RecruitingNCT06747884
Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
Sponsor
Virginia Commonwealth University
Enrollment
200 participants
Start Date
Jun 6, 2025
Study Type
OBSERVATIONAL
Conditions
Summary
This is a natural history study to improve the types of assessments and biological samples that will be used in clinical drug trials in both congenital myotonic dystrophy and childhood myotonic dystrophy.
Eligibility
Min Age: 3 YearsMax Age: 17 Years
Plain Language Summary
Simplified for easier understanding
This clinical trial is studying a new treatment for people with childhood myotonic dystrophy, congenital myotonic dystrophy, and other related conditions. The study is currently recruiting participants at 1 location. People eligible for this study include aged 3 Years to 17 Years.
This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.
Interested in this trial?
Get notified about updates and connect with the research team.
Locations(4)
View Full Details on ClinicalTrials.gov
For the most up-to-date information, visit the official listing.
NCT06747884
Related Trials
Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
NCT077002251 location
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
NCT0748693420 locations
DMCRN-02-001: Assessing Pediatric Endpoints in DM1
NCT052247785 locations
A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
NCT068442149 locations
Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic Volunteers
NCT073219771 location