AGS Clinical Trials in Washington D.C., District of Columbia
3 recruitingWashington D.C., District of Columbia
Showing 1–3 of 3 trials
Recruiting
The Myelin Disorders Biorepository Project
AdrenoleukodystrophyCockayne SyndromeRefsum Disease+63 more
Children's Hospital of Philadelphia12,000 enrolled23 locationsNCT03047369
Recruiting
Hepatic Histopathology in Urea Cycle Disorders
Urea Cycle DisorderOrnithine Transcarbamylase DeficiencyCitrullinemia 1+7 more
Baylor College of Medicine70 enrolled2 locationsNCT04908319
Recruiting
Orphan Europe Carbaglu® Surveillance Protocol
N-acetylglutamate Synthase (NAGS) Deficiency
Nicholas Ah Mew30 enrolled3 locationsNCT03409003