RecruitingPhase 2NCT07160608

Safety and Efficacy of Tarperprumig in Adult Participants With Anti-Neutrophil Cytoplasmic Antibody (ANCA)-Associated Vasculitis

Phase 2, Randomized, Double-Blind, Placebo-controlled, Parallel-Group, Multicenter Study to Evaluate the Safety and Efficacy of Tarperprumig in Adult Participants With Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis (I TRANSCEND)


Sponsor

Alexion Pharmaceuticals, Inc.

Enrollment

75 participants

Start Date

Nov 26, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

The primary objective of this study is to evaluate the safety and tolerability of tarperprumig in participants with newly diagnosed or relapsing anti-neutrophil cytoplasmic antibody (ANCA)-associated vasculitis.


Eligibility

Min Age: 18 YearsMax Age: 80 Years

Inclusion Criteria3

  • Newly diagnosed or relapsing ANCA-associated vasculitis, GPA and MPA subtypes consistent with the 2022 ACR/EULAR classification criteria for GPA and MPA for whom treatment with rituximab or cyclophosphamide is considered.
  • Positive test for antibodies to either PR3-ANCA or MPO-ANCA at Screening or in the past by a quantitative assay (for example, ELISA, bead assay).
  • At least one major item, or at least 3 minor items, or at least 2 renal items in the BVAS.

Exclusion Criteria4

  • Other systemic diseases that, in the judgment of the Investigator, constitute the primary illness, including but not limited to: eosinophilic granulomatosis with polyangiitis (EGPA), systemic lupus erythematosus, IgA nephropathy and/or IgA associated vasculitis with or without Henoch-Schonlein purpura, rheumatoid vasculitis, Sjogren's syndrome, anti-GBM disease, cryoglobulinemic vasculitis, autoimmune hemolytic anemia, or mixed connective tissue disease.
  • Alveolar hemorrhage requiring invasive pulmonary ventilation support at Screening.
  • Any diseases or conditions that, in the judgment of the Investigator, present a substantial clinical risk to participate in this study.
  • For patients with a previous diagnosis of CKD, patients known to have a stable eGFR for greater than 3 months prior to Screening and a decline less than 25% of previous eGFR at Screening will be excluded.

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Interventions

DRUGPlacebo

Participants will receive placebo.

DRUGTarperprumig

Participants will receive tarperprumig.


Locations(78)

Research Site

Ciudad de Buenos Aires, Argentina

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Ciudad de Buenos Aires, Argentina

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La Plata, Argentina

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Rosario, Argentina

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San Juan Bautista, Argentina

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Santa Fe, Argentina

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Clayton, Australia

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Heidelberg, Australia

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Nedlands, Australia

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Wollongong, Australia

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Barretos, Brazil

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Belo Horizonte, Brazil

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Porto Alegre, Brazil

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Recife, Brazil

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São Paulo, Brazil

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São Paulo, Brazil

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São Paulo, Brazil

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Calgary, Alberta, Canada

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Edmonton, Alberta, Canada

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Etobicoke, Ontario, Canada

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Hamilton, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Baotou, China

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Beijing, China

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Beijing, China

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Guangzhou, China

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Hangzhou, China

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Nanchang, China

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Shenzhen, China

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Marseille, France

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Paris, France

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Paris, France

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Strasbourg, France

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Toulouse, France

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Berlin, Germany

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Essen, Germany

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Göttingen, Germany

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Ludwigshafen, Germany

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München, Germany

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Brescia, Italy

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Padova, Italy

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Pavia, Italy

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Pisa, Italy

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Gdansk, Poland

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Krakow, Poland

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Poznan, Poland

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Warsaw, Poland

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Daegu, South Korea

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Daegu, South Korea

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Daejeon, South Korea

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Seoul, South Korea

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Seoul, South Korea

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Seoul, South Korea

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Seoul, South Korea

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Seoul, South Korea

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Wŏnju, South Korea

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Barcelona, Spain

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Pamplona, Spain

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San Sebastián de los Reyes, Spain

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Santander, Spain

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Seville, Spain

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Kaohsiung City, Taiwan

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Taichung, Taiwan

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Taipei, Taiwan

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Taoyuan District, Taiwan

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Altındağ, Turkey (Türkiye)

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Ankara, Turkey (Türkiye)

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Center, Turkey (Türkiye)

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Istanbul, Turkey (Türkiye)

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Istanbul, Turkey (Türkiye)

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Kocaeli, Turkey (Türkiye)

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Birmingham, United Kingdom

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Cambridge, United Kingdom

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Leicester, United Kingdom

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London, United Kingdom

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London, United Kingdom

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Manchester, United Kingdom

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NCT07160608


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