RecruitingPhase 3NCT06456346

Bomedemstat vs Hydroxyurea for Essential Thrombocythemia (MK-3543-007)

A Phase 3, Randomized, Double-blind, Active-Comparator-Controlled Clinical Study to Evaluate the Efficacy and Safety of Bomedemstat (MK-3543) Versus Hydroxyurea in Cytoreductive Therapy Naïve Essential Thrombocythemia Participants


Sponsor

Merck Sharp & Dohme LLC

Enrollment

300 participants

Start Date

Jul 16, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of this study is to evaluate the efficacy and safety of bomedemstat compared with hydroxyurea in cytoreductive therapy naïve essential thrombocythemia (ET) participants for whom cytoreductive therapy is indicated. Its primary objective is to compare bomedemstat to hydroxyurea with respect to durable clinicohematologic response (DCHR). The primary hypothesis is that bomedemstat is superior to hydroxyurea with respect to DCHR.


Eligibility

Min Age: 18 Years

Inclusion Criteria6

  • Diagnosis of Essential Thrombocythemia (ET) based on World Health Organization Criteria for myeloproliferative neoplasms, and an indication for cytoreductive therapy regardless of age or risk status
  • Has a centrally assessed bone marrow fibrosis score of Grade 0 or Grade 1, as per a modified version of the European Consensus Criteria for Grading Myelofibrosis
  • Has received no prior cytoreductive treatment for their ET
  • Human Immunodeficiency Virus (HIV)-infected participants have well controlled HIV on antiretroviral therapy
  • Participants who are Hepatitis B surface antigen (HBsAg) positive are eligible if they have received Hepatitis B Virus (HBV) antiviral therapy for at least 4 weeks and have undetectable HBV viral load
  • Participants with history of Hepatitis C Virus (HCV) infection are eligible if HCV viral load is undetectable

Exclusion Criteria5

  • History of any illness/impairment of gastrointestinal function that might interfere with drug absorption
  • History of a malignancy, unless potentially curative treatment has been completed with no evidence of malignancy for 2 years
  • HIV-infected participants with a history of Kaposi's sarcoma and/or Multicentric Castleman's Disease
  • Has an active infection requiring systemic therapy
  • Has had a major surgery \<4 weeks prior to first dose of study intervention or has not recovered from side effects of major surgery \>4 weeks prior to first dose

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Interventions

DRUGBomedemstat

Oral capsule

DRUGHydroxyurea

Oral capsule

DRUGBomedemstat placebo

Oral capsule placebo

DRUGHydroxyurea placebo

Oral capsule placebo


Locations(166)

Palo Verde Cancer Specialists ( Site 0052)

Glendale, Arizona, United States

Los Angeles Cancer Network ( Site 0025)

Glendale, California, United States

Stanford Cancer Center ( Site 0024)

Palo Alto, California, United States

Exempla Lutheran Medical Center ( Site 0014)

Golden, Colorado, United States

Yale University School of Medicine ( Site 0051)

New Haven, Connecticut, United States

Parkview Research Center at Parkview Regional Medical Center ( Site 0006)

Fort Wayne, Indiana, United States

University of Michigan ( Site 0003)

Ann Arbor, Michigan, United States

Optum Care Cancer Center ( Site 0053)

Las Vegas, Nevada, United States

Levine Cancer Institute ( Site 0009)

Charlotte, North Carolina, United States

Duke University Health System (DUHS) ( Site 0012)

Durham, North Carolina, United States

Wake Forest Baptist Health-Internal Medicine, Section on Hematology & Oncology ( Site 0013)

Winston-Salem, North Carolina, United States

The Ohio State University Wexner Medical Center ( Site 0028)

Columbus, Ohio, United States

Oregon Health & Science University ( Site 0018)

Portland, Oregon, United States

University of Texas MD Anderson Cancer Center ( Site 0026)

Houston, Texas, United States

University of Texas Health Science Center at San Antonio ( Site 0021)

San Antonio, Texas, United States

University of Virginia ( Site 0020)

Charlottesville, Virginia, United States

VCU Health Adult Outpatient Pavillion ( Site 0008)

Richmond, Virginia, United States

Hospital Universitario Austral ( Site 0101)

