RecruitingPhase 3NCT06282575

Efficacy and Safety of Zanidatamab With Standard-of-care Therapy Against Standard-of-care Therapy for Advanced HER2-positive Biliary Tract Cancer

An Open-label Randomized Trial of the Efficacy and Safety of Zanidatamab With Standard-of-care Therapy Against Standard-of-care Therapy Alone for Advanced HER2-positive Biliary Tract Cancer


Sponsor

Jazz Pharmaceuticals

Enrollment

286 participants

Start Date

Jul 19, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of this study is to evaluate the efficacy and safety of Zanidatamab plus CisGem (Cisplatin and Gemcitabine) with or without the addition of a programmed death protein 1/ligand-1 (PD-1/L1) inhibitor (physician's choice of either Durvalumab or Pembrolizumab, where approved under local regulations) as first line of treatment for participants with human epidermal growth factor receptor 2 (HER2)-positive biliary tract cancer.


Eligibility

Min Age: 18 Years

Inclusion Criteria10

  • Histologically- or cytologically-confirmed Biliary Tract Cancer (BTC), including Gallbladder Cancer (GBC), Intrahepatic Cholangiocarcinoma (ICC), or Extrahepatic Cholangiocarcinoma (ECC).
  • Locally advanced unresectable or metastatic BTC and not eligible for curative resection, transplantation, or ablative therapies.
  • Received no more than 2 cycles of systemic therapy which is limited to Cisplatin and Gemcitabine (CisGem) with or without a PD-1/L1 inhibitor (physician's choice of durvalumab or pembrolizumab, where approved under local regulations) for advanced unresectable or metastatic disease.
  • HER2-positive disease (defined as IHC 3+; or IHC 2+/ ISH+) by IHC and in situ Hybridization (ISH) assay (in participants with IHC 2+ tumors) at a central laboratory on new biopsy tissue or archival tissue from the most recent biopsy.
  • Assessable (measurable or non-measurable) disease as defined by Response Evaluation Criteria in Solid Tumors Version 1.1 (RECIST 1.1), per investigator assessment.
  • Male or female ≥ 18 years or age (or the legal age of adulthood per country-specific regulations).
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
  • Adequate organ function
  • Females of childbearing potential must have a negative pregnancy test result.
  • Females of childbearing potential and males with a partner of childbearing potential must be willing to use 2 methods of birth control.

Exclusion Criteria13

  • Prior treatment with a HER2-targeted agent
  • Prior treatment with checkpoint inhibitors, other than durvalumab or pembrolizumab
  • The following BTC histologic subtypes are excluded: small cell cancer, neuroendocrine tumors, lymphoma, sarcoma, mixed tumor histology, and mucinous cystic neoplasms detected in the biliary tract region.
  • Use of systemic corticosteroids.
  • Brain metastases
  • Severe chronic or active infections
  • History of allogeneic organ transplantation.
  • Active or prior autoimmune inflammatory conditions
  • History of interstitial lung disease or non-infectious pneumonitis.
  • Participation in another clinical trial with an investigational medicinal product within the last 3 months.
  • Females who are breastfeeding
  • Any other medical, social, or psychosocial factors that, in the opinion of the investigator, could impact safety or compliance with study procedures.
  • Use of phenytoin

Interventions

DRUGZanidatamab

Administered intravenously (IV)

DRUGCisplatin

Administered intravenously (IV)

DRUGGemcitabine

Administered intravenously (IV)

DRUGPembrolizumab

Administered intravenously (IV)

DRUGDurvalumab

Administered intravenously (IV)


Locations(183)

City of Hope(City of Hope National Medical Center, City of Hope Medical Center)

Duarte, California, United States

Rocky Mountain Cancer Centers, LLP

Lone Tree, Colorado, United States

AdventHealth Hematology and Oncology

Orlando, Florida, United States

Winship Cancer Institute

Atlanta, Georgia, United States

The University of Kansas Cancer Center - Westwood

Westwood, Kansas, United States

Norton Cancer Institute - Audubon

Louisville, Kentucky, United States

Ochsner Clinic Foundation

New Orleans, Louisiana, United States

Tufts Medical Center

Boston, Massachusetts, United States

University of Michigan Hospital

Ann Arbor, Michigan, United States

Henry Ford Health System

Detroit, Michigan, United States

Minnesota Oncology Hematology, P.A.

