RecruitingPhase 2NCT06680830

A Phase 2 Study and Open-Label Extension of NEU-411 in Companion Diagnostic-Positive Participants With Early Parkinson's Disease

A Phase 2, Randomized, Double-Blind, Placebo-Controlled Study and Open-Label Extension to Evaluate the Safety and Efficacy of NEU-411 in Companion Diagnostic-Positive Participants With Early Parkinson's Disease (NEULARK)


Sponsor

Neuron23 Inc.

Enrollment

150 participants

Start Date

Jan 17, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

The goal of this Phase 2 clinical trial is to investigate the efficacy and safety of NEU-411 in men and women aged 40-80 years with early Parkinson's Disease (PD) who have predicted elevations in the activity of the "leucine-rich repeat kinase 2" ("LRRK2" for short) pathway based on their genetic profile. A DNA test will be used to identify the "LRRK2-driven" population with predicted elevation in the LRRK2 pathway.


Eligibility

Min Age: 40 YearsMax Age: 80 Years

Inclusion Criteria4

  • Aged 40-80 years at time of screening, inclusive
  • Diagnosis of clinically established or clinically probable Parkinson's Disease (PD)
  • LRRK2-driven PD using the investigational companion diagnostic genetic test (CDx)
  • Modified Hoehn and Yahr (mH\&Y) of 1 to 2.5

Exclusion Criteria3

  • Secondary or atypical parkinsonian syndromes
  • Uncontrolled diabetes mellitus with hemoglobin A1c (HbA1c) \>8%
  • Other significant medical conditions (as determined by medical history, examination, or clinical investigations at screening)

Interventions

DRUGNEU-411

NEU-411, a potent, selective, orally bioavailable, highly permeable, brain penetrant, small molecule inhibitor of LRRK2 activity

OTHERPlacebo

Orally-administered matched placebo


Locations(69)

Banner Sun Health Research Institute

Sun City, Arizona, United States

University of Arkansas

Little Rock, Arkansas, United States

Neuro-Pain Medical Center

Fresno, California, United States

University of California, Irvine

Irvine, California, United States

University of California, Los Angeles

Los Angeles, California, United States

Esperanza Clinical

Murrieta, California, United States

Parkinson's Research Centers of America - Palo Alto

Palo Alto, California, United States

Sutter Neuroscience Institute

Sacramento, California, United States

University of Colorado - Anschutz Medical Campus

Aurora, Colorado, United States

Parkinson's Disease and Movement Disorders Center of Boca Raton

Boca Raton, Florida, United States

University of Florida

Gainesville, Florida, United States

Neurology One

Orlando, Florida, United States

USF Parkinson's & Movement Disorders Clinic

Tampa, Florida, United States

Emory University

Atlanta, Georgia, United States

Augusta University

Augusta, Georgia, United States

Northwestern Medical Group, Department of Neurology

Chicago, Illinois, United States

University of Kansas Medical Center

Kansas City, Kansas, United States

University of Kentucky

Lexington, Kentucky, United States

Ochsner Clinic Foundation

New Orleans, Louisiana, United States

University of Maryland

Baltimore, Maryland, United States

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Quest Research Institute

Farmington Hills, Michigan, United States

Struthers Parkinson Center

Golden Valley, Minnesota, United States

Cleveland Clinic

Las Vegas, Nevada, United States

Northwell Health

Great Neck, New York, United States

Icahn School of Medicine at Mount Sinai/Mount Sinai West

New York, New York, United States

Columbia University

New York, New York, United States

University of Rochester

Rochester, New York, United States

University of North Carolina - Chapel Hill

Chapel Hill, North Carolina, United States

The Ohio State University

Columbus, Ohio, United States

The Movement Disorder Clinic of Oklahoma

Tulsa, Oklahoma, United States

Oregon Health & Science University (OHSU)

Portland, Oregon, United States

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, United States

Medical University of South Carolina

Charleston, South Carolina, United States

Vanderbilt University

Nashville, Tennessee, United States

Neurology Consultants of Dallas PA

Dallas, Texas, United States

Baylor College of Medicine

Houston, Texas, United States

The University of Texas Health Science Center at Houston

Houston, Texas, United States

Central Texas Neurology Consultants

Round Rock, Texas, United States

University of Utah Movement Division

Salt Lake City, Utah, United States

University of Virginia

Charlottesville, Virginia, United States

EvergreenHealth

Kirkland, Washington, United States

Inland Northwest Research

Spokane, Washington, United States

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Rambam Medical Center

Haifa, Israel

Shaare Zedek Medical Center

Jerusalem, Israel

Sheba Medical Center

Ramat Gan, Israel

Tel Aviv Medical Center

Tel Aviv, Israel

IRCCS Ospedale San Raffaele (HSR) - Dipartimento Di Neurologia

Milan, Italy

Universita Degli Studi Della Campania "Luigi Vanvitelli" - Azienda Ospedaliera Universitaria

Napoli, Italy

Universita Degli Studi Di Padova - Azienda Ospedaliera Di Padova - Clinica Neurologica

Padua, Italy

Azienda Ospedaliero Universitaria Pisana - Stabilimento Ospedaliero Di Santa Chiara

Pisa, Italy

Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) - San Raffaele Pisana

Rome, Italy

Fondazione Policilinico Universitario A Gemelli IRCCS

Rome, Italy

Centrum Medyczne Neuromed

Bydgoszcz, Poland

NZOZ Wielospecjalistyczna Poradnia Lekarska Synapsis Lech Szczechowski

Katowice, Poland

Pro Life Medica Sp. z o. o. ETA Lublin

Lublin, Poland

Insula Badania Sp. Z o.o.

Warsaw, Poland

Policlinica Gipuzkoa - Centro de Investigacion Parkinson (CIP)

San Sebastián, Donostia, Spain

Instituto de Investigacion Sanitaria Biocruces Bizkaia - Hospital Universitario Cruces

Barakaldo, Spain

Hospital Universitari Vall d'Hebron

Barcelona, Spain

Hospital Clinic de Barcelona (Hospital Clinic i Provincial) - Barnaclinic S.A.

Barcelona, Spain

Universidad Autonoma de Madrid (UAM) - Hospital Universitario de La Princesa

Madrid, Spain

Hospital Universitario HM Puerta del Sur

Móstoles, Spain

Hospital Universitario Virgen del Rocio (HUVR) - Instituto de Biomedicina de Sevilla (IBIS)

Seville, Spain

St George's Hospital, University of London

London, England, United Kingdom

University College London Hospitals NHS Foundation Trust

London, England, United Kingdom

Clinical Aging Research Unit, Newcastle University

Newcastle upon Tyne, England, United Kingdom

Ninewells Hospital and Medical School - NHS Tayside

Dundee, Scotland, United Kingdom

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NCT06680830


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