RecruitingPhase 3NCT05827081

Phase IIIb Study of Ribociclib + ET in Early Breast Cancer

A Phase IIIb Study to Characterize the Efficacy and Safety of Adjuvant Ribociclib Plus Endocrine Therapy in a Close-to-clinical Practice Patient Population With HR+ HER2- Early Breast Cancer (Adjuvant WIDER)


Sponsor

Novartis Pharmaceuticals

Enrollment

1,400 participants

Start Date

Feb 28, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of this open-label, multicenter, phase IIIb, single-arm study is to characterize the efficacy and safety of the combination of ribociclib and standard adjuvant endocrine therapy (ET) on invasive breast cancer-free survival (iBCFS), in a close to clinical practice patient population with HR-positive (HR+), HER2-negative (HER2-), Anatomic Stage Group III, IIB, and a subset of Stage IIA Early Breast Cancer (EBC).


Eligibility

Min Age: 18 YearsMax Age: 100 Years

Inclusion Criteria16

  • Participant is an adult, male or female ≥ 18 years of age at the time of informed consent form signature (IC).
  • Participant has a histologically and/or cytologically confirmed diagnosis of estrogen-receptor positive and/or progesterone receptor positive breast cancer (BC) based on the most recently analyzed tissue sample tested by a local laboratory prior to enrollment.
  • Participant has HER2- BC defined as a negative in situ hybridization test or an immunohistochemistry (IHC) status of 0, 1+ or 2+. If IHC is 2+, a negative in situ hybridization (FISH, CISH, or SISH) test is required by local laboratory testing based on the most recently analyzed tissue sample.
  • Participants may have already received any standard neoadjuvant and/or adjuvant ET, including tamoxifen or toremifene at the time of informed consent signature, but enrollment should occur within 36 months of prior ET start date and participants should have at least 3 years remaining of endocrine adjuvant therapy.
  • For participants with prior ET treatment \> 12 months, restaging is highly recommended (unless contradictory to local regulations) to rule out disease recurrence prior to enrollment.
  • The number of participants with prior ET between 12 and 36 months will be capped at 30%. The cap will not apply to Black or African American participants.
  • Participant has no contraindication to receive adjuvant ET in the study.
  • Participant after surgical resection where tumor was removed completely, with the final surgical specimen microscopic margins free from tumor, and belongs to one of the following categories:
  • Anatomic Stage Group III, or
  • Anatomic Stage Group IIB, or
  • A subset of Anatomic Stage Group IIA.
  • Participant has an Eastern Cooperative Oncology Group (ECOG) Performance Status of 0, 1 or 2.
  • Participant has adequate bone marrow and organ function.
  • ECG values assessed by KardiaMobile-6L device, or standard 12-lead ECG per local investigator where KardiaMobile-6L cannot be used, as:
  • QTcF interval at Screening \< 450 msec (QT interval using Fridericia's correction).
  • Mean resting heart rate 50-99 beats per minute (determined from the ECG).

Exclusion Criteria6

  • Participant with distant metastases of BC beyond regional lymph nodes (Stage IV according to AJCC 8th edition) and/or evidence of recurrence after curative surgery.
  • Participant is concurrently using other antineoplastic therapy with the exception of adjuvant ET.
  • Participant has any other concurrent severe and/or uncontrolled medical condition that would, in the Investigator's judgment, cause unacceptable safety risks, contraindicate participant participation in the clinical study or compromise compliance with the protocol, or limit life expectancy to ≤5 years.
  • Clinically significant, uncontrolled heart disease and/or cardiac repolarization abnormality.
  • Pregnant or breast-feeding (lactating) women or women who plan to become pregnant or breast-feed during the trial.
  • Women of child-bearing potential (CBP), defined as all women physiologically capable of becoming pregnant, unless they are using highly effective methods of contraception while taking study treatment and for 21 days after stopping the treatment.

Interventions

DRUGExemestane

Exemestane 25 mg once daily continuously

DRUGRibociclib

Ribociclib 400 mg orally once daily on days 1-21 of a 28 day cycle followed by 7 days rest

DRUGLetrozole

Letrozole 2.5 mg orally once daily continuously

DRUGAnsastrozole

Anastrozole 1 mg orally once daily continuously.

