Phase 1 Angelman Syndrome Clinical Trials
2 recruitingPhase 1
What is a Phase 1 trial?
Phase 1 trials test a new treatment in a small group of people for the first time. The primary goal is to evaluate safety, determine a safe dosage range, and identify side effects. These studies typically enroll 20 to 80 participants.
Showing 1–2 of 2 trials
Recruiting
Phase 1Phase 2
A Phase 1/2 Study of the Safety and Efficacy of MVX-220 in Angelman Syndrome
Angelman Syndrome
MavriX Bio, LLC12 enrolled3 locationsNCT07181837
Recruiting
Phase 1Phase 2
HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
Angelman Syndrome
Ionis Pharmaceuticals, Inc.70 enrolled11 locationsNCT05127226