RecruitingEarly Phase 1NCT06959979

Novel Molecular Targets and Innovative Therapeutic Perspective in Medulloblastoma


Sponsor

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Enrollment

60 participants

Start Date

Nov 25, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

Medulloblastoma (MB), a rare yet critical pediatric brain tumor, is divided into 4 molecular subgroups (WNT, SHH, Group 3, Group 4), each with distinct genetic profiles. Despite diagnostic and therapeutic advances, neurotoxicity from standard treatments (resection, radiotherapy, chemotherapy) and the need for long-term care remain challenges. CDK4/6 inhibitors (palbociclib, ribociclib, abemaciclib), approved for breast cancer, show potential in other tumors, but their efficacy in MB is unclear. Treatment resistance is a concern. This project aims to identify genetic markers of sensitivity to CDK4/6 inhibitors in MB, to improve therapies and overcome resistance.


Eligibility

Min Age: 0 YearsMax Age: 18 Years

Inclusion Criteria1

  • All patients affected by Medulloblastoma operated on at the Pediatric Neurosurgery Unit during their pediatric age will be elected to take part to the study

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Interventions

DRUGCDK4/6 Inhibitor (Palbociclib, Ribociclib, Abemaciclib)

Evaluation of the response to CDK4/6 inhibitors (Palbociclib, Ribociclib, Abemaciclib) on selected Medulloblastoma (MB) patient-derived organoids (PDOs).


Locations(1)

Fondazione Policlinico Gemelli Irccs

Roma, ROMA, Italy

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NCT06959979


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