RecruitingPhase 2NCT06990269

Phase 2 Study of ADX-038 in Participants With Geographic Atrophy

A Phase 2, Randomized, Masked, Placebo-Controlled Study of Subcutaneously Administered ADX-038 in Participants With Geographic Atrophy (GA) Secondary to Age-Related Macular Degeneration (AMD)


Sponsor

ADARx Pharmaceuticals, Inc.

Enrollment

240 participants

Start Date

Nov 10, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

Phase 2 study is designed to assess the efficacy of ADX-038 compared with placebo in participants with GA secondary to AMD. Safety, pharmacokinetics (PK), and pharmacodynamics (PD) will also be assessed.


Eligibility

Min Age: 60 Years

Inclusion Criteria4

  • Clinical diagnosis of GA of the macula secondary to AMD
  • GA lesions between 2.5 and 12.5 mm2 at screening
  • Sufficiently clear ocular media, adequate pupillary dilation and fixation to permit quality fundus imaging in the study eye as described in the protocol
  • Willing and able to comply with clinic visits and study-related procedures, including completion of the full series of meningococcal vaccinations and pneumococcal vaccination required per protocol

Exclusion Criteria10

  • Has GA secondary to causes other than AMD
  • Has active ocular disease that compromises or confounds visual function
  • History of surgery for retinal detachment
  • Has ocular condition other than GA secondary to AMD
  • Use of intravitreal complement inhibitors in study eye
  • Hereditary or acquired complement deficiency
  • Active viral, bacterial or fungal infection
  • Liver injury as evidenced by abnormal liver function tests
  • Donating blood
  • History of choroidal neovascularization in the study eye

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Interventions

DRUGADX-038

siRNA duplex oligonucleotide

DRUGPlacebo

Saline


Locations(24)

ADARx Clinical Site

Gilbert, Arizona, United States

ADARx Clinical Site

Phoenix, Arizona, United States

ADARx Clinical Site

Beverly Hills, California, United States

ADARx Clinical Site

Huntington Beach, California, United States

ADARx Clinical Site

Poway, California, United States

ADARx Clinical Site

Orlando, Florida, United States

ADARx Clinical Site

Wildwood, Florida, United States

ADARx Clinical Site

Hagerstown, Maryland, United States

ADARx Clinical Site

Reno, Nevada, United States

ADARx Clinical Site

Erie, Pennsylvania, United States

ADARx Clinical Site

Austin, Texas, United States

ADARx Clinical Site

Dallas, Texas, United States

ADARx Clinical Site

McAllen, Texas, United States

ADARx Clinical Site

Round Rock, Texas, United States

ADARx Clinical Site

San Antonio, Texas, United States

ADARx Clinical Site

The Woodlands, Texas, United States

ADARx Clinical Site

St. George, Utah, United States

ADARx Clinical Site

Albury, New South Wales, Australia

ADARx Clinical Site

Hurstville, New South Wales, Australia

ADARx Clinical Site

Parramatta, New South Wales, Australia

ADARx Clinical Site

East Melbourne, Victoria, Australia

ADARx Clinical Site

Rowville, Victoria, Australia

ADARx Clinical Site

Ottawa, Ontario, Canada

ADARx Clinical Site

Toronto, Ontario, Canada

View Full Details on ClinicalTrials.gov

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NCT06990269


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