RecruitingPhase 3NCT06951711

A Study to Evaluate the Efficacy and Safety of KarXT for the Treatment of Manic Episodes in Bipolar-I Disorder (BALSAM-2)

A Phase 3, Randomized, Double-blind, Placebo-controlled Study to Evaluate the Efficacy and Safety of KarXT for the Treatment of Manic Episodes in Bipolar-I Disorder (BALSAM-2)


Sponsor

Bristol-Myers Squibb

Enrollment

274 participants

Start Date

Jun 13, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

This is a Phase 3, randomized, double-blind, placebo-controlled, multicenter, inpatient study in participants with bipolar disorder experiencing an acute episode of mania or mania with mixed features. The primary objective of the study is to evaluate the efficacy of KarXT compared to placebo in treating symptoms of mania during a 3-week inpatient period. The duration of the study including screening, the double-blind inpatient treatment period and safety-follow-up is no more than seven weeks.


Eligibility

Min Age: 18 YearsMax Age: 65 Years

Inclusion Criteria6

  • Participants must have a primary diagnosis of Bipolar-I disorder established by a comprehensive psychiatric evaluation.
  • Participants must be experiencing an acute episode or relapse of mania or mania with mixed features (≤ 3 weeks).
  • Participants must require hospitalization for the acute exacerbation or relapse of mania.
  • Participants must have all psychotropic medications washed out in no more than 14 days prior to the first dose of the study drug.
  • Participants must have a Young Mania Rating Scale (YMRS) score of ≥ 20 at Screening and at Baseline.
  • Participants must have a Clinical Global Impressions-Bipolar (CGI-BP) ≥ 4 at Screening and at Baseline.

Exclusion Criteria5

  • Participants must not have any primary Diagnostic and Statistical Manual of Mental Disorders (5th Edition, Text Revision) (DSM-5-TR) disorder, other than BP-I with mania or mania with mixed features within 12 months before screening, including BP-I with depression (for previous 3 months only), BP-II disorder, borderline personality disorder, major depressive disorder, and primary psychotic disorder, with the exception of mild anxiety disorders.
  • Participants must not have a primary diagnosis of BP-I with rapid cycling (≥ 4 distinct mood episodes in one year).
  • Participants must not have a DSM-5-TR diagnosis of moderate to severe substance use disorder (except tobacco use disorder) within the 12 months before screening, or current use as determined by urine toxicology screen or alcohol test.
  • Participants must not be at risk for suicidal behavior at screening or the baseline visit as determined by the Investigator's clinical assessment and the Columbia-Suicide Severity Rating Scale (C-SSRS).
  • Participants must not have cirrhosis, liver cancer, clinically significant liver disease based on the liver function test results.

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Interventions

DRUGKarXT

Specified dose on specified days

OTHERPlacebo

Specified dose on specified days


Locations(69)

Pillar Clinical Research- Little Rock

Little Rock, Arkansas, United States

Woodland Research Northwest

Rogers, Arkansas, United States

Proscience Research Group

Culver City, California, United States

Clinical Innovations, Inc. dba CITrials

Riverside, California, United States

Collaborative Neuroscience Research, LLC

Torrance, California, United States

Local Institution - 0036

Hialeah Gardens, Florida, United States

Behavioral Clinical Research

Hollywood, Florida, United States

LCC Medical Research Institute

Miami, Florida, United States

Innovative Clinical Research, Inc.

Miami Lakes, Florida, United States

South Florida Research Phase I-IV

Miami Springs, Florida, United States

Local Institution - 0019

Tampa, Florida, United States

Health Synergy Clinical Research

West Palm Beach, Florida, United States

Atlanta Center for Medical Research

Atlanta, Georgia, United States

CenExel iResearch, LLC

Decatur, Georgia, United States

Local Institution - 0020

Chicago, Illinois, United States

CBH Health

Gaithersburg, Maryland, United States

Precise Research Centers

Flowood, Mississippi, United States

Arch Clinical Trials

St Louis, Missouri, United States

Local Institution - 0076

North Las Vegas, Nevada, United States

Hassman Research Institute Marlton Site

Marlton, New Jersey, United States

Local Institution - 0031

Marlton, New Jersey, United States

Local Institution - 0075

Charlotte, North Carolina, United States

University of Cincinnati Medical Center

Cincinnati, Ohio, United States

Neuro-Behavioral Clinical Research

North Canton, Ohio, United States

InSite Clinical Research

DeSoto, Texas, United States

Local Institution - 0028

Houston, Texas, United States

Pillar Clinical Research - Richardson

Richardson, Texas, United States

Local Institution - 0009

Zagreb, City of Zagreb, Croatia

Klinika za psihijatriju "Vrapče"

Zagreb, Croatia

Klinika za psihijatriju "Vrapče"

Zagreb, Croatia

Local Institution - 0078

Zagreb, Croatia

Psihijatrijska bolnica "Sveti Ivan"

Zagreb, Croatia

Local Institution - 0065

Vadodara, Gujarat, India

Local Institution - 0082

Belagavi, Karnataka, India

Local Institution - 0053

Kozhikode, Kerala, India

Local Institution - 0051

Ludhiana, Punjab, India

Local Institution - 0052

Hyderabad, Telangana, India

Local Institution - 0055

Hyderabad, Telangana, India

Local Institution - 0054

Kolkata, West Bengal, India

Shalvata Mental Health Center

Hod HaSharon, Central District, Israel

Local Institution - 0046

Ness Ziona, Central District, Israel

Local Institution - 0058

Petah Tikva, Central District, Israel

Sheba Medical Center

Ramat Gan, Central District, Israel

Be'er Sheva Mental Health Center

Beersheba, Southern District, Israel

Kfar Shaul Mental Health Center

Jerusalem, Israel

Local Institution - 0001

Milan, Lombardy, Italy

Local Institution - 0056

Pisa, Tuscany, Italy

Local Institution - 0007

Siena, Tuscany, Italy

Local Institution - 0041

Ancona, Italy

Local Institution - 0040

Genova, Italy

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Centrul de Evaluare și Tratament a Toxicodependenței pentru Tineri Sf.Stelian

Bucharest, Romania

Spitalul Universitar de Urgenta Militar Central Dr. Carol Davila

Bucharest, Romania

Local Institution - 0047

Iași, Romania

Local Institution - 0061

Sanpetru /Brasov, Romania

Local Institution - 0071

Košice, Košice Region, Slovakia

Local Institution - 0073

Košice, Košice Region, Slovakia

Local Institution - 0072

Vranov nad Topľou, Presov, Slovakia

Hospital Universitari Vall d'Hebron

Barcelona, Barcelona [Barcelona], Spain

Osi Bilbao-Basurto

Bilbao, Basque Country, Spain

Hospital Clínic de Barcelona

Barcelona, Catalunya [Cataluña], Spain

Nacka Local Hospital

Nacka, Stockholms Län [se-01], Sweden

Local Institution - 0067

Uppsala, Uppsala Län [se-03], Sweden

Local Institution - 0070

Gothenburg, Västra Götalands Län [se-14], Sweden

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NCT06951711