Study of the Reproducibility of the French Version of the Modified SMAFRS Scale
Institut de Myologie, France
60 participants
Jul 18, 2025
OBSERVATIONAL
Conditions
Summary
The goal of this observational study is to evaluate the test-retest reliability of the French version of the mSMAFRS in adult patients with SMA. The main question\[s\] is to answer if: * ICC is a good estimate of test-retest reliability? * mSMAFRS-F correlate with other outcome measures? Participants will simply answer a french version of the SMA-FRS questionnaire during their routine follow-up visit then again fifteen days later.
Eligibility
Inclusion Criteria5
- Age ≥ 18 years
- Genetically confirmed SMA
- Able to comply with all protocol requirements (no significant cognitive impairment)
- French-speaking
- Affiliated or beneficiary of a social security scheme
Exclusion Criteria5
- Persons subject to a legal protection measure
- Subjects unable to complete the French version of the questionnaire mSMAFRS-Fbecause of lack of French fluency
- Subjects unable to complete the French version of the questionnaire mSMAFRS-Fbecause of cognitive impairment
- Inability to comply with protocol requirements
- Any medical and social conditions that could interfere with the study under theappreciation of the medical coordinator
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Interventions
Patients will answer the french mSMA-FRS during their introduction to treatment or treatment follow-up visit, then again, fifteen days after this visit.
Locations(1)
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NCT07321990