RecruitingPhase 3NCT06051617

Seladelpar in Subjects With Primary Biliary Cholangitis (PBC) and Compensated Cirrhosis

AFFIRM: A Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Effect of Seladelpar on Clinical Outcomes in Patients With Primary Biliary Cholangitis (PBC) and Compensated Cirrhosis


Sponsor

Gilead Sciences

Enrollment

318 participants

Start Date

Sep 7, 2023

Study Type

INTERVENTIONAL

Conditions

Summary

To Evaluate the Effect of Seladelpar on Clinical Outcomes in Patients with Primary Biliary Cholangitis (PBC) and Compensated Cirrhosis.


Eligibility

Min Age: 18 Years

Inclusion Criteria7

  • Individuals must meet the following criteria to be eligible for study participation:
  • Must be at least 18 years old.
  • Must have a confirmed prior diagnosis of PBC
  • Evidence of cirrhosis
  • CP Score A or B
  • Females of reproductive potential must use at least 1 barrier contraceptive and a second effective birth control method during the study and for at least 90 days after the last dose. Male individuals who are sexually active with female partners of reproductive potential must use barrier contraception, and their female partners must use a second effective birth control method during the study and for at least 90 days after the last dose
  • Individuals must be able to comply with the instructions for study drug administration and be able to complete the study schedule of assessments (SOA)

Exclusion Criteria19

  • Individuals must not meet any of the following criteria to be eligible for study participation:
  • Prior exposure to seladelpar
  • A medical condition other than PBC that, in the Investigator's opinion, would preclude full participation in the study
  • History of liver transplantation or actively listed for cadaveric or planned living donor transplant.
  • Decompensated cirrhosis
  • Evidence of portal vein thrombosis based on imaging at time of Screening by Doppler ultrasound or prior evidence by CT or MRI
  • Hospitalization for liver-related complication within 12 weeks of Screening
  • Laboratory parameters at Screening:
  • Alkaline phosphatase (ALP) \< 1.5× Upper limit of normal (ULN) or ≥ 10×ULN
  • Alanine aminotransferase (ALT) or Aspartate aminotransferase (AST) ≥5×ULN
  • Total bilirubin (TB) ≤ 0.6 × ULN or ≥ 5 × ULN
  • Platelet count ≤50×10\^3/µL
  • Albumin ≤2.8 g/dL
  • Estimated glomerular filtration rate (eGFR) \<45 mL/min/1.73 m\^2
  • MELD score \>12. For individuals on anticoagulation medication, baseline International normalized ratio (INR) determination for MELD score calculation should take anticoagulant use into account, in consultation with the Medical Monitor.
  • Serum alpha-fetoprotein (AFP) \>20 ng/mL
  • INR \>1.7
  • CP-C cirrhosis
  • History or presence of other concomitant liver diseases

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Interventions

DRUGSeladelpar

* Seladelpar 10 mg one capsule daily for up to 36 months in participants with CP-A cirrhosis or * Seladelpar 5 mg one capsule daily for up to 36 months in participants with CP-B cirrhosis.

DRUGPlacebo

One capsule daily for up to 36 months.


Locations(191)

St. Joseph's Hospital and Medical Center - 350 W. Thomas

Phoenix, Arizona, United States

OM Research LLC

Lancaster, California, United States

SCPMG/Kaiser Permanente Los Angeles Medical Center

Los Angeles, California, United States

Cedar Sinai Medical Center

Los Angeles, California, United States

California Liver Research Institute

Pasadena, California, United States

Stanford University

Redwood City, California, United States

University of California, Davis Medical Center

Sacramento, California, United States

California Pacific Medical Center - Sutter Pacific Medical Foundation

San Francisco, California, United States

Connie Frank Transplant Center at UCSF

San Francisco, California, United States

Covenant Metabolic Specialists, LLC

Fort Myers, Florida, United States

Schiff Center for Liver Diseases/University of Miami

Miami, Florida, United States

Covenant Metabolic Specialists, LLC

Sarasota, Florida, United States

Florida Research Institute

Tampa, Florida, United States

Piedmont Atlanta Hospital / Piedmont Transplant Institute

Atlanta, Georgia, United States

Northwestern University

Chicago, Illinois, United States

University of Chicago Medical Center

Chicago, Illinois, United States

University Of Iowa Hospitals And Clinics

Iowa City, Iowa, United States

University of Louisville, Clinical Trials Unit

Louisville, Kentucky, United States

Ochsner Clinic Foundation

Jefferson, Louisiana, United States

University Health System - East Jefferson General Hospital Campus

New Orleans, Louisiana, United States

Mercy Medical Center

Baltimore, Maryland, United States

Walter Reed National Military

Bethesda, Maryland, United States

Massachusetts General Hospital

Boston, Massachusetts, United States

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Henry Ford Medical Center - Columbus

