RecruitingNCT06410976

Prospective Clinical Assessment Study in Children With Hypochondroplasia

Prospective Clinical Assessment Study in Children With Hypochondroplasia: ACCEL


Sponsor

QED Therapeutics, a BridgeBio company

Enrollment

150 participants

Start Date

Jun 5, 2024

Study Type

OBSERVATIONAL

Conditions

Summary

This is a long-term, multicenter, non-interventional study of children ages 2.5 to \<17 years with hypochondroplasia (HCH).


Eligibility

Min Age: 30 MonthsMax Age: 16 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a new treatment for people with hypochondroplasia. The study is currently recruiting participants at 25 locations. People eligible for this study include aged 30 Months to 16 Years.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Locations(25)

UCSF Benioff Children's Hospital

Oakland, California, United States

Childrens Hospital Colorado

Aurora, Colorado, United States

Children's National Hospital

Washington D.C., District of Columbia, United States

Johns Hopkins School of Medicine

Baltimore, Maryland, United States

University of Missouri

Columbia, Missouri, United States

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Vanderbilt University Medical Center

Nashville, Tennessee, United States

University of Wisconsin Madison - Waisman Center Bone Dysplasia Clinic

Madison, Wisconsin, United States

Murdoch Children's Research Institute - The Royal Children's Hospital Melbourne

Parkville, Victoria, Australia

London Health Sciences Centre - Children's Hospital of Western Ontario

London, Ontario, Canada

Children's Hospital of Eastern Ontario Research Institute

Ottawa, Ontario, Canada

Université de Montréal - Centre Hospitalier Universitaire Sainte-Justine

Montreal, Quebec, Canada

Hôpital Femme Mère Enfant HCL

Bron, France

Hôpital Necker-Enfants Malades

Paris, France

Centre Hospitalier Universitaire (CHU) de Toulouse - Hôpital des Enfants

Toulouse, France

Haukeland University Hospital

Bergen, Norway

Paediatric Clinical Research Unit at Oslo University Hospital

Oslo, Norway

Hospital Pediátrico de Coimbra

Coimbra, Portugal

KK Women's and Children's Hospital

Singapore, Singapore

Unidad de Cirugía Artroscopica, Hopsital MIKS

Vitoria-Gasteiz, Spain

Astrid Lindgren Children's Hospital

Solna, Sweden

The Portland Hospital for Women and Children

London, England, United Kingdom

Manchester University

Manchester, England, United Kingdom

Sheffield Children's NHS Foundation Trust

Sheffield, England, United Kingdom

Glasgow Clinical Research Facility, Queen Elizabeth University Hospital

Glasgow, Scotland, United Kingdom

View Full Details on ClinicalTrials.gov

For the most up-to-date information, visit the official listing.

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NCT06410976


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