RecruitingPhase 2NCT07023614

A Trial to Evaluate the Efficacy and Safety of Ninerafaxstat in Patients With Symptomatic Non-obstructive Hypertrophic Cardiomyopathy

A Global Phase 2b, Randomized, Double-Blinded, Placebo-Controlled Trial to Evaluate the Efficacy and Safety of Ninerafaxstat in Patients With Symptomatic Non-Obstructive Hypertrophic Cardiomyopathy - FORTITUDE-HCM


Sponsor

Imbria Pharmaceuticals, Inc.

Enrollment

165 participants

Start Date

Oct 6, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

FORTITUDE-HCM is a global, multicenter, double-blind, parallel-group, placebo-controlled Phase 2b study that will assess the efficacy and safety of ninerafaxstat compared to placebo on top of Standard of Care in patients with symptomatic nHCM


Eligibility

Min Age: 18 Years

Inclusion Criteria4

  • Has a clinical diagnosis of HCM consistent with current American College of Cardiology/American Heart Association and European Society of Cardiology Guideline definitions
  • Has had confirmation of nHCM by the echocardiography core laboratory based on screening rest and exercise stress echocardiography
  • New York Heart Association (NYHA) functional Class II or III at screening
  • Functional limitation as defined by a screening CPET

Exclusion Criteria4

  • Has a known or suspected infiltrative, genetic, or storage disorder causing cardiac hypertrophy that mimics nHCM
  • Has any other condition judged by the investigator to be the primary cause of dyspnea, exercise intolerance, and/or angina
  • Has an inability to exercise on a treadmill or bicycle (eg, orthopedic limitations)
  • Has any medical condition that precludes upright exercise stress testing

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Interventions

DRUGNinerafaxstat 200mg MR

Ninerafaxstat 200mg Modified Release tablet administered BID

DRUGPlacebo

Matching placebo tablet administered BID


Locations(23)

Imbria Investigational Site

La Jolla, California, United States

Imbria Investigational Site

San Francisco, California, United States

Imbria Investigational Site

Washington D.C., District of Columbia, United States

Imbria Investigational Site

Chicago, Illinois, United States

Imbria Investigational Site

Boston, Massachusetts, United States

Imbria Investigational Site

Burlington, Massachusetts, United States

Imbria Investigational Site

St Louis, Missouri, United States

Imbria Investigational Site

Houston, Texas, United States

Imbria Investigational Site

Charlottesville, Virginia, United States

Imbria Investigational Site

Montpellier, France

Imbria Investigational Site

Paris, France

Imbria Investigational Site

Saint-Herblain, France

Imbria Investigational Site

Katowice, Poland

Imbria Investigational Site

Guimarães, Portugal

Imbria Investigational Site

Lisbon, Portugal

Imbria Investigational Site

Barcelona, Barcelona, Spain

Imbria Investigational Site

A Coruña, Galicia, Spain

Imbria Investigational Site

Madrid, Madrid, Spain

Imbria Investigational Site

Vigo, Pontevedra, Spain

Imbria Investigational Site

Seville, Sevilla, Spain

Imbria Investigational Site

Seville, Sevilla, Spain

Imbria Investigational Site

London, England, United Kingdom

Imbria Investigational Site

Glasgow, Scotland, United Kingdom

View Full Details on ClinicalTrials.gov

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NCT07023614


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