Early Phase 1 Bone Marrow Failure Clinical Trials

3 recruitingEarly Phase 1

What is a Early Phase 1 trial?

Early Phase 1 trials are the earliest stage of testing in humans. These small studies focus on how a drug is processed in the body and how it affects the body, often enrolling just a handful of participants to establish initial safety data.

Showing 1–3 of 3 trials

Recruiting

Early Phase 1

Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC

LeukemiaInborn Errors of MetabolismBone Marrow Failure Syndromes+2 more

Children's Hospital of Philadelphia100 enrolled1 locationNCT02356653

Recruiting

Early Phase 1

Fludarabine Based RIC for Bone Marrow Failure Syndromes

Bone Marrow Failure Syndromes

Children's Hospital of Philadelphia25 enrolled1 locationNCT02928991

Recruiting

Early Phase 1

CD7 CAR-T Cell Sequential Allo-HSCT for Non-malignant Blood and Immune System Diseases

Bone Marrow Failure Syndrome

Zhejiang University20 enrolled1 locationNCT06787560