An Open Label Dose Escalation Study to Assess the Safety, Tolerability, and Pharmacologic Properties of High Dose Ambroxol Hydrochloride in Adult (≥ 18 Years of Age) Subjects With MPS III
Ozlem Goker-Alpan
10 participants
Dec 1, 2024
INTERVENTIONAL
Conditions
Summary
A dose escalation study to evaluate the safety, tolerability, and pharmacologic properties of Ambroxol in adult participants with Sanfilippo disease(s) (MPS3).
Eligibility
Plain Language Summary
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Interventions
Ambroxol Hydrochloride 30 mg oral pill/tablet - 9 mg/kg/day
Ambroxol Hydrochloride 30 mg oral pill/tablet - 18 mg/kg/day
Ambroxol Hydrochloride 30 mg oral pill/tablet - 27 mg/kg/day
Locations(1)
View Full Details on ClinicalTrials.gov
For the most up-to-date information, visit the official listing.
NCT06614894