RecruitingPhase 3NCT07223203

TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy

TRITON-PN: A Phase 3, Global, Randomized, Open-Label Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy (hATTR-PN)


Sponsor

Alnylam Pharmaceuticals

Enrollment

125 participants

Start Date

Dec 12, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of this study is to: * Determine the efficacy of nucresiran in patients with hATTR-PN by evaluating the effect on neurologic impairment, quality of life, nutritional status, disability, and gait speed * Demonstrate superiority of nucresiran compared to in-study vutrisiran with respect to serum transthyretin (TTR) levels


Eligibility

Min Age: 18 YearsMax Age: 85 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a drug called Nucresiran and a drug called Vutrisiran for people with hereditary transthyretin-mediated amyloidosis with polyneuropathy and hattr-pn. The study is currently recruiting participants at 29 locations.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGNucresiran

Nucresiran 300 mg administered SC q6M

DRUGVutrisiran

Vutrisiran 25 mg administered SC q3M


Locations(29)

Clinical Trial Site

Aurora, Colorado, United States

Clinical Trial Site

Chicago, Illinois, United States

Clinical Trial Site

Baltimore, Maryland, United States

Clinical Trial Site

Boston, Massachusetts, United States

Clinical Trial Site

Rochester, Minnesota, United States

Clinical Trial Site

New York, New York, United States

Clinical Trial Site

Chapel Hill, North Carolina, United States

Clinical Trial Site

Dallas, Texas, United States

Clinical Trial Site

Darlinghurst, Australia

Clinical Trial Site

São Paulo, Brazil

Clinical Trial Site

Égkomi, Cyprus

Clinical Trial Site

Créteil, France

Clinical Trial Site

Le Kremlin-Bicêtre, France

Clinical Trial Site

Marseille, France

Clinical Trial Site

Athens, Greece

Clinical Trial Site

Heraklion, Greece

Clinical Trial Site

Florence, Italy

Clinical Trial Site

Milan, Italy

Clinical Trial Site

Pavia, Italy

Clinical Trial Site

Suita, Japan

Clinical Trial Site

Kuala Lumpur, Malaysia

Clinical Trial Site

Porto, Portugal

Clinical Trial Site

Seoul, South Korea

Clinical Trial Site

Seoul, South Korea

Clinical Trial Site

Stockholm, Sweden

Clinical Trial Site

Umeå, Sweden

Clinical Trial Site

Taipei, Taiwan

Clinical Trial Site

Taipei, Taiwan

Clinical Trial Site

Taoyuan City, Taiwan

View Full Details on ClinicalTrials.gov

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NCT07223203