Pilar, Buenos Aires, Argentina

Hospital Italiano de Buenos Aires ( Site 0102)

ABB, Buenos Aires F.D., Argentina

C.I.C.E. 9 de Julio ( Site 0104)

San Miguel de Tucumán, Tucumán Province, Argentina

Clínica de Nefrología, Urología y Enfermedades Cardiovasculares ( Site 0105)

Santa Fe, Argentina

Westmead Hospital ( Site 0201)

Westmead, New South Wales, Australia

Royal Adelaide Hospital-Haematology Clinical Trials Unit ( Site 0203)

Adelaide, South Australia, Australia

Monash Health-Haematology Research ( Site 0202)

Clayton, Victoria, Australia

Austin Health-Cancer Clinical Trials Centre ( Site 0206)

Heidelberg, Victoria, Australia

Royal Perth Hospital-Haematology ( Site 0204)

Perth, Western Australia, Australia

Ordensklinikum Linz GmbH Elisabethinen ( Site 0562)

Linz, Upper Austria, Austria

Arthur J.E. Child Comprehensive Cancer Centre ( Site 0038)

Calgary, Alberta, Canada

Centre Intégré de Santé et de Services Sociaux de la Montérégie-Centre ( Site 0037)

Greenfield Park, Quebec, Canada

IC La Serena Research ( Site 0150)

La Serena, Coquimbo Region, Chile

FALP-UIDO ( Site 0148)

Santiago, Region M. de Santiago, Chile

Clínica Inmunocel ( Site 0147)

Santiago, Region M. de Santiago, Chile

Clínica Alemana de Santiago ( Site 0143)

Santiago, Region M. de Santiago, Chile

Bradfordhill-Clinical Area ( Site 0142)

Santiago, Region M. de Santiago, Chile

Biocenter ( Site 0149)

Concepción, Región del Biobío, Chile

The First Afflilated Hospital of Bengbu Medical College ( Site 0651)

Bengbu, Anhui, China

Anhui Provincial Hospital ( Site 0657)

Hefei, Anhui, China

Peking University Third Hospital-Hematology ( Site 0659)

Beijing, Beijing Municipality, China

Chinese Academy of medical science, Peking Union Medical College Hospital(Dongdan) ( Site 0675)

Beijing, Beijing Municipality, China

Chongqing University Cancer Hospital ( Site 0666)

Chongqing, Chongqing Municipality, China

The Second Affiliated Hospital of Fujian Medical University ( Site 0671)

Quanzhou, Fujian, China

The First Affiliated hospital of Xiamen University ( Site 0658)

Xiamen, Fujian, China

Sun Yat-sen Memorial Hospital, Sun Yat-sen University-hematology department ( Site 0668)

Guangzhou, Guangdong, China

Southern Medical University Nanfang Hospital-Department of Hematopathology ( Site 0655)

Guangzhou, Guangdong, China

The Second Afilliated Hospital of Hebei Medical University ( Site 0650)

Shijiazhuang, Hebei, China

The First Hospital of Hebei Medical University ( Site 0649)

Shijiazhuang, Hebei, China

Henan Cancer Hospital-hematology department ( Site 0644)

Zhengzhou, Henan, China

Union Hospital Tongji Medical College Huazhong University of Science and Technology ( Site 0642)

Wuhan, Hubei, China

The First Affiliated Hospital of Soochow University ( Site 0676)

Suzhou, Jiangsu, China

The First affiliated hospital of Nanchang University (Xianghu campus) ( Site 0645)

Nanchang, Jiangxi, China

The First Hospital of Jilin University-Hematology ( Site 0672)

Changchun, Jilin, China

Shaanxi provincial people's hospital ( Site 0652)

Xi'an, Shaanxi, China

Jinan Central Hospital ( Site 0667)

Jinan, Shandong, China

Zhongshan Hospital,Fudan University-Hematology ( Site 0674)

Shanghai, Shanghai Municipality, China

Huashan Hospital, Fudan University ( Site 0669)

Shanghai, Shanghai Municipality, China

West China Hospital, Sichuan University ( Site 0661)

Chengdu, Sichuan, China

Institute of hematology&blood disease hospital-Hematology ( Site 0641)

