RecruitingPhase 3NCT05682378

Long-term Safety and Tolerability of Inclisiran in Participants With HeFH or HoFH Who Have Completed the Pediatric ORION-16, ORION-13, ORION-20, or ORION-19 Studies

An Open-label, Single Arm, Multicenter Extension Study to Evaluate Long-term Safety and Tolerability of Inclisiran in Participants With Heterozygous or Homozygous Familial Hypercholesterolemia Who Have Completed the Pediatric ORION-16, ORION-13, ORION-20 or ORION-19 Studies (VICTORION-PEDS-OLE)


Sponsor

Novartis Pharmaceuticals

Enrollment

195 participants

Start Date

Feb 10, 2023

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of this open-label, single arm, multicenter extension study is to evaluate the long-term safety and tolerability of inclisiran in participants with HeFH or HoFH who have completed the ORION-16 (CKJX839C12301), ORION-13 (CKJX839C12302), ORION-20 (CKJX839C12303) or ORION-19 (CKJX839C12304) studies.


Eligibility

Min Age: 12 YearsMax Age: 100 Years

Inclusion Criteria2

  • Male and female participants with a diagnosis of HeFH or HoFH who completed the ORION-16, ORION-13, ORION-20 or ORION-19 studies
  • Per investigator's clinical judgment, participant derived benefit from treatment with inclisiran in the ORION-16, ORION-13, ORION-20 or ORION-19 studies

Exclusion Criteria2

  • Participants who in the feeder ORION-16, ORION-13, ORION-20, or ORION-19 studies either screen failed or permanently discontinued from the treatment/study for any reason or had serious safety or tolerability issues related to inclisiran treatment
  • Any uncontrolled or serious disease, or any medical, physical, or surgical condition, that may either interfere with participation in the clinical study or interpretation of clinical study results, and/or put the participant at significant risk

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Interventions

DRUGInclisiran

Solution for injection


Locations(52)

Excel Medical Clinical Trials LLC

Boca Raton, Florida, United States

Icahn School of Med at Mt Sinai

New York, New York, United States

Cincinnati Childrens Hospital MC

Cincinnati, Ohio, United States

Childrens Hosp Pittsburgh UPMC

Pittsburgh, Pennsylvania, United States

Primary Childrens Medical Center

Salt Lake City, Utah, United States

Novartis Investigative Site

Formosa, Formosa Province, Argentina

Novartis Investigative Site

Fortaleza, Ceará, Brazil

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Novartis Investigative Site

Québec, Quebec, Canada

Novartis Investigative Site

Prague, Czechia

Novartis Investigative Site

Prague, Czechia

Novartis Investigative Site

Besançon, France

Novartis Investigative Site

Toulouse, France

Novartis Investigative Site

Frankfurt am Main, Hesse, Germany

Novartis Investigative Site

Freiburg im Breisgau, Germany

Novartis Investigative Site

Athens, Greece

Novartis Investigative Site

Athens, Greece

Novartis Investigative Site

Pécs, Baranya, Hungary

Novartis Investigative Site

Jerusalem, Israel

Novartis Investigative Site

Ramat Gan, Israel

Novartis Investigative Site

Milan, MI, Italy

Novartis Investigative Site

Modena, MO, Italy

Novartis Investigative Site

Roma, RM, Italy

Novartis Investigative Site

Roma, Italy

Novartis Investigative Site

Irbid, Jordan

Novartis Investigative Site

Beirut, Lebanon

Novartis Investigative Site

Beirut, Lebanon

Novartis Investigative Site

Sungai Buloh, Selangor, Malaysia

Novartis Investigative Site

Kuala Lumpur, Malaysia

Novartis Investigative Site

Amsterdam, North Holland, Netherlands

Novartis Investigative Site

Rotterdam, South Holland, Netherlands

Novartis Investigative Site

Oslo, Norway

Novartis Investigative Site

Gdansk, Poland

Novartis Investigative Site

Lodz, Łódź Voivodeship, Poland

Novartis Investigative Site

Kemerovo, Russia

Novartis Investigative Site

Moscow, Russia

Novartis Investigative Site

Poprad, Slovakia

Novartis Investigative Site

Ljubljana, Slovenia

Novartis Investigative Site

Bloemfontein, Free State, South Africa

Novartis Investigative Site

Cape Town, Western Cape, South Africa

Novartis Investigative Site

Pamplona, Navarre, Spain

Novartis Investigative Site

Oviedo, Principality of Asturias, Spain

Novartis Investigative Site

A Coruña, Spain

Novartis Investigative Site

Córdoba, Spain

Novartis Investigative Site

Geneva, Switzerland

Novartis Investigative Site

Taipei, Taiwan

Novartis Investigative Site

Istanbul, Fatih, Turkey (Türkiye)

Novartis Investigative Site

Adana, Saricam, Turkey (Türkiye)

Novartis Investigative Site

Ankara, Yenimahalle, Turkey (Türkiye)

Novartis Investigative Site

Izmir, Turkey (Türkiye)

Novartis Investigative Site

Middlesex, United Kingdom

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NCT05682378