RecruitingPhase 3NCT07115004

Study to Evaluate Subcutaneous (SC) VGA039 in Patients With Von Willebrand Disease (VWD)

A Prospective, Multicenter, Open-label, Phase 3 Clinical Study to Evaluate the Efficacy and Safety of Prophylactic VGA039 in Adolescent and Adult Patients With Von Willebrand Disease (VIVID-6)


Sponsor

Vega Therapeutics, Inc

Enrollment

60 participants

Start Date

Oct 15, 2025

Study Type

INTERVENTIONAL

Summary

This is a phase 3 study that will evaluate subcutaneous (SC) VGA039 in patients with von Willebrand Disease (VWD)


Eligibility

Min Age: 12 YearsMax Age: 75 Years

Inclusion Criteria6

  • to 75 years of age, inclusive
  • No clinically significant laboratory, ECG, or vital signs results
  • Documented diagnosis consistent with VWD of any type
  • Historical annualized bleeding rate (ABR; excluding menstrual bleeds and bleeds under the skin) of both untreated and treated bleeds ≥12 per year
  • Patients with VWD who are judged by the investigator to be suitable candidates for routine prophylaxis to reduce the frequency of bleeding episodes
  • Hemoglobin level ≥ 8 g/dL and platelet count ≥ 100 x 109/L at Screening

Exclusion Criteria6

  • Use of routine prophylaxis of VWF-containing concentrates defined as at least 1 VWF-containing concentrate infusion to prevent or reduce bleeding per week during the previous 6 months prior to screening
  • Planning to initiate routine prophylaxis with VWF-containing concentrates or any other hemostatic treatment during the study
  • Patients with pro-thrombotic disorders or abnormal findings on laboratory thrombophilia evaluation performed at screening or previously documented
  • History of arterial or venous thrombosis, including superficial thrombophlebitis, or embolism
  • Evidence of renal, hepatic, central nervous system, respiratory, cardiovascular disease, cerebrovascular disease, peripheral vascular disease, or metabolic dysfunction
  • Baseline FVIII activity > lower limit of normal (LLN)

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Interventions

DRUGVGA039

VGA039 SC administered for 49-weeks during the interventional phase following a 24-week observational period.


Locations(14)

Arkansas Children's Hospital

Little Rock, Arkansas, United States

Luskin Orthopaedic Institute For Children

Los Angeles, California, United States

UC Davis Medical Center

Sacramento, California, United States

University of California San Francisco

San Francisco, California, United States

Emory University Hospital

Atlanta, Georgia, United States

Children's Healthcare of Atlanta

Atlanta, Georgia, United States

University of Minnesota

Minneapolis, Minnesota, United States

Science 37, Inc. (Virtual Clinical MetaSite)

Morrisville, North Carolina, United States

Hemophilia Center of Western PA

Pittsburgh, Pennsylvania, United States

UT Southwestern Children's Hospital

Dallas, Texas, United States

Washington Center for Bleeding Disorders

Seattle, Washington, United States

K Eristavi National Center of Experimental and Clinical Surgery (ქირურგიის ეროვნული ცენტრი)

Tbilisi, Georgia

Frankfurt University Hospital (Universitätsmedizin Frankfurt)

Frankfurt, Germany

Charlotte Maxeke Johannesburg Academic Hospital School of Pathology Clinical Haematologist

Johannesburg, South Africa

View Full Details on ClinicalTrials.gov

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NCT07115004