RecruitingPhase 3NCT07007312

Studies to Assess Ziftomenib in Combination With Ven+Aza or 7+3 in Patients With Untreated NPM1-m or KMT2A-r AML

Phase 3 Randomized, Double-blind, Placebo-controlled Studies Assessing Ziftomenib in Combination With Either Standard of Care Nonintensive (Venetoclax+Azacitidine) or Intensive (7+3) Therapy in Patients With Untreated NPM1 Mutated or KMT2A Rearranged Acute Myeloid Leukemia


Sponsor

Kura Oncology, Inc.

Enrollment

1,300 participants

Start Date

Sep 26, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

Ziftomenib is an investigational drug in development for the treatment of patients with acute myeloid leukemia (AML) with eligible genetic alterations. Ziftomenib is a type of therapy known to target the menin pathway in cancer cells. This protocol has 2 separate studies that will investigate the benefits and risks of adding ziftomenib to standard-of-care (SOC) AML treatments in patients with certain genetic mutations who have not received any treatment for their AML. In the first study, the Nonintensive Therapy Study, older patients or those with serious medical problems will receive the SOC therapies venetoclax (ven) and azacitidine (aza), plus either ziftomenib or a placebo. In the second study, the Intensive Therapy Study, medically fit patients will receive (a) the SOC therapies cytarabine and daunorubicin, plus either ziftomenib or a placebo during a first treatment phase called induction, (b) cytarabine plus either ziftomenib or a placebo during a second treatment phase called consolidation, and (c) ziftomenib or a placebo during a third treatment phase called maintenance. The physician will determine which study is the appropriate treatment for the patient, but neither the patient nor their physician will know whether the patient has been assigned to receive ziftomenib or a placebo. This design is called "double-blinded".


Eligibility

Min Age: 18 Years

Plain Language Summary

Simplified for easier understanding

This study is testing ziftomenib — a targeted drug — in combination with standard treatments for newly diagnosed acute myeloid leukemia (AML) with specific genetic mutations (NPM1 or KMT2A). There are two parts: one for patients who cannot tolerate intensive chemotherapy and one for patients who can. **You may be eligible if...** - You are 18 years or older - You have been newly diagnosed with AML per 2022 WHO criteria - Your leukemia has an NPM1 mutation (both groups) or a KMT2A rearrangement (intensive group only) - Your overall health meets the study requirements (ECOG 0–2) - For the non-intensive group: you are age 75+, or age 65–74 with health conditions that make intensive chemo unsafe **You may NOT be eligible if...** - You have previously received chemotherapy for AML - You have certain additional mutations (e.g., FLT3-ITD ratio ≥ 0.05, KMT2A partial tandem duplication) - You do not have either NPM1 mutation or KMT2A rearrangement - Your organ function does not meet required levels Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGZiftomenib

Oral administration

DRUGPlacebo

Oral administration

DRUGVenetoclax

Oral administration

DRUGAzacitidine (AZA)

Intravenous or subcutaneous administration

DRUGDaunorubicin

Intravenous administration

DRUGCytarabine (Ara-C)

Intravenous administration


Locations(39)

Banner MD Anderson Cancer Center

Gilbert, Arizona, United States

University of California, Fresno

Clovis, California, United States

University of California, San Diego

La Jolla, California, United States

Cedars-Sinai Medical Center

Los Angeles, California, United States

University of California, Irvine

Orange, California, United States

University of Colorado

Aurora, Colorado, United States

Colorado Blood Cancer Institute

Denver, Colorado, United States

Hartford HealthCare Cancer Institute

Hartford, Connecticut, United States

Yale University School of Medicine

New Haven, Connecticut, United States

University of Miami

Miami, Florida, United States

Moffitt Cancer Center & Research Institute

Tampa, Florida, United States

University of Kentucky

Lexington, Kentucky, United States

Wayne State University School of Medicine

Detroit, Michigan, United States

University of Minnesota

Minneapolis, Minnesota, United States

Rutgers Biomedical and Health Sciences

New Brunswick, New Jersey, United States

University of New Mexico

Albuquerque, New Mexico, United States

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Weill Cornell Medical Center

New York, New York, United States

University of North Carolina, Chapel Hill

Chapel Hill, North Carolina, United States

Duke University Medical Center

Durham, North Carolina, United States

Ohio State University

Columbus, Ohio, United States

Willamette Valley Cancer Institute

Eugene, Oregon, United States

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Baptist Clinical Research Institute

Memphis, Tennessee, United States

Tennessee Oncology

Nashville, Tennessee, United States

TriStar Centennial Medical Center

Nashville, Tennessee, United States

Texas Oncology-Austin Midtown

Austin, Texas, United States

Texas Oncology-Presbyterian Cancer Center

Dallas, Texas, United States

University of Texas

Houston, Texas, United States

Texas Oncology - San Antonio Medical Center

San Antonio, Texas, United States

University of Virginia School of Medicine

Charlottesville, Virginia, United States

Virginia Cancer Specialists

Manassas, Virginia, United States

WVU Medicine Wheeling Hospital

Wheeling, West Virginia, United States

Froedtert & Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Centre Hospitalier de Béziers

Béziers, France

Centre Hospitalier Universitaire de Nantes

Nantes, France

Dong-A University Hospital

Busan, South Korea

Chungnam National University Daejeon Hospital

Daejeon, South Korea

Chonnam National University Hwasun Hospital

Hwasun, South Korea

View Full Details on ClinicalTrials.gov

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NCT07007312


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