Tianjin, Tianjin Municipality, China

The first Affiliated Hospital, Zhejiang University School of Medicine ( Site 0646)

Hangzhou, Zhejiang, China

Zhejiang University School of Medicine-The Fourth Affiliated Hospital ( Site 0662)

Yiwu, Zhejiang, China

Fundacion Colombiana de Cancerología Clinica Vida ( Site 0164)

Medellín, Antioquia, Colombia

Los Cobos Medical Center ( Site 0165)

Bogotá, Bogota D.C., Colombia

IMAT S.A.S ( Site 0162)

Montería, Departamento de Córdoba, Colombia

Rigshospitalet-Hematology - CTU ( Site 0321)

Copenhagen, Capital Region, Denmark

Aarhus Universitetshospital, Skejby-Blodsygdomme ( Site 0324)

Aarhus, Central Jutland, Denmark

Roskilde Sygehus-Department of Hematology ( Site 0323)

Roskilde, Region Sjælland, Denmark

Odense Universitetshospital-Department of Hematology ( Site 0325)

Odense C, Region Syddanmark, Denmark

Centre Hospitalier Universitaire de Nice - Hôpital l'Archet-Hematology ( Site 0349)

Nice, Alpes-Maritimes, France

CHU Bordeaux Haut-Leveque-service de mèdecine interne et maladies infectieuses ( Site 0346)

Pessac, Aquitaine, France

Hôpital de la Conception ( Site 0351)

Marseille, Bouches-du-Rhone, France

Institut Universitaire du Cancer Toulouse - Oncopole - CHU de TOULOUSE ( Site 0352)

Toulouse, Haute-Garonne, France

Centre Hospitalier Universitaire de Limoges - Hôpital Dupuytren ( Site 0344)

Limoges, Haute-Vienne, France

Centre Hospitalier Régional Universitaire de Tours - Hôpital-Hématologie et Thérapie Cellulaire ( Site 0342)

Tours, Indre-et-Loire, France

Centre Hospitalier Universitaire de Nantes - L' Hopital l'hôtel-Dieu ( Site 0347)

Nantes, Pays de la Loire Region, France

centre hospitalier lyon sud ( Site 0343)

Pierre-Bénite, Rhone, France

HENRI MONDOR HOSPITAL ( Site 0348)

Créteil, Val-de-Marne, France

Hopital Saint-Louis ( Site 0341)

Paris, France

VK&K Studien GbR ( Site 0370)

Landshut, Bavaria, Germany

Medizinische Hochschule Hannover ( Site 0371)

Hanover, Lower Saxony, Germany

Universitätsklinikum Aachen ( Site 0367)

Aachen, North Rhine-Westphalia, Germany

Universitaetsklinikum Essen ( Site 0366)

Essen, North Rhine-Westphalia, Germany

Universitätsmedizin Johannes Gutenberg Universität Mainz-3. Medizinische Klinik und Poliklinik ( Site 0365)

Mainz, Rhineland-Palatinate, Germany

Universitätsklinikum Halle ( Site 0361)

Halle, Saxony-Anhalt, Germany

Universitätsklinikum Jena-Klinik für Innere Medizin II, Abt. Hämatologie und Internistische Onkolog ( Site 0364)

Jena, Thuringia, Germany

Charité Universitaetsmedizin Berlin - Campus Mitte ( Site 0369)

Berlin, Germany

Queen Mary Hospital ( Site 0221)

Hksar, Hong Kong

Szegedi Tudományegyetem Szent-Györgyi Albert Klinikai Központ-Belgyógyászati Klinika ( Site 0407)

Szeged, Csongrád megye, Hungary

Petz Aladar Egyetemi Oktato Korhaz-Hematológia ( Site 0405)

Győr, Győr-Moson-Sopron, Hungary

Somogy Vármegyei Kaposi Mór Oktató Kórház-Haematológiai osztály ( Site 0406)

Kaposvár, Somogy County, Hungary

Szabolcs-Szatmár-Bereg Megyei Kórházak és Egyetemi Oktatókór-Haematológia osztály ( Site 0404)

