RecruitingNCT05755451
Natural History of SMA
Natural History of SMA: Long Term Longitudinal Study and Development of a Registry
Sponsor
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Enrollment
1,200 participants
Start Date
Jun 21, 2018
Study Type
OBSERVATIONAL
Conditions
Summary
This is an investigator initiated observational study with the aim to record several aspects of function, care and adverse events in a large cohort of SMA patients followed longitudinally by using a structured academic disease registry.
Eligibility
Inclusion Criteria1
- all patients
Exclusion Criteria1
- if enrolled in clinical trials
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Locations(5)
View Full Details on ClinicalTrials.gov
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NCT05755451
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