Detroit, Michigan, United States

University of Rochester Medical Center - Strong Memorial Hospital

Rochester, Minnesota, United States

Northwell Health Center for Liver Disease and Transplantation

Manhasset, New York, United States

NYU Langone Health

New York, New York, United States

Mount Sinai

New York, New York, United States

Wake Forest Baptist Medical Center

Winston-Salem, North Carolina, United States

University Hosptials Cleveland Medical Center

Cleveland, Ohio, United States

The Cleveland Clinic Foundation

Cleveland, Ohio, United States

The Ohio State University Medical Center

Columbus, Ohio, United States

Penn State Health Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

University of Pennsylvania Perelman Center for Advanced Medicine

Philadelphia, Pennsylvania, United States

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

UPMC Center for Liver Diseases

Pittsburgh, Pennsylvania, United States

Medical University of South Carolina

Charleston, South Carolina, United States

Gastro One

Cordova, Tennessee, United States

The Liver Institute at Methodist Dallas Medical Center

Dallas, Texas, United States

University of Texas Southwestern Medical Center, Professional Office Building One

Dallas, Texas, United States

Soma Clinical Trials

Denison, Texas, United States

American Research Corporation

San Antonio, Texas, United States

Pinnacle Clinical Research, PLLC

San Antonio, Texas, United States

MedStar Health Research Institute / MedStar Georgetown Transplant Institute at Fairfax

Fairfax, Virginia, United States

Maryview Hospital LLC d/b/a Bon Secours Liver Institute of Hampton Roads

Newport News, Virginia, United States

VCU Health Clinical Research Services Unit (CRSU)

Richmond, Virginia, United States

Liver Institute Northwest

Seattle, Washington, United States

Hospital Italiano de Buenos Aires

Buenos Aires, Argentina

Consultorios Médicos Dr. Doreski - PPDS

Buenos Aires, Argentina

Buenos Aires Mácula

Buenos Aires, Argentina

Centro de Investigación y Prevención Cardiovascular

Buenos Aires, Argentina

AES - AS - Glenny Corp. S.A. Buenos Aires

Buenos Aires, Argentina

Higea S.A.