Maple Grove, Minnesota, United States

Atlantic Health System/Morristown Medical Center

Morristown, New Jersey, United States

Laura and Isaac Perlmutter Cancer Center at NYU Langone - Ambulatory Care Center

New York, New York, United States

Memorial Sloan Kettering Cancer Centers

New York, New York, United States

Saint Francis Cancer Center

Greenville, South Carolina, United States

SCRI Oncology Partners

Nashville, Tennessee, United States

Texas Oncology - DFW

Dallas, Texas, United States

University of Texas Southwestern Medical Center

Dallas, Texas, United States

The Univerrsity of Texas MD Anderson Cancer Center

Houston, Texas, United States

Virginia Commonwealth University, VCU Health

Richmond, Virginia, United States

Hospital Italiano de Buenos Aires

Ciudad Autónoma de Buenos Aires (caba), Buenos Altes, Argentina

Fundación ARS Médica

San Salvador de Jujuy, Jujuy Province, Argentina

Centro de Investigaciónes Clínicas - Clínica Viedma

Viedma, Río Negro Province, Argentina

Hospital Provincial Del Centenario

Rosario, Santa Fe Province, Argentina

Instituto Médico de la Fundación Estudios Clínicos

Rosario, Santa Fe Province, Argentina

CAIPO Centro para la Atención Integral del Paciente Oncológico

San Miguel de Tucumán, Tucumán Province, Argentina

Centro Médico en Oncología Clínica EXELSUS S.R.L

San Miguel de Tucumán, Tucumán Province, Argentina

Centro Médico Privado CEMAIC

Córdoba, Argentina

Imelda VZW

Bonheiden, Antwerpen, Belgium

UZ Antwerpen

Edegem, Antwerpen, Belgium

UZ Leuven

Leuven, Vlaams-Brabant, Belgium

Liga Norte Riograndense Contra O Cancer

Natal, Rio Grande do Norte, Brazil

Hospital de Clinicas de Porto Alegre - HCPA

Porto Alegre, Rio Grande do Sul, Brazil

Irmandade Da Santa Casa de Misericordia de Porto Alegre - ISCMPA

Porto Alegrev, Rio Grande do Sul, Brazil

Fundação Pio XII Hospital de Amor de Barretos

Barretos, São Paulo, Brazil

Fundação Doutor Amaral Carvalho - Hospital Amaral Carvalho

Jaú, São Paulo, Brazil

Fundação Faculdade Regional de Medicina de São José do Rio Preto (FUNFARME)

São José do Rio Preto, São Paulo, Brazil

Hospital Nossa Senhora Da Conceição/Centro Integrado de Pesquisa em Oncologia CIPO-GHC

Porto Alegre, Brazil

Instituto Nacional de Cancer - INCA

Rio de Janeiro, Brazil

London Health Sciences Centre

London, Ontario, Canada

Princess Margaret Cancer Centre - University Health Network

Toronto, Ontario, Canada

Centre Hospitalier de l'Universite de Montreal (CHUM)

Montreal, Quebec, Canada

Servicios Médicos URUMED SpA

Rancagua, Libertador Gen Bernardo O Higgins, Chile

Clinica Puerto Montt

Port Montt, Los Lagos Region, Chile

James Lind Centro de Investigacion del Cancer

Temuco, Región de la Araucanía, Chile

Centro de Investigacion y Especialidades Medicas (CDIEM)

Santiago, Santiago Metropolitan, Chile

Fundación Arturo López Pérez (FALP)

