RecruitingPhase 3NCT06382948

Elacestrant + Everolimus in Patients ER+/HER2-, ESR1mut, Advanced Breast Cancer Progressing to ET and CDK4/6i.

A Randomized Phase 3, Double-Blind, Placebo-Controlled Study of Elacestrant Plus Everolimus Versus Elacestrant in Patients With ER+/HER2-, ESR1mut Advanced Breast Cancer Progressing to Endocrine Therapy and CDK4/6 Inhibitors


Sponsor

MedSIR

Enrollment

240 participants

Start Date

Dec 5, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

This trial will study a type of advanced breast cancer (ABC) defined as endocrine receptor (ER)-positive/human epidermal growth factor receptor 2(HER2)-negative and estrogen receptor 1 (ESR1)-mutated. Patients will be treated with elacestrant, a compound that acts as a selective estrogen receptor degrader, and everolimus (or placebo), a kinase inhibitor indicated for the treatment of postmenopausal women with advanced hormone receptor-positive, HER2-negative breast cancer. The main purpose of the study is to analyze the efficacy (to find out how effective a treatment is) of elacestrant plus everolimus therapy in patients who have ER-positive/HER2-negative, ESR1-mutated, ABC progressing to endocrine therapy and cyclin-dependent kinase 4/6 (CDK4/6) inhibitor. The efficacy of elacestrant plus everolimus combination will be determined by assessing the period from elacestrant plus everolimus (or placebo) treatment initiation until to the first occurrence of disease progression, unacceptable toxicity, death, or discontinuation from the study treatment for any other reason, whichever occurs first, defined as progression free survival. Rigorous eligibility criteria based on specific co-morbidities and clinicopathologic features of their disease have been designed to minimize the risk of patients participating in this study. The anticipated favorable clinical benefits of elacestrant combined with everolimus are projected to outweigh the risks of this treatment. This study will be performed in full compliance with International Council for Harmonisation of Technical Requirements for Pharmaceuticals for Human Use (ICH) and all applicable local Good Clinical Practice (GCP) and regulations.


Eligibility

Min Age: 18 Years

Plain Language Summary

Simplified for easier understanding

This trial tests a combination of two targeted drugs — elacestrant and everolimus — for patients with advanced hormone receptor-positive (ER+), HER2-negative breast cancer that carries a specific gene change called an ESR1 mutation, and whose cancer progressed on both hormone therapy and a CDK4/6 inhibitor (two standard treatments). **You may be eligible if...** - You are 18 or older (male or female) - You have advanced ER+, HER2-negative breast cancer with a confirmed ESR1 mutation - Your cancer progressed on prior hormone therapy and a CDK4/6 inhibitor - Pre/perimenopausal patients and men must be on an LHRH agonist (a hormone-lowering injection) for at least 28 days before starting - Your organ function is adequate **You may NOT be eligible if...** - You have already had more lines of chemotherapy or targeted therapy than allowed by the protocol - Your tumor does not have an ESR1 mutation - You are pregnant or breastfeeding - You have serious uncontrolled medical conditions Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGEverolimus

Patients will receive 7.5 mg of everolimus orally once daily.

DRUGElacestrant

Patients will receive elacestrant 345 mg orally once daily

DRUGPlacebo

Patients will receive placebo orally once daily

DRUGAuxiliary Medicinal Product - Dexamethasone

10 mL of alcohol-free dexamethasone 0.5 mg per 5 mL mouthwashes (swish for 2 min and spit, four times daily for 8 weeks). After 8 weeks, dexamethasone mouthwash could be continued for up to eight additional weeks at the discretion of the clinician and patient. Used for prevention of treatment-induced stomatitis.

DRUGAuxiliary Medicinal Product - Luteinizing hormone-releasing hormone (LHRH) analogues

According to clinical practice (for premenopausal/perimenopausal patients and male patients in both treatment arms). Used to suppress estrogen production.


Locations(99)

