RecruitingNCT06036693

MPS (RaDiCo Cohort) (RaDiCo-MPS)

Mucopolysaccharidosis Patients in France in the Era of Specific Therapeutics

Sponsor

Institut National de la Santé Et de la Recherche Médicale, France

Enrollment

1,000 participants

Start Date

Dec 20, 2017

Study Type

OBSERVATIONAL

Conditions

Mucopolysaccharidosis I Mucopolysaccharidosis II Mucopolysaccharidosis III Mucopolysaccharidosis IV Mucopolysaccharidosis VI Mucopolysaccharidosis VII Mucopolysaccharidosis IX Multiple Sulfatase Deficiency Disease

Summary

The goal of this observational study is to characterize the epidemiology and natural history of MPS diseases by building a retrospective and prospective collection of extensive phenotypic data from French MPS patients.

Eligibility

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a new treatment for people with mucopolysaccharidosis i, mucopolysaccharidosis ii, and other related conditions. The study is currently recruiting participants at 23 locations.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Locations(23)

Centre Hospitalier Universitaire d'Angers

Angers, France

Hôpital des Enfants - Groupe Hospitalier Pellegrin

Bordeaux, France

Hôpital Morvan

Brest, France

Hôpital d'Estaing

Clermont-Ferrand, France

Hôpital Beaujon

Clichy, France

Hôpital Raymond-Poincaré

Garches, France

Hôpital Jeanne de Flandre

Lille, France

Hôpital de la Timone

Marseille, France

Hôpital Gui de Chauliac

Montpellier, France

Hôpital Brabois

Nancy, France

Hôpital Armand Trousseau

Paris, France

Hôpital de la Croix Saint-Simon

Paris, France

Hôpital de la Pitié-Salpêtrière

Paris, France

Hôpital Necker-Enfants Malades

Paris, France

Hôpital Robert Debré

Paris, France

Centre Hospitalier de Pau

Pau, France

American Memorial Hospital

Reims, France

Hôpital Pontchaillou

Rennes, France

Hôpital Charles Nicolle

Rouen, France

Hôpital de Hautepierre

Strasbourg, France

Clinique Monié

Toulouse, France

Hôpital des Enfants

Toulouse, France

Hôpital Clocheville

Tours, France

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NCT06036693

Related Trials

MPS (RaDiCo Cohort) (RaDiCo-MPS)

Conditions

Summary

Eligibility

Plain Language Summary

Locations(23)

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