RecruitingPhase 2Phase 3NCT06943755

Zanzalintinib Versus Everolimus in Participants With Locally Advanced or Metastatic Neuroendocrine Tumors

A Phase 2/3, Multicenter, Randomized Open-Label Study of Zanzalintinib vs Everolimus in Participants With Previously Treated, Unresectable, Locally Advanced or Metastatic Neuroendocrine Tumors


Sponsor

Exelixis

Enrollment

440 participants

Start Date

Jul 21, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

The primary purpose of this study is to assess the effectiveness of zanzalintinib compared to everolimus in participants with previously treated, unresectable, locally advanced or metastatic neuroendocrine tumors.


Eligibility

Min Age: 18 Years

Inclusion Criteria5

  • Histologically confirmed, locally advanced/unresectable or metastatic, well-differentiated Grade 1, 2, or 3 NETs of pancreatic origin or extra-pancreatic origin.
  • Allowed prior lines of therapy, based on the site of NET and functional status.
  • Documented radiographic disease progression per RECIST 1.1, as assessed by the Investigator based on imaging assessments (computed tomography \[CT\] or magnetic resonance imaging \[MRI\]) within 12 months before randomization.
  • Measurable disease according to RECIST 1.1 as determined by the Investigator.
  • Archival tumor tissue is required, if available. If archival tumor tissue is not available, a fresh biopsy may be submitted if it can be safely and feasibly obtained. Every attempt should be made to provide tumor tissue.

Exclusion Criteria5

  • Histologically confirmed neuroendocrine carcinomas (including small cell lung cancer), medullary thyroid cancer, pheochromocytoma, paraganglioma, Merkel cell carcinoma, and mixed neuroendocrine non-neuroendocrine neoplasm (MiNEN).
  • Prior treatment with a vascular endothelial growth factor receptor (VEGFR) -targeting tyrosine kinase inhibitor or a mammalian target of rapamycin (mTOR) inhibitor.
  • Systemic chemotherapy and any liver-directed or other ablative therapy within 4 weeks before randomization.
  • Systemic radionuclide therapy within 6 weeks before randomization.
  • Radiation therapy for bone metastases within 2 weeks, any other radiation therapy, except as indicated above, within 4 weeks before randomization.

Interventions

DRUGZanzalintinib

Administered as specified in the treatment arm.

DRUGEverolimus

Administered as specified in the treatment arm.


Locations(53)

Exelixis Clinical Site #43

Birmingham, Alabama, United States

Exelixis Clinical Site #36

Phoenix, Arizona, United States

Exelixis Clinical Site #42

Tucson, Arizona, United States

Exelixis Clinical Site #18

Beverly Hills, California, United States

Exelixis Clinical Site #16

Los Angeles, California, United States

Exelixis Clinical Site #12

Santa Monica, California, United States

Exelixis Clinical Site #29

Vallejo, California, United States

Exelixis Clinical Site #19

Washington D.C., District of Columbia, United States

Exelixis Clinical Site #35

Jacksonville, Florida, United States

Exelixis Clinical Site #11

Tampa, Florida, United States

Exelixis Clinical Site #9

Lexington, Kentucky, United States

Exelixis Clinical Site #23

Metairie, Louisiana, United States

Exelixis Clinical Site #8

Boston, Massachusetts, United States

Exelixis Clinical Site #47

Detroit, Michigan, United States

Exelixis Clinical Site #1

Grand Rapids, Michigan, United States

Exelixis Clinical Site #38

Rochester, Minnesota, United States

Exelixis Clinical Site #5

St Louis, Missouri, United States

Exelixis Clinical Site #25

Omaha, Nebraska, United States

Exelixis Clinical Site #14

Albuquerque, New Mexico, United States

Exelixis Clinical Site #7

New York, New York, United States

Exelixis Clinical Site #53

Rochester, New York, United States

Exelixis Clinical Site #17

Chapel Hill, North Carolina, United States

Exelixis Clinical Site #6

Durham, North Carolina, United States

Exelixis Clinical Site #39

Cleveland, Ohio, United States

Exelixis Clinical Site #28

Columbus, Ohio, United States

Exelixis Clinical Site #27

Portland, Oregon, United States

Exelixis Clinical Site #20

Philadelphia, Pennsylvania, United States

Exelixis Clinical Site #21

Pittsburgh, Pennsylvania, United States

Exelixis Clinical Site #24

Knoxville, Tennessee, United States

Exelixis Clinical Site #10

Grapevine, Texas, United States

Exelixis Clinical Site #15

Salt Lake City, Utah, United States

Exelixis Clinical Site #3

Charlottesville, Virginia, United States

Exelixis Clinical Site #13

Fairfax, Virginia, United States

Exelixis Clinical Site #34

Seattle, Washington, United States

Exelixis Clinical Site #31

Milwaukee, Wisconsin, United States

Exelixis Clinical Site #40

Saint Leonards, New South Wales, Australia

Exelixis Clinical Site #51

Clayton, Victoria, Australia

Exelixis Clinical Site #48

Graz, Austria

Exelixis Clinical Site #49

Toronto, Canada

Exelixis Clinical Site #52

Tübingen, Germany

Exelixis Clinical Site #45

Katowice, Poland

Exelixis Clinical Site #37

Warsaw, Poland

Exelixis Clinical Site #2

San Juan, Puerto Rico

Exelixis Clinical Site # 4

San Juan, Puerto Rico

Exelixis Clinical Site #30

Seoul, South Korea

Exelixis Clinical Site #46

Seoul, South Korea

Exelixis Clinical Site #32

Seoul, South Korea

Exelixis Clinical Site #41

Seoul, South Korea

Exelixis Clinical Site #26

Seoul, South Korea

Exelixis Clinical Site #44

Madrid, Spain

Exelixis Clinical Site #22

London, England, United Kingdom

Exelixis Clinical Site #50

Liverpool, United Kingdom

Exelixis Clinical Site #33

Sheffield, United Kingdom

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NCT06943755