RecruitingPhase 3NCT06517758

A Phase III Study to Investigate Efficacy, Safety and Tolerability of Iptacopan Compared With Placebo in Participants Aged 18 to 85 Years With gMG.

A Randomized, Double-blind, Placebo-controlled Phase III Study to Evaluate the Efficacy, Safety, and Tolerability of Iptacopan in Patients With Generalized Myasthenia Gravis, Followed by an Open-label Extension Phase


Sponsor

Novartis Pharmaceuticals

Enrollment

146 participants

Start Date

Jul 31, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

The study is a randomized, double-blind, placebo-controlled, multicenter, Phase III study, to evaluate efficacy, safety and tolerability of iptacopan in patients with AChR+ gMG who are on stable SOC treatment. Participants who meet the eligibility criteria will be randomized in a ratio of 1:1, to receive either iptacopan or matching placebo, for 6 months (180 days) while continuing on a stable SOC treatment. The randomization will be stratified based on region.


Eligibility

Min Age: 18 YearsMax Age: 85 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a drug called Iptacopan and Matching Placebo for people with generalized myasthenia gravis. The study is currently recruiting participants at 125 locations. People eligible for this study include aged 18 Years to 85 Years.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGIptacopan

Hard gelatin capsule

OTHERMatching Placebo

Hard gelatin capsule


Locations(125)

Honor Health Research Institute

Scottsdale, Arizona, United States

Fullerton Neuro and Headache Ctr

Fullerton, California, United States

SC3 Research Pasadena

Pasadena, California, United States

California Pacific Medical Center

Sacramento, California, United States

Neurology Offices Of South Florida

Boca Raton, Florida, United States

Superior Associates in Research LLC

Hialeah, Florida, United States

Augusta University Georgia

Augusta, Georgia, United States

Hawaii Pacific Neuroscience LLC

Honolulu, Hawaii, United States

University of Chicago Medical Centr

Chicago, Illinois, United States

Prairie Heart Institute

Springfield, Illinois, United States

Mid Atlantic Epilepsy and Sleep Ctr

Bethesda, Maryland, United States

Massachusetts General Hospital

Boston, Massachusetts, United States

Henry Ford Health System

Detroit, Michigan, United States

Duke University Medical Center

Durham, North Carolina, United States

Neuroscience Research Ctr

Canton, Ohio, United States

Ohio State University Medical Center

Columbus, Ohio, United States

Penn Presbyterian Medical Center

Philadelphia, Pennsylvania, United States

Vanderbilt University Medical CenterX

Nashville, Tennessee, United States

Nerve and Muscle Center of Texas

Houston, Texas, United States

Central TX Neuro Consultants P A

Round Rock, Texas, United States

Center for Neurological Disorders G

Greenfield, Wisconsin, United States

Novartis Investigative Site

CABA, Buenos Aires, Argentina

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Córdoba, Córdoba Province, Argentina

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Buenos Aires, Argentina

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Córdoba, Argentina

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Camperdown, Sydney, Australia

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Porto Alegre, Rio Grande do Sul, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Joinville, Santa Catarina, Brazil

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Bahia, Brazil

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São Paulo, Brazil

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Hefei, Anhui, China

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Guangzhou, Guangdong, China

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Shenzhen, Guangdong, China

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Shijiazhuang, Hebei, China

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Changsha, Hunan, China

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Suzhou, Jiangsu, China

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Nanchang, Jiangxi, China

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Xi'an, Shaanxi, China

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Xianyang, Shaanxi, China

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Beijing, China

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Beijing, China

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Beijing, China

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Fujian, China

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Jinan, China

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Copenhagen, Denmark

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Limoges, Haute Vienne, France

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Garches, France

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Nice, France

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Paris, France

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Paris, France

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Munich, Bavaria, Germany

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Regensburg, Bavaria, Germany

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Würzburg, Bavaria, Germany

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Frankfurt am Main, Hesse, Germany

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Bochum, Germany

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Bochum, Germany

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Essen, Germany

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Athens, Greece

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Chaïdári, Greece

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Larissa, Greece

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Pátrai, Greece

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Thessaloniki, Greece

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Haifa, Israel

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Jerusalem, Israel

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Bologna, BO, Italy

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Florence, FI, Italy

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Genova, GE, Italy

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Milan, MI, Italy

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Palermo, PA, Italy

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Palermo, PA, Italy

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Roma, RM, Italy

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Roma, RM, Italy

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Roma, RM, Italy

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Orbassano, TO, Italy

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Naples, Italy

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Chiba, Chiba, Japan

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Narita, Chiba, Japan

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Sapporo, Hokkaido, Japan

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Nishinomiya, Hyōgo, Japan

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Hanamaki, Iwate, Japan

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Sendai, Miyagi, Japan

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Suita, Osaka, Japan

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Higashi-Matsuyama, Saitama, Japan

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Shinjuku Ku, Tokyo, Japan

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Fukuoka, Japan

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Fukushima, Japan

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Hiroshima, Japan

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Lublin, Lublin Voivodeship, Poland

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Warsaw, Masovian Voivodeship, Poland

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Krakow, POL, Poland

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Katowice, Silesian Voivodeship, Poland

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Bydgoszcz, Poland

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Katowice, Poland

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Krakow, Poland

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Lublin, Poland

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Poznan, Poland

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Rzeszów, Poland

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Warsaw, Poland

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Lisbon, Portugal

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Lisbon, Portugal

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Porto, Portugal

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Vila Nova de Gaia, Portugal

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Belgrade, Serbia

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Niš, Serbia

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Daegu, South Korea

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Gwangju, South Korea

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Seoul, South Korea

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Seoul, South Korea

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Santiago Compostela, A Coruna, Spain

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L'Hospitalet de Llobregat, Barcelona, Spain

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Alicante, Spain

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Barcelona, Spain

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Lleida, Spain

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Madrid, Spain

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Málaga, Spain

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Valencia, Spain

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Inverness, Invernesshire, United Kingdom

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Ilford, London, United Kingdom

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Swinton, Manchester, United Kingdom

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Birmingham, West Midlands, United Kingdom

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Liverpool, United Kingdom

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London, United Kingdom

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London, United Kingdom

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Southampton, United Kingdom

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NCT06517758


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