Mendoza, Argentina

DIM Clinica Privada

Ramos Mejía, Argentina

CINME S.A. - Centro de Investigaciones Metabólicas

Recoleta, Argentina

Hospital Provincial Del Centenario

Rosario, Argentina

Princess Alexandra Hospital

Queensland, Queensland, Australia

Flinders Medical Center

Adelaide, South Australia, Australia

Monash Health, Monash Medical Centre

Clayton, Victoria, Australia

Northern Health

Epping, Victoria, Australia

Alfred Hospital

Melbourne, Victoria, Australia

Landeskrankenhaus Hall

Hall in Tirol, Austria

Krankenhaus der Barmherzigen Brüder

Vienna, Austria

Medizinische Universität Wien

Vienna, Austria

Klinikum Wels-Grieskirchen GmbH - Standort Wels

Wels, Austria

UZ Antwerpen

Edegem, Belgium

UZ Gent

Ghent, Belgium

UZ Leuven - PPDS

Leuven, Belgium

University of Calgary

Calgary, Canada

University of Alberta

Edmonton, Canada

Centre Hospitalier de l'Universite de Montreal

Montreal, Canada

Ottawa Hospital

Ottawa, Canada

Diex Recherche - Québec - PPDS

Québec, Canada

Toronto General Hospital

Toronto, Canada

GI Research Institute Foundation

Vancouver, Canada

Centro de Investigación y Prevención Cardiovascular

La Serena, Chile

Pontificia Universidad Católica de Chile

Santiago, Chile

BIOCINETIC Ltda

Santiago, Chile

Clinical Research Chile SpA - PPDS

Valdivia, Chile

Beijing Youan Hospital, Capital Medical University

Beijing, China

Beijing Ditan Hospital, Capital Medical University

Beijing, China

Beijing Friendship Hospital, Capital Medical University

Beijing, China

The First Hospital of Jilin University

Changchun, China

West China Hospital of Sichuan University

Chengdu, China

The Second Affiliated Hospital of Chongqing Medical University

Chongqing, China

Mengchao Hepatobiliary Hospital of Fujian Medical University

Fuzhou, China

The Third Affiliated Hospital, Sun Yat-Sen University

Guangzhou, China

Guizhou Provincial People's Hospital

Guiyang, China

The First Affiliated Hospital of Anhui Medical University

Hefei, China

The First People's Hospital of Yunnan Province

Kunming, China

The Second Hospital of Nanjing

Nanjing, China

Shanghai Jiaotong University School of Medicine, Renji Hospital

Shanghai, China

The First Affiliated Hospital of Xinjiang Medical University

Ürümqi, China

Union Hospital Tongji Medical College Huazhong University of Science and Technology

Wuhan, China

The First Affiliated Hospital of PLA Air Force Medical University

Xi'an, China

The First Affiliated Hospital of Xi'an Jiaotong University

Xi'an, China

The First Affiliated Hospital, Zhejiang University School of Medicine

Zhejiang, China

Henan Provincial People's Hospital

Zhengzhou, China

The Third People's Hospital of Zhenjiang

Zhenjiang, China

Fakultni nemocnice Ostrava

Ostrava, Czechia

RESEARCH Site s.r.o

Pilsen, Czechia

Aarhus Universitetshospital

Aarhus, Denmark

Hôpital Claude Huriez-Lille-1 Place de Verdun

Lille, France

Hospices Civils de Lyon (HCL) - Hopital de la Croix-Rousse

Lyon, France

CHU-Montpellier-Hopital St Eloi

Montipellier, France

Hopital Saint Antoine, Assistance Publique-Hopitaux de Paris

Paris, France

AP-HP Hopital Henri Mondor

Paris, France

CHU de Strasbourg - Nouvel Hôpital Civil

Strasbourg, France

CHRU de Nancy - Hôpitaux de Brabois

Vandœuvre-lès-Nancy, France

Charité Campus Virchow-Klinikum-Augustenburger Platz 1

Berlin, Germany

Universitatsklinikum des Saarlandes

Homburg, Germany

Gastroenterologisch - Hepatologisches MVZ Kiel GmbH

Kiel, Germany

Evangelismos General Hospital

Athens, Greece

University General Hospital of Larissa

Larissa, Greece

General Hospital of Thessaloniki ''Hippokratio''

Thessaloniki, Greece

Prince of Wales Hospital - Hong Kong

Hong Kong, Hong Kong

Queen Mary Hospital - PPDS

Hong Kong, Hong Kong

Princess Margaret Hospital - Hong Kong

Hong Kong, Hong Kong

Semmelweis Egyetem - Sebészeti,

Budapest, Hungary

Somogy Varmegyei Kaposi Mor Oktato Korhaz

Kaposvár, Hungary

Lady Davis Carmel Medical Center

Haifa, Israel

Liver Unit, institute of Gasteroenterology and Liver Diseases

Jerusalem, Israel

Azienda Ospedaliero Universitaria delle Marche -Umberto I G.M. Lancisi G. Salesi

Ancona, Italy

IRCCS Saverio de Bellis-UOSD "Epatopatie"

Castellana Grotte, Italy

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico

Milan, Italy

ASST Santi Paolo Carlo, S.C. Medicina ad Indirizzo Epatologico e Gastroenterologico

Milan, Italy

Azienda Ospedaliero-Universitaria di Modena - Ospedale Civile di Baggiovara

Modena, Italy

Fondazione IRCCS San Gerardo dei Tintori

Monza, Italy

A.O.U.P. Paolo Giaccone , U.O.C di Gastroeneterologia

Palermo, Italy

A.O.U. Pisana, U.O. Epatologia

Pisa, Italy

Ospedale Casa Sollievo Della Sofferenza IRCCS

San Giovanni Rotondo, Italy

Clinica de Higado y Gastroenterologia Integral, S.C.