Nyíregyháza, Szabolcs-Szatmár-Bereg, Hungary

Debreceni Egyetem Klinikai Kozpont-Belgyógyászati Klinika (Haematologia) ( Site 0402)

Debrecen, Hungary

Soroka Medical Center ( Site 0427)

Beersheba, Israel

Rambam Health Care Campus ( Site 0429)

Haifa, Israel

Carmel Hospital ( Site 0426)

Haifa, Israel

Hadassah Medical Center ( Site 0424)

Jerusalem, Israel

Galilee Medical Center ( Site 0431)

Nahariya, Israel

Rabin Medical Center ( Site 0425)

Petah Tikva, Israel

Sheba Medical Center ( Site 0428)

Ramat Gan, Israel

Sourasky Medical Center ( Site 0422)

Tel Aviv, Israel

Yitzhak Shamir Medical Center. ( Site 0421)

Ẕerifin, Israel

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico ( Site 0447)

Milan, Lombardy, Italy

Azienda Ospedaliera Universitaria Careggi ( Site 0441)

Florence, Tuscany, Italy

Azienda Ospedaliero-Universitaria SS. Antonio e Biagio e Cesare Arrigo ( Site 0443)

Alessandria, Italy

IRCCS Azienda Ospedaliero-Universitaria di Bologna, Policlinico di Sant'Orsola ( Site 0446)

Bologna, Italy

Fondazione IRCCS Policlinico San Matteo-Oncology ( Site 0444)

Pavia, Italy

Fondazione Policlinico Universitario Agostino Gemelli IRCCS - Università Cattolica del Sacro Cuore ( Site 0445)

Roma, Italy

Ospedale di Circolo e Fondazione Macchi Varese ( Site 0442)

Varese, Italy

Fujita Health University Hospital ( Site 0613)

Toyoake, Aichi-ken, Japan

Ehime University Hospital ( Site 0612)

Tōon, Ehime, Japan

Hokkaido University Hospital ( Site 0601)

Sapporo, Hokkaido, Japan

Kobe City Medical Center General Hospital ( Site 0603)

Kobe, Hyōgo, Japan

Kanazawa University Hospital ( Site 0614)

Kanazawa, Ishikawa-ken, Japan

Mie University Hospital ( Site 0615)

Tsu, Mie-ken, Japan

National Hospital Organization Sendai Medical Center ( Site 0617)

Sendai, Miyagi, Japan

Kansai Medical University Hospital ( Site 0607)

Hirakata, Osaka, Japan

Kindai University Hospital ( Site 0600)

Sakai, Osaka, Japan

Juntendo University Hospital ( Site 0611)

Bunkyo-ku, Tokyo, Japan

University of Yamanashi Hospital ( Site 0606)

Chūō, Yamanashi, Japan

Kyushu University Hospital ( Site 0605)

Fukuoka, Japan

Fukushima Medical University Hospital ( Site 0616)

Fukushima, Japan

University of Miyazaki Hospital ( Site 0609)

Miyazaki, Japan

Okayama University Hospital ( Site 0604)

Okayama, Japan

Nippon Medical School Hospital ( Site 0608)

Tokyo, Japan

Medivest Centro de Investigación Integral ( Site 0183)

Chihuahua City, Chihuahua, Mexico

Higiea Oncologia ( Site 0184)

Mexico City, Mexico City, Mexico

Centro de Investigacion Clinica de Oaxaca ( Site 0181)

Oaxaca City, Oaxaca, Mexico

Samodzielny Publiczny Szpital Kliniczny nr 1 w Lublinie-Oddział Hematoonkologii, Transplantacji Szp ( Site 0463)

Lublin, Lublin Voivodeship, Poland

Pratia Onkologia Katowice ( Site 0461)

Katowice, Silesian Voivodeship, Poland

Swietokrzyskie Centrum Onkologii, Samodzielny Publiczny Zakl-Klinika Hematologii i Transplantacji S ( Site 0466)

Kielce, Świętokrzyskie Voivodeship, Poland

Hospital Germans Trias i Pujol-Instituto Catalán de Oncología de Badalona ( Site 0490)

Badalona, Barcelona, Spain

Hospital Universitario Marqués de Valdecilla-Haematology ( Site 0486)