Santiago, Santiago Metropolitan, Chile

Oncovida

Santiago, Santiago Metropolitan, Chile

Biocinetic Ltda

Santiago, Santiago Metropolitan, Chile

Hospital Clinico Universidad de Chile

Santiago, Santiago Metropolitan, Chile

The First Affiliated Hospital of USTC(Anhui Provincial Hospital)

Hefei, Anhui, China

Beijing Cancer Hospital

Beijing, Beijing Municipality, China

The First Hospital of Lanzhou University

Lanzhou, Gansu, China

Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, China

Hunan Provincial People's Hospital

Changsha, Hunan, China

Jilin Cancer Hospital

Changchun, Jilin, China

Shandong Provincial Third Hospital

Jinan, Shandong, China

Sichuan Cancer Hospital

Chengdu, Sichuan, China

West China Hospital Sichuan University

Chengdu, Sichuan, China

Zhongshan Hospital Fudan University

Shanghai, China

Fakultní nemocnice Brno, Interní hematologická a onkologická klinika

Brno, Czechia

Fakultni nemocnice Hradec Kralove, Klinika onkologie a radioterapie

Hradec Králové, Czechia

Fakultni nemocnice v Motole, Onkologicka klinika

Prague, Czechia

Docrates Cancer Center

Helsinki, Finland

Comprehensive Cancer Center, Helsinki University Hospital

Helsinki, Finland

Kuopio University Hospital

Kuopio, Finland

CHU de Toulouse- (Toulouse University Hospital Center)

Toulouse, Cedex 9, France

CHU Besancon

Besançon, Cedex, France

CHU de Bordeaux - Hôpital Haut Leveque

Pessac, Cedex, France

CHU Brest Hôpital de la Cavale Blanche

Brest, France

CHU Estaing

Clermont-Ferrand, France

Hospital Beaujon University

Clichy, France

Hopital Henri Mondor

Créteil, France

CHU Montepellier - Hôpital Saint Eloi

Montpellier, France

CHU Poitiers

Poitiers, France

Institut de Cancérologie de l'Ouest

Saint-Herblain, France

Gustave Roussy

Villejuif, France

Universitätsklinikum Freiburg - Klinik für Innere Medizin II,

Freiburg im Breisgau, Baden-Wurttemberg, Germany

Nationales Centrum für Tumorerkrankungen (NCT) Heidelberg

Heidelberg, Baden-Wurttemberg, Germany

Universitätsklinikum Tübingen - Medizinische Universitätsklinik, Innere Medizin I

Tübingen, Baden-Wuttemberg, Germany

LMU Universitätsklinikum München, Campus Großhadern, Medizinische Klinik und Poliklinik III - Hämatologie und Onkologie

München, Bavaria, Germany

Krankenhaus Nordwest - Institut für Klinisch-Onkologische Forschung (IFK)

Frankfurt am Main, Hesse, Germany

Medizinische Hochschule Hannover - Klinik Fur Gastroenterologie, Hepatologie, Infektiologie und Endokrinologie

Hanover, Nieder-Sachsen, Germany

Technische Universität Dresden Medizinische Fakultät Carl Gustav Carus

Dresden, Saxony, Germany

Universitätsklinikum Schleswig-Holstein - Campus Lübeck, Medizinische Klinik I (MKI)

Lübeck, Schleswig-Holstein, Germany

Charité - Universitätsmedizin Berlin - Campus Virchow Klinikum, Medizinische Klinik mit Schwerpunkt Hamatologie und Tumorimmunologie

Berlin, Germany

Asklepios Tumorzentrum Hamburg, Asklepios Klinik Altona - Onkologie und Palliativmedizin mit Sektionen Hamatologie und Rheumatologie

Hamburg, Germany

KLES Dr Prabhakar Kore Hospital and Medical Research Centre

Belagavi, Karnataka, India

Tata Memorial Hospital

Mumbai, Maharashtra, India

Chopda Medicare & Research Centre Pvt. Ltd - Magnum Heart Institute

Nashik, Maharashtra, India

AIG Hospitals (A Unit of Asian Institute of Gastroenterology)

