Congenital Myotonic Dystrophy Clinical Trials in Los Angeles, California
2 recruitingLos Angeles, California
Showing 1–2 of 2 trials
Recruiting
DMCRN-02-001: Assessing Pediatric Endpoints in DM1
Congenital Myotonic DystrophyCDM
Virginia Commonwealth University50 enrolled5 locationsNCT05224778
Recruiting
Phase 2Phase 3
Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
Congenital Myotonic Dystrophy
AMO Pharma Limited76 enrolled14 locationsNCT05004129