Angelman Syndrome Clinical Trials in Philadelphia, Pennsylvania
2 recruitingPhiladelphia, Pennsylvania
Showing 1–2 of 2 trials
Recruiting
Phase 3
REVEAL: A Phase 3 Study of ION582 in Angelman Syndrome
Angelman Syndrome
Ionis Pharmaceuticals, Inc.158 enrolled38 locationsNCT06914609
Recruiting
Phase 2
A Safety and Efficacy Study of GTX-102 in Subjects With Deletion- or Nondeletion-type Angelman Syndrome (AS)
Angelman Syndrome
Ultragenyx Pharmaceutical Inc60 enrolled22 locationsNCT07157254