DRUGGoserelin

Goserelin administered subcutaneously at 3.6 mg once every 4 weeks if the one-month depot formulation is used or at 10.8 mg once every 3 months if the three-month depot formulation is used

DRUGLeuprolide

Leuprolide administered subcutaneously at 3.75 mg once every 4 weeks if the one-month depot formulation is used or at 11.25 mg once every 3 months if the three-month depot formulation is used


Locations(193)

Novartis Investigative Site

Ottawa, Ontario, Canada

Novartis Investigative Site

Toronto, Ontario, Canada

Novartis Investigative Site

Montreal, Quebec, Canada

Novartis Investigative Site

Montreal, Quebec, Canada

Novartis Investigative Site

Montreal, Quebec, Canada

Novartis Investigative Site

Québec, Quebec, Canada

Novartis Investigative Site

Beijing, Beijing Municipality, China

Novartis Investigative Site

Guangzhou, Guangdong, China

Novartis Investigative Site

Harbin, Heilongjiang, China

Novartis Investigative Site

Zhengzhou, Henan, China

Novartis Investigative Site

Zhengzhou, Henan, China

Novartis Investigative Site

Nanjing, Jiangsu, China

Novartis Investigative Site

Nanchang, Jiangxi, China

Novartis Investigative Site

Changchun, Jilin, China

Novartis Investigative Site

Jinan, Shandong, China

Novartis Investigative Site

Jinan, Shandong, China

Novartis Investigative Site

Jining, Shandong, China

Novartis Investigative Site

Chengdu, Sichuan, China

Novartis Investigative Site

Chengdu, Sichuan, China

Novartis Investigative Site

Ürümqi, Xinjiang, China

Novartis Investigative Site

Hangzhou, Zhejiang, China

Novartis Investigative Site

Hangzhou, Zhejiang, China

Novartis Investigative Site

Wenzhou, Zhejiang, China

Novartis Investigative Site

Beijing, China

Novartis Investigative Site

Beijing, China

Novartis Investigative Site

Guangzhou, China

Novartis Investigative Site

Qingdao, China

Novartis Investigative Site

Shanghai, China

Novartis Investigative Site

Shijiazhuang, China

Novartis Investigative Site

Tianjin, China

Novartis Investigative Site

Freiburg im Breisgau, Baden-Wurttemberg, Germany

Novartis Investigative Site

Munich, Bavaria, Germany

Novartis Investigative Site

Regensburg, Bavaria, Germany

Novartis Investigative Site

Weiden in Der Oberpfalz, Bavaria, Germany

Novartis Investigative Site

Langen, Hesse, Germany

Novartis Investigative Site

Hildesheim, Lower Saxony, Germany

Novartis Investigative Site

Bergisch Gladbach, North Rhine-Westphalia, Germany

Novartis Investigative Site

Bielefeld, North Rhine-Westphalia, Germany

Novartis Investigative Site

Düsseldorf, North Rhine-Westphalia, Germany

Novartis Investigative Site

Essen, North Rhine-Westphalia, Germany

Novartis Investigative Site

Mönchengladbach, North Rhine-Westphalia, Germany

Novartis Investigative Site

Velbert, North Rhine-Westphalia, Germany

Novartis Investigative Site

Dresden, Saxony, Germany

Novartis Investigative Site

Lübeck, Schleswig-Holstein, Germany

Novartis Investigative Site

Augsburg, Germany

Novartis Investigative Site

Augsburg, Germany

Central Alabama Research

Birmingham, Alabama, United States

Alaska Oncology and Hematology LLC

Anchorage, Alaska, United States

Western Reg MC-COH Phoenix

Goodyear, Arizona, United States

CARTI Cancer Center

Little Rock, Arkansas, United States

Onco Inst of Hope and Innovation

Cerritos, California, United States

City of Hope National Medical

Duarte, California, United States

Providence Medical Foundation

Fullerton, California, United States

Palo Alto Medical Foundation

Mountain View, California, United States

UC Irvine Medical Center

Orange, California, United States

Sutter Inst Medical Research

Sacramento, California, United States

School Of Medicine

Sacramento, California, United States

Rocky Mountain Cancer Centers

Denver, Colorado, United States

Georgetown University Lombardi Cancer Center

Washington D.C., District of Columbia, United States

Washington Hospital Center

Washington D.C., District of Columbia, United States

Holy Cross Health

Fort Lauderdale, Florida, United States

Memorial Cancer Institute

Hollywood, Florida, United States

Ocala Research Institute, Inc

Ocala, Florida, United States

Summit Cancer Care PC

Savannah, Georgia, United States

Affiliated Oncologists IL

Chicago, Illinois, United States

Hope And Healing Care

Hinsdale, Illinois, United States

Midwestern Reg MC COH Chicago

Zion, Illinois, United States

Investigative Clinical R of Indiana

Indianapolis, Indiana, United States

University of Iowa Health Care

Waukee, Iowa, United States

University of Kansas Cancer Center

Westwood, Kansas, United States

Cancer Center of Kansas

Wichita, Kansas, United States

Willis-Knighton Cancer Center

Shreveport, Louisiana, United States

Mercy Medical Center

Baltimore, Maryland, United States

Maryland Oncology Hematology P A

Silver Spring, Maryland, United States

Boston Medical Center

Boston, Massachusetts, United States

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Minnesota Oncology Hematology P A