Hyderabad, Telangana, India

Pi Health Cancer Hospital

Hyderabad, Telangana, India

Mahamana Pandit Madan Mohan Malviya Cancer Centre

Varanasi, Uttar Pradesh, India

Max Super Speciality Hospital - Saket (a unit of Devki Devi foundation)

New Delhi, India

Rajiv Gandhi Cancer Institute And Research Centre

New Delhi, India

Rambam Health Care Campus

Haifa, Israel

The Hadassah University Medical Center, Ein Kerem Hospital

Jerusalem, Israel

Rabin Medical Center, Bellinson Hospital

Petah Tikva, Israel

The Chaim Sheba Medical Center, Tel Hashomer

Ramat Gan, HaMerkaz, Israel

Tel Aviv Sourasky Medical Center (Ichilov)

Tel Aviv, Israel

Azienda Ospedaliero Universitaria di Cagliari Presidio Ospedaliero Duilio Casula

Monserrato, Cagliari, Italy

Instituo di Candiolo, Fondazione del Piemonte per l'Oncologia (IRCCS)

Candiolo, Torino, Italy

IRCCS Ospedale Policlinico San Martino

Genova, Italy

Fondazione IRCCS Istituto Nazionale per lo studio e la cura dei Tumori

Milan, Italy

AOU dell'Universit~ degli Studi della Campania Luigi Vanvitelli

Napoli, Italy

Veneto Institute of Oncology IOV - I.R.C.C.S.

Padua, Italy

Azienda Ospedaliero - Universitaria Pisana

Pisa, Italy

Fondazione Policlinico Universitario Gemelli-IRCCS

Roma, Italy

Istituto Clinico Humanitas

Rozzano, Italy

Azienda Sanitaria Universitaria Friuli Centrale - P.O. S. Maria della Misericordia

Udine, Italy

Azienda Ospedaliera Universitaria Integrata Verona

Verona, Italy

Aichi Cancer Center

Nagoya, Aichi-ken, Japan

Chiba Cancer Center

Chiba, Chiba, Japan

National Cancer Center Hospital East

Kashiwa, Chiba, Japan

National Hospital Organization Shikoku Cancer Center

Matsuyama, Ehime, Japan

National Hospital Organization Kyushu Cancer Center

Fukuoka, Fukuoka, Japan

Hokkaido University Hospital

Sapporo, Hokkaidô, Japan

Kanazawa University Hospital

Kanazawa, Ishikawa-ken, Japan

Kagoshima University Hospital

Kagoshima, Kagoshima-ken, Japan

Kanagawa Cancer Center

Yokohama, Kanagawa, Japan

Kyoto University Hospital

Kyoto, Kyôto, Japan

Mie University Hospital

Tsu, Mie-ken, Japan

Tohoku University Hospital

Sendai, Miyagi, Japan

Niigata University Medical and Dental Hospital

Niigata, Niigata, Japan

Osaka Prefectural Hospital Organization Osaka International Cancer Institute

Osaka, Osaka, Japan

The University of Tokyo Hospital

Bunkyo-ku, Tokyo, Japan

National Cancer Center Hospital

Chuo-Ku, Tokyo, Japan

The Cancer Institute Hospital of Japanese Foundation For Cancer Research

Koto-Ku, Tokyo, Japan

Kyorin University Hospital

Mitaka-shi, Tokyo, Japan

Yamaguchi University Hospital

Ube-Shi, Yamaguchi, Japan

Osaka University Hospital

Suita-Shi, Ôsaka, Japan

Unidade Local de Saude de Almada-Seixal, E.P.E. - Hospital Garcia de Orta

Almada, Portugal

Unidade Local de Saude de Coimbra, EPE - Hospitais da Universidade de Coimbra

Coimbra, Portugal

Unidade Local de Saúde de São José - Hospital de Santo António dos Capuchos

Lisbon, Portugal

Champalimaud Clinical Center

Lisbon, Portugal

Instituto Português de Oncologia Do Porto Francisco Gentil, EPE

Porto, Portugal

Hospital Oncologico, Puerto Rico Medical Center

Rio Piedras, Puerto Rico

Spital Clinic Judetean de Urgenta Bihor

Oradea, Bihor County, Romania

Centrul De Oncologie "SF. Nectarie" S.R.L.

