RecruitingNCT07358078

DemonsTTRate: A Global, Observational, Multicenter, Long-term Study of Patients With ATTR-CM in a Real-World Setting

DemonsTTRate: A Global, Observational, Multicenter, Long-term Study of Patients With Transthyretin-Mediated Amyloidosis With Cardiomyopathy in a Real-World Setting


Sponsor

Alnylam Pharmaceuticals

Enrollment

2,000 participants

Start Date

Jan 9, 2026

Study Type

OBSERVATIONAL

Conditions

Summary

The purpose of this study is to: * Describe the clinical characteristics of adult patients with transthyretin-mediated amyloidosis with cardiomyopathy (ATTR-CM) treated with vutrisiran in routine clinical care * Describe treatment patterns of adult patients with ATTR-CM treated with vutrisiran in routine clinical care * Assess health-related quality of life (HRQOL) in adult patients with ATTR-CM treated with vutrisiran in routine clinical care * Assess healthcare resource use (HCRU) in adult patients with ATTR-CM treated with vutrisiran in routine clinical care Compare the long-term effectiveness of vutrisiran versus other approved ATTR-CM treatments in routine clinical care


Eligibility

Min Age: 18 Years

Inclusion Criteria2

  • Has a diagnosis of ATTR-CM
  • Is initiating treatment with vutrisiran or another approved ATTR-CM therapy

Exclusion Criteria1

  • Is enrolled in an interventional clinical trial

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Locations(3)

Clinical Trial Site

Naples, Florida, United States

Clinical Trial Site

New Brunswick, New Jersey, United States

Clinical Trial Site

Memphis, Tennessee, United States

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NCT07358078


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