Minneapolis, Minnesota, United States

Jackson Oncology Associates

Jackson, Mississippi, United States

HCA Midwest Division

Kansas City, Missouri, United States

WA Uni School Of Med

St Louis, Missouri, United States

Intermountain Healthcare

Billings, Montana, United States

Nebraska Cancer Specialists

Omaha, Nebraska, United States

Renown Regional Medical Center

Reno, Nevada, United States

Summit Health

Florham Park, New Jersey, United States

The Valley Hospital

Ridgewood, New Jersey, United States

Presbyterian Medical Group

Albuquerque, New Mexico, United States

Queens Cancer Center of Queens Hospital

Jamaica, New York, United States

Clinical Research Alliance

Lake Success, New York, United States

Mount Sinai School of Medicine

New York, New York, United States

Duke Cancer Network

Durham, North Carolina, United States

Cone Health Cancer Center

Greensboro, North Carolina, United States

Oncology Associates of Oregon PC

Eugene, Oregon, United States

Northwest Cancer Specialists

Portland, Oregon, United States

Oregon Oncology Specialists Salem

Salem, Oregon, United States

Consultants In Med Onco And Hema

Drexel Hill, Pennsylvania, United States

Univ of Pittsburg Med Ctr Pinnacle

Harrisburg, Pennsylvania, United States

Rhode Island Hospital

Providence, Rhode Island, United States

Lexington Medical Center

West Columbia, South Carolina, United States

Sanford USD Medical Center

Sioux Falls, South Dakota, United States

Sarah Cannon Research Institute

Nashville, Tennessee, United States

El Paso Texas Oncology

El Paso, Texas, United States

Kelsey Seybold Clinic

Houston, Texas, United States

University of Texas

Houston, Texas, United States

Texas Oncology P A Plano East

Plano, Texas, United States

Texas Oncology PA Tyler

Tyler, Texas, United States

Bon Secours Virginia Health System

Midlothian, Virginia, United States

Virginia Oncology Associates

Norfolk, Virginia, United States

Providence Regional Cancer System

Lacey, Washington, United States

Northwest Medical Specialties

Tacoma, Washington, United States

Novartis Investigative Site

Córdoba, Argentina

Novartis Investigative Site

Gateshead, New South Wales, Australia

Novartis Investigative Site

Tiwi, Northern Territory, Australia

Novartis Investigative Site

Clayton, Victoria, Australia

Novartis Investigative Site

East Melbourne, Victoria, Australia

Novartis Investigative Site

Victoria, British Columbia, Canada

Novartis Investigative Site

Halifax, Nova Scotia, Canada

Novartis Investigative Site

Oakville, Ontario, Canada

Novartis Investigative Site

Berlin, Germany

Novartis Investigative Site

Berlin, Germany

Novartis Investigative Site

Bottrop, Germany

Novartis Investigative Site

Böblingen, Germany

Novartis Investigative Site

Dessau, Germany

Novartis Investigative Site

Erlangen, Germany

Novartis Investigative Site

Essen, Germany

Novartis Investigative Site

Hamburg, Germany

Novartis Investigative Site

Kiel, Germany

Novartis Investigative Site

Leipzig, Germany

Novartis Investigative Site

Mainz, Germany

Novartis Investigative Site

München, Germany

Novartis Investigative Site

Ravensburg, Germany

Novartis Investigative Site

Hong Kong, Hong Kong

Novartis Investigative Site

Kowloon, Hong Kong

Novartis Investigative Site

Tuenmen, Hong Kong

Novartis Investigative Site

Hyderabad, Andhra Pradesh, India

