RecruitingPhase 1NCT06585449

A Study to Evaluate ALN-HTT02 in Adult Patients With Huntington's Disease

A Randomized, Double-blind, Placebo-controlled Study, to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered Single Ascending Doses of ALN-HTT02 in Adult Patients With Huntington's Disease


Sponsor

Alnylam Pharmaceuticals

Enrollment

66 participants

Start Date

Oct 14, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of this study is to evaluate the safety, tolerability, pharmacodynamics (PD) and pharmacokinetics (PK) of single or repeat doses of ALN-HTT02.


Eligibility

Min Age: 25 YearsMax Age: 70 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a drug called ALN-HTT02 and a drug called Placebo for people with huntington’s disease. The study is currently recruiting participants at 19 locations. People eligible for this study include aged 25 Years to 70 Years.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

Interested in this trial?

Get notified about updates and connect with the research team.

Interventions

DRUGALN-HTT02

ALN-HTT02 will be administered intrathecally

DRUGPlacebo

Placebo will be administered intrathecally


Locations(19)

Clinical Trial Site

Edmonton, Canada

Clinical Trial Site

Montreal, Canada

Clinical Trial Site

Ottawa, Canada

Clinical Trial Site

Vancouver, Canada

Clinical Trial Site

Berlin, Germany

Clinical Trial Site

Bochum, Germany

Clinical Trial Site

Bonn, Germany

Clinical Trial Site

Dresden, Germany

Clinical Trial Site

Münster, Germany

Clinical Trial Site

Taufkirchen, Germany

Clinical Trial Site

Ulm, Germany

Clinical Trial Site

Birmingham, United Kingdom

Clinical Trial Site

Cambridge, United Kingdom

Clinical Trial Site

Cardiff, United Kingdom

Clinical Trial Site

Glasgow, United Kingdom

Clinical Trial Site

Greater Manchester, United Kingdom

Clinical Trial Site

London, United Kingdom

Clinical Trial Site

Oxford, United Kingdom

Clinical Trial Site

Plymouth, United Kingdom

View Full Details on ClinicalTrials.gov

For the most up-to-date information, visit the official listing.

Visit

NCT06585449


Related Trials