Medizinische Universität Innsbruck

Innsbruck, Austria

Ordensklinikum Linz Barmherzige Schwestern

Linz, Austria

Ordination Priv.-Doz. Dr. Michael Hubalek

Schwaz, Austria

Medical University of Vienna

Vienna, Austria

Tacchini Instituto de Pesquisa

Bento Gonçalves, Brazil

Hospital Cachoeiro de Itapemirim

Cachoeiro de Itapemirim, Brazil

Catarina Pesquisa Clínica - Neoplasias Litoral

Itajaí, Brazil

UPCO - Hospital de Clinicas de Porto Alegre

Porto Alegre, Brazil

NOB Ondina

Salvador, Brazil

Masaryk Memorial Cancer Institute

Brno, Czechia

Multiscan Nemocnice Horovice

Hořovice, Czechia

University Hospital Olomouc

Olomouc, Czechia

General University Hospital Prague

Prague, Czechia

Tomas Bata Regional Hospital in Zlin

Zlín, Czechia

Polyclinique Bordeaux Nord Aquitaine

Bordeau, France

Institut Bergonié Bordeaux

Bordeaux, France

Centre Georges François Leclerc

Dijon, France

Centre Hospitalier de Limoges

Limoges, France

CHU Lyon Sud

Lyon, France

Institut Paoli Calmettes

Marseille, France

APHP Tenon

Paris, France

Hospital prive des Cotes d'Amor

Plérin, France

CHU Saint Etienne

Saint-Priest-en-Jarez, France

IUCT Oncopole

Toulouse, France

Institute de Cancerologie de Lorraine - Nancy

Vandœuvre-lès-Nancy, France

MVZ Klinikum Aschaffenburg

Aschaffenburg, Germany

Hämatologie-Onkologie im Zentrum MVZ GmbH

Augsburg, Germany

Städtisches Klinikum Dessau

Dessau, Germany

Universitätsklinikum Dusseldorf

Düsseldorf, Germany

Universitätsklinikum Essen

Essen, Germany

MVZ II der Niels Stensen Kliniken

Georgsmarienhütte, Germany

Klinikum Worms - Frauenklinik

Worms, Germany

University General Hospital Alexandroupoli

Alexandroupoli, Greece

251 Air Force General Hospital

Athens, Greece

Aretaeio Hospital

Athens, Greece

Attikon University Hospital

Athens, Greece

Metropolitan General Hospital 4th department

Athens, Greece

University General Hospital of Heraklion

Heraklion, Greece

University General Hospital of Larissa

Larissa, Greece

General University Hospital of Patras

Pátrai, Greece

Metropolitan Hospital Greece 1st department

Piraeus, Greece

EU Interbalkan Medical Center

Thessaloniki, Greece

Cliniche Gavazzeni

Bergamo, Italy

Azienda Ospedaliero-Universitaria (AOU) di Cagliari

Cagliari, Italy

Aou Careggi

Florence, Italy

IRCCS Ospedale Policlinico San Martino

Genova, Italy

Ospedali Riuniti Livorno

Livorno, Italy

Instituto Europeo di Oncologia

Milan, Italy

AOU Policilinico Modena

Modena, Italy

IRCCS San Gerardo

Monza, Italy

Fondazione Pascale

Naples, Italy

Azienda Ospedaliero- Universitaria Maggiore Della Carita

Novara, Italy

Oncologia Medica AUSL Piacenza

Piacenza, Italy

Policlinico A. Gemelli IRCCS

Roma, Italy

Hospital Universitari Dexeus

Barcelona, Barcelona, Spain

Centro Oncológico de Galicia

A Coruña, Spain

Complejo Hospitalario Universitario de Santiago (CHUS)

A Coruña, Spain

Hospital General Universitario Dr. Balmis (Alicante)

Alicante, Spain

Hospital Universitario San Juan de Alicante

Alicante, Spain

Institut Català d' Oncologia Badalona (ICO)

Badalona, Spain

Hospital Clínic i Provincial de Barcelona

Barcelona, Spain

Hospital del Mar

Barcelona, Spain

Hospital Universitari Vall D'Hebron

Barcelona, Spain

Hospital Universitario de Basurto

Bilbao, Spain

Hospital Universitario de Burgos

Burgos, Spain

Hospital Provincial de Castellón

Castellon, Spain

Hospital San Pedro de Alcántara

Cáceres, Spain

Hospital Universitario Clínico San Cecilio de Granada

Granada, Spain

Complejo Hospitalario de Jaén

Jaén, Spain

Hospital Universitario Insular de Gran Canaria

Las Palmas de Gran Canaria, Spain

Hospital Universitario de León

León, Spain

Hospital Universitario Arnau de Vilanova de Lleida

Lleida, Spain

Hospital Beata María Ana

Madrid, Spain

Hospital Universitario Doce de Octubre

Madrid, Spain

Hospital Universitario La Paz

Madrid, Spain

Hospital Universitario Puerta de Hierro Majadahonda

Madrid, Spain

Hospital Universitario Ramón y Cajal

Madrid, Spain

Hospital Universitario Sanchinarro-START-CIOCC

Madrid, Spain

MD Anderson Cancer Center Madrid

Madrid, Spain

Hospital Clínico Universitario Virgen de la Arrixaca

Murcia, Spain

Hospital Universitari Son Espases

Palma de Mallorca, Spain

Hospitalario Universitario de Navarra

Pamplona, Spain

Hospital Universitario de Canarias

Santa Cruz de Tenerife, Spain

Hospital Quirónsalud Sagrado Corazón

Seville, Spain

Hospital Universitario Virgen del Rocío

Seville, Spain

Hospital Universitario Virgen Macarena

Seville, Spain

Hospital Universitari Sant Joan de Reus

Tarragona, Spain

Hospital Universitario Marqués de Valdecilla

Valdecilla, Spain

Consorci Hospital General Universitari de València

Valencia, Spain

Hospital Arnau de Vilanova de Valencia

Valencia, Spain

Hospital Clínico Universitario de Valencia

Valencia, Spain

Hospital Universitario La Ribera - Alzira

Valencia, Spain

Hospital Clínico Universitario Lozano Blesa

Zaragoza, Spain

Western General Hospital

Edinburgh, United Kingdom

Barts Health NHS Trust

London, United Kingdom

Genesis Care Oxford

Oxford, United Kingdom

Royal Surrey County Hospital

Surrey Quays, United Kingdom

Royal Cornwall Hospital NHS Trust

Truro, United Kingdom

Genesis Cancer Care UK

Waterlooville, United Kingdom

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NCT06382948


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