Cuernavaca, Mexico

PROACTIVE CR MEXICO SA de CV

Irapuato, Mexico

Consultorio Medico - Distrito Federal

Mexico City, Mexico

Centro De Investigacion Y Gastroenterogia, S.C.

México, Mexico

Oaxaca Site Management Organization - Hospital - OSMO - PPDS

Oaxaca City, Mexico

FAICIC

Veracruz, Mexico

ID Clinic Arkadiusz Pisula

Mysłowice, Poland

PlanetMed SP. z. o. o

Wroclaw, Poland

Institutul Clinic Fundeni

Bucharest, Romania

National University Hospital

Singapore, Singapore

Singapore General Hospital (SGH)

Singapore, Singapore

Tan Tock Seng Hospital

Singapore, Singapore

Changi General Hospital

Singapore, Singapore

Pusan National University Hospital

Busan, South Korea

Kyungpook National University Hospital

Daegu, South Korea

Chonnam National University Hospital

Gwangju, South Korea

Seoul National University Bundang Hospital

Seongnam, South Korea

Asan Medical Center

Seoul, South Korea

Korea University Guro Hospital

Seoul, South Korea

Seoul National University Hospital

Seoul, South Korea

Severance Hospital, Yonsei University Health System

Seoul, South Korea

Samsung Medical Center

Seoul, South Korea

The Catholic University of Korea, Seoul St. Mary's Hospital

Seoul, South Korea

Complexo Hospitalario Universitario De Santiago

A Coruña, Spain

Hospital Universitario Fundacion Alcorcon

Alcorcón, Spain

Hospital Universitario Germans Trias i Pujol

Badalona, Spain

Hospital del Mar

Barcelona, Spain

Hospital Universitario Vall d'Hebron-VIHR

Barcelona, Spain

Hospital Clinic de Barcelona

Barcelona, Spain

C.H. Regional Reina Sofia - PPDS

Córdoba, Spain

Hospital Universitario Virgen de la Victoria

Málaga, Spain

Hospital Universitario Marques de Valdecilla

Santander, Spain

Hospital Universitario Virgen del Rocio - PPDS

Seville, Spain

Universitätsspital Bern

Bern, Switzerland

Universitätsspital Zürich

Zurich, Switzerland

Kaohsiung Medical University Hospital

Kaohsiung City, Taiwan

Chang Gung Medical Foundation Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, Taiwan

National Cheng Kung University Hospital

Tainan, Taiwan

National Taiwan University Hospital

Taipei, Taiwan

Chang Gung Memorial Hospital, Linkou

Taoyuan District, Taiwan

Adana City Training and Research Hospital

Adana, Turkey (Türkiye)

Ankara Bilkent City Hospital

Ankara, Turkey (Türkiye)

Gaziantep University Medical Faculty Sahinbey Research and Practice Hospital

Gaziantep, Turkey (Türkiye)

Uludag University Medical Faculty

Görükle, Turkey (Türkiye)

Ege University

Izmir, Turkey (Türkiye)

Katip Celebi University

Karabağlar, Turkey (Türkiye)

Kocaeli University Medical Faculty Hospital

Kocaeli, Turkey (Türkiye)

Mersin Universitesi Tip Fakultesi Hastanesi

Mersin, Turkey (Türkiye)

Marmara University Pendik Training and Research Hospital

Pendik, Turkey (Türkiye)

Rize Recep Tayyip Erdogan University Training and Research Hospital

Rize Merkez, Turkey (Türkiye)

Hull Royal Infirmary

Hull, United Kingdom

East Suffolk and North Essex NHS Foundation Trust, Ipswich Hospital

Ipswich, United Kingdom

The Royal London Hospital

London, United Kingdom

Royal Free Hospital

London, United Kingdom

King's College Hospital

London, United Kingdom

Freeman Hospital

Newcastle upon Tyne, United Kingdom

John Radcliffe Hospital

Oxford, United Kingdom

Sheffield teaching hospital NHS foundation trust

Sheffield, United Kingdom

New Cross Hospital

Wolverhampton, United Kingdom

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NCT06051617


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