RecruitingPhase 2NCT06414954

Safety and Efficacy of 3 Dose Levels of NMD670 in Adult Patients With Myasthenia Gravis

A Phase 2b, Randomised, Double-Blind, Placebo-Controlled Study to Evaluate the Efficacy, Safety, and Tolerability of 3 Dose Levels of NMD670 Over 21 Days in Adult Patients With AChR/MuSK-Ab+ Myasthenia Gravis


Sponsor

NMD Pharma A/S

Enrollment

84 participants

Start Date

May 16, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

This Phase 2 proof-of-concept, dose range finding study aims to evaluate the safety and efficacy of 3 dose levels of NMD670 vs placebo in adult patients with MG with antibodies against AChR or MuSK, administered twice a day (BID) for 21 days.


Eligibility

Min Age: 18 Years

Inclusion Criteria7

  • Participant must be a male or female being 18 or more, at the time of signing the informed consent
  • Diagnosis of MG, MGFA class II, III or IV
  • Documented positive AChR or MuSK antibody test.
  • Participant must be able to swallow tablets
  • Body mass index between 18 and 35 kg/m2, inclusive, at screening, and with a minimum weight of 40 kg
  • Contraceptive use by men and women must be consistent with local regulations regarding the methods of contraception for those participating in clinical studies
  • Participant is capable of and has given signed informed consent

Exclusion Criteria5

  • Known medical or psychological condition(s) or risk factor that, in the opinion of the Investigator, might interfere with the patient's full participation in the study, pose any additional risk for the patient, or confound the assessment of the patient or outcome of the study
  • Participants with other significant clinical and/or laboratory safety findings that may interfere with the conduction or interpretation of the study
  • Participants that received treatment with an investigational medical product within 30 days or 5 half-lives of the medication, whichever is longer prior to Day 1
  • Participants with history of poor compliance with relevant MG therapy
  • Female patients who plan to become pregnant during the study or are currently pregnant or breastfeeding

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Interventions

DRUGNMD670

Tablets taken twice a day for 21 days

DRUGPlacebo

Tablets taken twice a day for 21 days


Locations(39)

Profound Research LLC

Carlsbad, California, United States

University of California Irvine Medical Center

Irvine, California, United States

University of Colorado Neuromuscular Division

Aurora, Colorado, United States

SFM Clinical Research, LLC

Boca Raton, Florida, United States

Neuromuscular Research Division | University of South Florida

Tampa, Florida, United States

Augusta University, Neuroscience Center

Augusta, Georgia, United States

NextGen Precision Health

Columbia, Missouri, United States

The University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

The Ohio State University

Columbus, Ohio, United States

University of Oregon

Portland, Oregon, United States

Semmes Murphey Clinic

Memphis, Tennessee, United States

UZ Leuven

Leuven, Belgium

Aarhus University Hospital

Aarhus, Denmark

Rigshospitalet University of Copenhagen

Copenhagen, Denmark

Centre de référence des maladies neuromusculaires AOC-CHU de Bordeaux - Hôpital Pellegrin

Bordeaux, France

Centre de Référence des Maladies Neuromusculaires et de la SLA

Marseille, France

Centre Hospitalier Universitaire de Nantes - Hôtel Dieu Centre de Référence des Maladies Neuromusculaires Rares -

Nantes, France

CHU de Nice

Nice, France

Unité de Recherche Clinique NeuroSciences

Nice, France

JSC Curatio

Tbilisi, Georgia

LTD David Tatishvili Health Center

Tbilisi, Georgia

Ltd New Hospitals

Tbilisi, Georgia

ASST Papa Giovanni XXIII (Azienda Ospedaliera Papa Giovanni XXIII)

Bergamo, Italy

IRCCS Istituo delle Scienze neurologiche di Bologna, UOC Clinica neurologica Ospedale

Bologna, Italy

IRCCS Ospedale Policlinico San Martino

Genova, Italy

IRCCS Fondazione Istituto Neurologico Carlo Besta, Dipartimento di Ricerca e Sviluppo clinico

Milan, Italy

DIMER, IRCCS, Ospedale San Raffaele

Milan, Italy

Centro Sclerosi Multipla Napoli - AOU Vanvitelli

Naples, Italy

AOU Pisana

Pisa, Italy

Azienda Ospedaliera Sant'Andrea - Universita di Roma La Sapienza

Roma, Italy

Leiden Universitair Medisch Centrum (LUMC)

Leiden, Netherlands

Neurologia Śląska Centrum Medyczne

Katowice, Poland

Szpital Specjalistyczny im. Ludwika Rydygiera w Krakowie sp.z o.o

Krakow, Poland

Centrum Medyczne Hope Clinic

Lublin, Poland

Galen Clinic

Lublin, Poland

Centrum Medyczne Neuro Protect

Warsaw, Poland

University Clinical Center of Serbia, Neurology Clinic

Belgrade, Serbia

University Clinical Center Nis, Neurology Clinic

Niš, Serbia

Hospìtal Universitari Vall d'Hebrón

Barcelona, Spain

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NCT06414954


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