miami, Florida, United States

Orlando Health Cancer Institute

Orlando, Florida, United States

University of Kansas Medical Center

Kansas City, Kansas, United States

Massachusetts General Hospital

Boston, Massachusetts, United States

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Henry Ford Hospital

Detroit, Michigan, United States

Mayo Clinic - Rochester

Rochester, Minnesota, United States

Washington University

St Louis, Missouri, United States

Rutgers Cancer Institute

New Brunswick, New Jersey, United States

NYU Langone Health

New York, New York, United States

Columbia University Medical Center

New York, New York, United States

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Duke Cancer Institute

Durham, North Carolina, United States

Cleveland Clinic

Cleveland, Ohio, United States

University of Texas Southwestern Medical Center

Dallas, Texas, United States

MD Anderson Cancer Center

Houston, Texas, United States

Huntsman Cancer Insititute, University of Utah

Salt Lake City, Utah, United States

UVA Health, Emily Couric Clinical Cancer Cente

Charlottesville, Virginia, United States

Fred Hutch Cancer Center

Seattle, Washington, United States

University of Wisconsin Health

Madison, Wisconsin, United States

St Vincents Hospital Sydney (Kinghorn)

Darlinghurst, New South Wales, Australia

Royal North Shore Hospital

Saint Leonards, New South Wales, Australia

Royal Brisbane and Women's Hospital

Herston, Queensland, Australia

Peter MacCallum Cancer Centre

Melbourne, Victoria, Australia

The Alfred

Melbourne, Victoria, Australia

Beijing Tiantan Hospital, Capital Medical University

Beijing, Beijing Municipality, China

Sanbo Brain Hospital, Capital Medical University

Beijing, Beijing Municipality, China

Xuanwu Hospital, Capital Medical University

Beijing, Beijing Municipality, China

Peking Union Medical College Hospital

Beijing, Beijing Municipality, China

The First Affiliated Hospital of Fujian Medical University

Fuzhou, Fujian, China

Sun Yat-sen University Cancer Center

Guangzhou, Guangdong, China

Xiangya Hospital of Central South University

Changsha, Hunan, China

Huashan Hospital Affiliated to Fudan University

Shanghai, Shanghai Municipality, China

West China Hospital of Sichuan University

Chengdu, Sichuan, China

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NCT05303519


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