Angelman Syndrome Clinical Trials in San Diego, California
3 recruitingSan Diego, California
Showing 1–3 of 3 trials
Recruiting
Phase 3
REVEAL: A Phase 3 Study of ION582 in Angelman Syndrome
Angelman Syndrome
Ionis Pharmaceuticals, Inc.158 enrolled38 locationsNCT06914609
Recruiting
Phase 1Phase 2
HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
Angelman Syndrome
Ionis Pharmaceuticals, Inc.70 enrolled11 locationsNCT05127226
Recruiting
Angelman Syndrome Natural History Study
Angelman Syndrome
Boston Children's Hospital300 enrolled11 locationsNCT04507997