RecruitingNCT05775523

A Post-Authorisation Safety Study (PASS) of Patients Treated With Lonapegsomatropin

A Prospective, Non-interventional (NIS), Long-term, Post-Authorisation Safety Study (PASS) of Patients Treated With Lonapegsomatropin


Sponsor

Ascendis Pharma Endocrinology Division A/S

Enrollment

500 participants

Start Date

Mar 20, 2023

Study Type

OBSERVATIONAL

Conditions

Summary

The goal of this study is to further characterise the potential long-term safety risks of lonapegsomatropin in patients treated with lonapegsomatropin under real-world conditions in the post-marketing setting.


Eligibility

Min Age: 1 YearMax Age: 18 Years

Inclusion Criteria4

  • Paediatric patients with GHD who are on treatment with lonapegsomatropin
  • Patients being clinically managed in Europe or the USA
  • Appropriate written informed consent/assent as applicable for the age of the patient
  • Patients willing to comply with follow-up requirements of the study

Exclusion Criteria7

  • Patients participating in any interventional clinical trial for short stature
  • Patients being treated with a GH or IGF-1 therapy, other than lonapegsomatropin, at enrollment
  • Patients for whom treatment with lonapegsomatropin is contraindicated
  • Patients with closed epiphyses
  • Patients with active malignant tumours
  • Patients under antitumour therapy within the past 12 months prior to instituting GH therapy
  • Hypersensitivity to somatropin or any of the excipients in lonapegsomatropin

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Interventions

DRUGNo intervention

No intervention


Locations(27)

Ascendis Investigational Site

Phoenix, Arizona, United States

Ascendis Investigational Site

Orange, California, United States

Ascendis Investigational Site

Sacramento, California, United States

Ascendis Investigational Site

San Francisco, California, United States

Ascendis Pharma Investigational Site

Centennial, Colorado, United States

Ascendis Investigational Site

Washington D.C., District of Columbia, United States

Ascendis Investigational Site

Orlando, Florida, United States

Ascendis Investigational Site

Orlando, Florida, United States

Ascendis Investigational Site

Tampa, Florida, United States

Ascendis Investigational Site

Sandy Springs, Georgia, United States

Ascendis Investigational Site

Boise, Idaho, United States

Ascendis Investigational Site

Indianapolis, Indiana, United States

Ascendis Investigational Site

Iowa City, Iowa, United States

Ascendis Investigational Site

Louisville, Kentucky, United States

Ascendis Investigational Site

Minneapolis, Minnesota, United States

Ascendis Investigational Site

Las Vegas, Nevada, United States

Ascendis Investigational Site

Lebanon, New Hampshire, United States

Ascendis Investigational Site

Manchester, New Hampshire, United States

Ascendis Investigational Site

Morristown, New Jersey, United States

Ascendis Investigational Site

New Hyde Park, New York, United States

Ascendis Investigational Site

Cincinnati, Ohio, United States

Ascendis Investigational Site

Portland, Oregon, United States

Ascendis Investigational Site

Columbia, South Carolina, United States

Ascendis Investigational Site

Dallas, Texas, United States

Ascendis Investigational Site

El Paso, Texas, United States

Ascendis Investigational Site

Norfolk, Virginia, United States

Ascendis Investigational Site

Seattle, Washington, United States

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NCT05775523


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