Santander, Cantabria, Spain

HOSPITAL CLÍNIC DE BARCELONA ( Site 0481)

Barcelona, Catalonia, Spain

Institut Català d'Oncologia - L'Hospitalet ( Site 0482)

L'Hospitalet de Llobregat, Catalonia, Spain

Clinica Universidad de Navarra-Hematology Department ( Site 0485)

Madrid, Madrid, Comunidad de, Spain

Hospital Universitario Ramón y Cajal-Hematology ( Site 0484)

Madrid, Madrid, Comunidad de, Spain

Hospital Costa del Sol-Hematology Service ( Site 0493)

Marbella, Malaga, Spain

Hospital Universitari Vall d'Hebron-Departamento de Oncologia- VHIO ( Site 0489)

Barcelona, Spain

Hospital Universitario 12 de Octubre ( Site 0494)

Madrid, Spain

Hospital Universitario de Salamanca - Complejo Asistencial Universitario de Salamanca-Hematology ( Site 0488)

Salamanca, Spain

Skånes Universitetssjukhus Lund-Department of Hematology ( Site 0544)

Lund, Skåne County, Sweden

Karolinska Universitetssjukhuset Huddinge ( Site 0541)

Huddinge, Stockholm County, Sweden

Akademiska sjukhuset ( Site 0545)

Uppsala, Uppsala County, Sweden

Sahlgrenska Universitetssjukhuset-Department of hematology and coagulation ( Site 0543)

Gothenburg, Västra Götaland County, Sweden

Universitetssjukhuset Örebro ( Site 0542)

Örebro, Örebro County, Sweden

Chang Gung Memorial Hospital- Chiayi ( Site 0242)

Chiayi City, Chiayi, Taiwan

National Cheng Kung University Hospital-Clinical Trial Center ( Site 0245)

Tainan, Taiwan

National Taiwan University Hospital ( Site 0241)

Taipei, Taiwan

Chang Gung Medical Foundation-Linkou Branch ( Site 0243)

Taoyuan District, Taiwan

Ege Universitesi Hastanesi ( Site 0503)

Bornova, İzmir, Turkey (Türkiye)

Dr. Abdurrahman Yurtaslan Ankara Onkoloji Egitim ve Arastırma Hastanesi-Hemotology ( Site 0510)

Ankara, Turkey (Türkiye)

Hacettepe Universite Hastaneleri-Department of Hematology ( Site 0505)

Ankara, Turkey (Türkiye)

Ankara Bilkent Şehir Hastanesi-Medical Oncology ( Site 0502)

Ankara, Turkey (Türkiye)

Ankara UTF Cebeci Arastırma ve Uygulama Hastanesi ( Site 0511)

Ankara, Turkey (Türkiye)

Antalya Egitim ve Arastırma Hastanesi ( Site 0508)

Antalya, Turkey (Türkiye)

Trakya University Medical Faculty Hospital-Hematology ( Site 0501)

Edirne, Turkey (Türkiye)

Medipol Mega Universite Hastanesi ( Site 0504)

Istanbul, Turkey (Türkiye)

Kocaeli Üniversitesi-Hematology ( Site 0506)

Kocaeli, Turkey (Türkiye)

Ondokuz Mayıs Universitesi-hematology ( Site 0507)

Samsun, Turkey (Türkiye)

Glan Clwyd Hospital ( Site 0528)

Bodelwyddan, Denbighshire, United Kingdom

Gloucestershire Royal Hospital ( Site 0521)

Gloucester, Gloucestershire, United Kingdom

Lincoln County Hospital ( Site 0535)

Lincoln, Great Britain, United Kingdom

Boston Pilgrim Hospital ( Site 0525)

Boston, Lincolnshire, United Kingdom

University College London Hospital ( Site 0527)

London, London, City of, United Kingdom

Guy's & St Thomas' NHS Foundation Trust ( Site 0523)

London, London, City of, United Kingdom

Hammersmith Hospital ( Site 0533)

London, London, City of, United Kingdom

Freeman Hospital ( Site 0532)

Newcastle upon Tyne, United Kingdom

Royal Gwent Hospital ( Site 0524)

Newport, United Kingdom

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