RecruitingPhase 3NCT07007793

A Study to Assess Efficacy and Safety of Baxdrostat in Participants With Primary Aldosteronism

A Randomised, Double-Blind, Placebo-Controlled, Parallel-Group Study to Assess the Efficacy and Safety of Baxdrostat in Adult Participants With Primary Aldosteronism


Sponsor

AstraZeneca

Enrollment

250 participants

Start Date

Aug 7, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

This is a Phase III, multicentre, randomised, double-blind, placebo-controlled, parallel-group study to evaluate the safety, tolerability, and efficacy of baxdrostat versus placebo, on the reduction of Seated Blood Pressure (SBP) and achieving normalization of the Renin Angiotensin Aldosterone System (RAAS) in approximately 180 participants ≥ 18 years of age with Primary Aldosteronism (PA), with or without prior treatment with Mineralocorticoid Receptor Antagonists (MRAs) or potassium-sparing diuretics. Baxdrostat (or placebo) will be administered once daily, up-titrated after 2 weeks based on clinical response and tolerability. The study is planned to be conducted globally in approximately 90 study centres and 12 countries.


Eligibility

Min Age: 18 Years

Inclusion Criteria9

  • Male or female participants must be ≥ 18 years of age
  • Participants with a documented diagnosis of PA that fulfils the criteria defined in the 2016 or 2025 Endocrine Society Guidelines.
  • Participants willing and able to cease dosing of MRA or potassium sparing diuretics per study requirement for participants taking an MRA or potassium sparing diuretic at Screening.
  • eGFR ≥ 45 mL/min/1.73m2 at Screening
  • Serum potassium level ≥ 3.0 and < 5.0 mmol/L at Screening determined as per the central laboratory.
  • Have a stable regimen of antihypertensive medications for at least 4 weeks prior to randomisation
  • Mean seated SBP on AOBPM of ≥ 135 mmHg and ≤ 170 mmHg and mean DBP of
  • ≤ 105 mmHg.
  • Serum potassium (local lab) > 3.0 mmol/L at randomization.

Exclusion Criteria8

  • \- If not taking an MRA or potassium sparing diuretic at Screening: Mean seated SBP > 170 mmHg or mean seated DBP >105 mmHg (on AOBPM).
  • If taking an MRA or potassium sparing diuretic at Screening: Mean seated SBP > 160 mmHg or mean seated DBP ≥ 100 mmHg.
  • Previous surgical intervention for an adrenal adenoma or have a planned adrenalectomy, renal nerve denervation, or adrenal ablative procedure during the course of the study.
  • Has the following known secondary causes of HTN: renal artery stenosis, uncontrolled or untreated hyperthyroidism, uncontrolled or untreated hypothyroidism, pheochromocytoma, Cushing's syndrome, aortic coarctation.
  • Serum sodium level < 135 mmol/L at Screening, determined as per central laboratory.
  • New York Heart Association functional HF class IV at Screening.
  • Persistent atrial fibrillation.
  • Treatment with any MRA or potassium-sparing diuretic within 2 weeks prior to Randomisation.

Interested in this trial?

Get notified about updates and connect with the research team.

Interventions

DRUGBaxdrostat

Baxdrostat tablet administered orally, once daily (QD).

DRUGPlacebo

Placebo tablet matching baxdrostat, administered orally, once daily (QD).


Locations(89)

Research Site

Los Angeles, California, United States

Research Site

San Francisco, California, United States

Research Site

Farmington, Connecticut, United States

Research Site

Chicago, Illinois, United States

Research Site

Springfield, Illinois, United States

Research Site

Baltimore, Maryland, United States

Research Site

Boston, Massachusetts, United States

Research Site

Boston, Massachusetts, United States

Research Site

Ann Arbor, Michigan, United States

Research Site

Rochester, Minnesota, United States

Research Site

Olive Branch, Mississippi, United States

Research Site

Kansas City, Missouri, United States

Research Site

New York, New York, United States

Research Site

Cleveland, Ohio, United States

Research Site

Columbus, Ohio, United States

Research Site

Portland, Oregon, United States

Research Site

Bethlehem, Pennsylvania, United States

Research Site

Philadelphia, Pennsylvania, United States

Research Site

Columbia, South Carolina, United States

Research Site

Brownsville, Texas, United States

Research Site

Dallas, Texas, United States

Research Site

Brisbane, Australia

Research Site

Clayton, Australia

Research Site

Perth, Australia

Research Site

Calgary, Alberta, Canada

Research Site

Ottawa, Ontario, Canada

Research Site

Toronto, Ontario, Canada

Research Site

Montreal, Quebec, Canada

Research Site

Beijing, China

Research Site

Beijing, China

Research Site

Beijing, China

Research Site

Changsha, China

Research Site

Chengdu, China

Research Site

Chengdu, China

Research Site

Chongqing, China

Research Site

Nanjing, China

Research Site

Shanghai, China

Research Site

Tianjin, China

Research Site

Wuhan, China

Research Site

Wuhan, China

Research Site

Xianyang, China

Research Site

Amiens, France

Research Site

Bois-Guillaume, France

Research Site

Bordeaux, France

Research Site

Lille, France

Research Site

Marseille, France

Research Site

Paris, France

Research Site

Paris, France

Research Site

Berlin, Germany

Research Site

Düsseldorf, Germany

Research Site

Kaiserslautern, Germany

Research Site

München, Germany

Research Site

Reinfeld (Holstein), Germany

Research Site

Würzburg, Germany

Research Site

Belagavi, India

Research Site

Delhi, India

Research Site

Hyderabad, India

Research Site

Kolkata, India

Research Site

Mumbai, India

Research Site

Mumbai, India

Research Site

Bologna, Italy

Research Site

Brescia, Italy

Research Site

Florence, Italy

Research Site

Milan, Italy

Research Site

Milan, Italy

Research Site

Torino, Italy

Research Site

Kawasaki-shi, Japan

Research Site

Kodaira-shi, Japan

Research Site

Minatoku, Japan

Research Site

Ōta-ku, Japan

Research Site

Shinjuku-ku, Japan

Research Site

Yokohama, Japan

Research Site

Yufu-shi, Japan

Research Site

Barcelona, Spain

Research Site

Madrid, Spain

Research Site

Madrid, Spain

Research Site

Madrid, Spain

Research Site

Seville, Spain

Research Site

Kaohsiung City, Taiwan

Research Site

Taichung, Taiwan

Research Site

Taipei, Taiwan

Research Site

Taoyuan, Taiwan

Research Site

Yunlin, Taiwan

Research Site

Zhubei, Taiwan

Research Site

Cambridge, United Kingdom

Research Site

Cardiff, United Kingdom

Research Site

Dundee, United Kingdom

Research Site

London, United Kingdom

Research Site

London, United Kingdom

View Full Details on ClinicalTrials.gov

For the most up-to-date information, visit the official listing.

Visit

NCT07007793


Related Trials