Craiova, Dolj, Romania

Institutul Clinic Fundeni

Bucharest, Romania

Centrul de Oncologie Euroclinic SRL

Iași, Romania

University Clinical Center of Serbia, Clinic for Gastroenterohepatology

Belgrade, Serbia

Military Medical Academy, Clinic for Gastroenterology and Hepatology

Belgrade, Serbia

Oncology Institute of Vojvodina, Internal Oncology Clinic

Kamenitz, Serbia

CHA Bundang Medical Center, CHA University

Bundang-Gu, Seongnam-Si, Gyeonggi-do, South Korea

National Cancer Center

Ilsandong-gu, Goyang-si, Gyeonggi-do, South Korea

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, South Korea

Pusan National University Hospital

Busan, South Korea

Korea University Anam Hospital

Seoul, South Korea

Seoul National University Hospital

Seoul, South Korea

Severance Hospital, Yonsei University Health System

Seoul, South Korea

Hanyang University Seoul Hospital

Seoul, South Korea

Asan Medical Center

Seoul, South Korea

Samsung Medical Center

Seoul, South Korea

Korea University Guro Hospital

Seoul, South Korea

Complejo Hospitalario Universitario de Santiago -Hospital Clinico Universitario de Santiago

Santiago de Compostela, A Coruna, Spain

Vall d'Hebron Institute of Oncology/Hospital Universitari de Vall d'Hebron

Barcelona, Spain

Hospital Universitario Reina Sofia

Córdoba, Spain

Hospital Universitario Fundacion Jimenez Diaz

Madrid, Spain

Hospital Universitario 12 de Octubre

Madrid, Spain

Hospital Universitario La Paz

Madrid, Spain

Hospital Regional Universitario de Malaga

Málaga, Spain

Clinica Universidad de Navarra

Pamplona, Spain

Hospital Universitario Virgen Macarena

Seville, Spain

Hospital Universitario y Politecnico La Fe

Valencia, Spain

Hospital Universitario Miguel Servet

Zaragoza, Spain

Onkologiska mottagningen, Sahlgrenska Universitetssjukhuset

Gothenburg, Sweden

Cancerstudieenheten Huddinge, Karolinska Universitetssjukhuset Huddinge

Huddinge, Sweden

Onkologiska mottagningen, Skånes Universitetssjukhus Malmö

Malmo, Sweden

Kaohsiung Medical University - Chung-Ho Memorial Hospital

Kaohsiung City, Taiwan

Chang Gung Memorial Hospital Kaohsiung Branch of the Chang Gung Medical Foundation

Kaohsiung City, Taiwan

National Cheng Kung University Hospital

Tainan, Taiwan

National Taiwan University Cancer Center

Taipei, Taiwan

Chang Gung Memorial Hospital Linkou Branch of the Chang Gung Medical Foundation

Taoyuan District, Taiwan

Istanbul University Cerrahpasa Medical Faculty Hospital/Clinical Research Center

Istanbul, Fatih, Turkey (Türkiye)

Hacettepe University Cancer Institute

Ankara, Sihhiye, Turkey (Türkiye)

Akdeniz University Medical Faculty Hospital

Antalya, Turkey (Türkiye)

Trakya University Faculty of Medicine

Edirne, Turkey (Türkiye)

Mount Vernon Cancer Centre

London, England, United Kingdom

NHS Foundation Trust Royal Marsden Hospital

London, England, United Kingdom

The Christie NHS Foundation Trust

Manchester, England, United Kingdom

Royal Marsden Hospital NHS Foundation Trust

Surrey, England, United Kingdom

Western General Hospital, Edinburgh Cancer Centre

Edinburgh, Scotland, United Kingdom

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NCT06282575


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