Novartis Investigative Site

Bangalore, Karnataka, India

Novartis Investigative Site

Mumbai, Maharashtra, India

Novartis Investigative Site

Pune, Maharasthra, India

Novartis Investigative Site

New Delhi, National Capital Territory of Delhi, India

Novartis Investigative Site

Bhubaneshwar, Odisha, India

Novartis Investigative Site

Chennai, Tamil Nadu, India

Novartis Investigative Site

Kolkata, West Bengal, India

Novartis Investigative Site

Ahmedabad, India

Novartis Investigative Site

Beersheba, Israel

Novartis Investigative Site

Petah Tikva, Israel

Novartis Investigative Site

Ramat Gan, Israel

Novartis Investigative Site

Tel Aviv, Israel

Novartis Investigative Site

Alc Cuahutemoc, Mexico City, Mexico

Novartis Investigative Site

Tlalpan, Mexico City, Mexico

Novartis Investigative Site

Monterrey, Nuevo León, Mexico

Novartis Investigative Site

Coimbra, Portugal

Novartis Investigative Site

Lisbon, Portugal

Novartis Investigative Site

Lisbon, Portugal

Novartis Investigative Site

Porto, Portugal

Novartis Investigative Site

Porto, Portugal

Novartis Investigative Site

Porto, Portugal

Pan Oncology

Rio Piedras, Puerto Rico

Novartis Investigative Site

Bundang Gu, Gyeonggi-do, South Korea

Novartis Investigative Site

Gyeonggi-do, Korea, South Korea

Novartis Investigative Site

Incheon, Korea, South Korea

Novartis Investigative Site

Seoul, Korea, South Korea

Novartis Investigative Site

Seoul, Korea, South Korea

Novartis Investigative Site

Seoul, Yangcheon Gu, South Korea

Novartis Investigative Site

Seongnam Gyeonggi, South Korea

Novartis Investigative Site

Seoul, South Korea

Novartis Investigative Site

Seoul, South Korea

Novartis Investigative Site

Seoul, South Korea

Novartis Investigative Site

Seoul, South Korea

Novartis Investigative Site

Seoul, South Korea

Novartis Investigative Site

Hualien City, Taiwan

Novartis Investigative Site

Kaohsiung City, Taiwan

Novartis Investigative Site

Tainan, Taiwan

Novartis Investigative Site

Taipei, Taiwan

Novartis Investigative Site

Taipei, Taiwan

Novartis Investigative Site

Sakarya, Adapazari, Turkey (Türkiye)

Novartis Investigative Site

Ankara, Bilkent-Cankaya, Turkey (Türkiye)

Novartis Investigative Site

Istanbul, Fatih, Turkey (Türkiye)

Novartis Investigative Site

Istanbul, Kadikoy, Turkey (Türkiye)

Novartis Investigative Site

Izmir, Karsiyaka, Turkey (Türkiye)

Novartis Investigative Site

Denizli, Kinikli, Turkey (Türkiye)

Novartis Investigative Site

Antalya, Konyaalti, Turkey (Türkiye)

Novartis Investigative Site

Istanbul, Sariyer, Turkey (Türkiye)

Novartis Investigative Site

Ankara, Sihhiye-Altindag, Turkey (Türkiye)

Novartis Investigative Site

Diyarbakır, Sur, Turkey (Türkiye)

Novartis Investigative Site

Istanbul, Uskudar, Turkey (Türkiye)

Novartis Investigative Site

Ankara, Yenimahalle, Turkey (Türkiye)

Novartis Investigative Site

Ankara, Yenimahalle, Turkey (Türkiye)

Novartis Investigative Site

Adana, Yuregir, Turkey (Türkiye)

Novartis Investigative Site

Ankara, Turkey (Türkiye)

Novartis Investigative Site

Istanbul, Turkey (Türkiye)

Novartis Investigative Site

Izmir, Turkey (Türkiye)

Novartis Investigative Site

Kecioren Ankara, Turkey (Türkiye)

Novartis Investigative Site

Konya, Turkey (Türkiye)

Novartis Investigative Site

Samsun, Turkey (Türkiye)

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