RecruitingPhase 1Phase 2NCT05776069

Study of VGA039 in Healthy Volunteers and Patients With Von Willebrand Disease (VIVID)

A Multi-Modular Trial to Evaluate VGA039 in Healthy Volunteers and Patients With Von Willebrand Disease and Other Bleeding Disorders (VIVID)


Sponsor

Vega Therapeutics, Inc

Enrollment

116 participants

Start Date

Mar 16, 2023

Study Type

INTERVENTIONAL

Conditions

Summary

The VIVID study is structured in a master protocol format comprised of multiple parts that evaluate intravenous (IV) and subcutaneous (SC) VGA039 in healthy volunteers and subjects with von Willebrand Disease (VWD) and other bleeding disorders.


Eligibility

Min Age: 12 YearsMax Age: 60 Years

Inclusion Criteria13

  • Subjects, 18 to 60 years of age, inclusive for Parts 1 and 2
  • Subjects, 12 to 60 years of age, inclusive for Parts 3 and 5
  • No clinically significant laboratory, ECG, or vital signs results.
  • Subjects with VWD who are symptomatic, defined as having a history of bleeding or bruising.
  • Hemoglobin level ≥ 8 g/dL and platelet count ≥ 150 × 109/L at Screening.
  • Exclusion Key Criteria (All Subjects)
  • Use of hormonal contraceptives within 56 days prior to administration of the study drug.
  • Subjects with detection of FV Leiden or Prothrombin G20210A mutation, protein C or S deficiency, antithrombin deficiency, or antiphospholipid antibody syndrome at Screening.
  • Subjects with other known pro-thrombotic disorders or abnormal findings in any prior laboratory thrombophilia evaluation.
  • History of arterial or venous thrombosis, including superficial thrombophlebitis, or embolism.
  • Evidence of renal, hepatic, central nervous system, respiratory, cardiovascular disease, cerebrovascular disease, peripheral vascular disease, or metabolic dysfunction.
  • Additional Key Exclusion Criterion (Subjects in Part 1 Only)
  • • Baseline FVIII activity \> 150 IU/dL.

Exclusion Criteria2

  • Baseline FVIII activity \> 50 IU/dL.
  • Any acute, clinically significant bleeding event requiring surgical or procedural intervention within 7 days prior to receiving study drug.

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Interventions

DRUGVGA039

Single doses of VGA039

OTHERPlacebo

Single doses of Placebo

DRUGVGA039

Multiple doses of VGA039


Locations(25)

Orthopedic Institute for Children (UCLA)

Los Angeles, California, United States

UC Davis Medical Center

Sacramento, California, United States

University of Colorado School of Medicine

Aurora, Colorado, United States

Hemophilia of Georgia Center for Bleeding & Clotting Disorders of Emory

Atlanta, Georgia, United States

Science 37, Inc.

Morrisville, North Carolina, United States

Hemophilia Center of Western PA

Pittsburgh, Pennsylvania, United States

Vanderbilt University Medical Center

Nashville, Tennessee, United States

University of Texas Southwestern

Dallas, Texas, United States

Washington Center for Bleeding Disorders

Seattle, Washington, United States

Versiti Comprehensive Center for Bleeding Disorders

Milwaukee, Wisconsin, United States

Royal Brisbane & Women's Hospital, Queensland Haemophilia Centre

Herston, Queenland, Australia

Medical University of Vienna

Vienna, Vienna, Austria

Centro de Hemoterapia e Hematologia do Rio de Janeiro HEMORIO

Rio de Janeiro, Rio de Janeiro, Brazil

Hemocentro Unicamp

Campinas, São Paulo, Brazil

Hospital das Clinicas - USP Endereco

São Paulo, São Paulo, Brazil

Hamilton Health Sciences Corporation

Hamilton, Ontario, Canada

Queens University

Kingston, Ontario, Canada

St. Michaels Hospital

Toronto, Ontario, Canada

K J Somaiya Super Speciality Hospital & Research Centre

Sion, Mumbai, India

Charlotte Maxeke Johannesburg Academic Hospital

Johannesburg, South Africa

Queen Elizabeth Hospital Birmingham

Birmingham, Edgbaston, United Kingdom

University Hospital Southampton NHS Foundation Trust

Southampton, Hampshire, United Kingdom

Royal Free Hospital

London, London, United Kingdom

Royal London Hospital, Clinical Haematology Research

Whitechapel, London, United Kingdom

Imperial College Healthcare NHS Trust- Queen Charlotte's & Chelsea Hospital

London, United Kingdom

View Full Details on ClinicalTrials.gov

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NCT05776069


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