Congenital Myotonic Dystrophy Clinical Trials in Rochester, New York
3 recruitingRochester, New York
Showing 1–3 of 3 trials
Recruiting
Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
facioscapulohumeral muscular dystrophyMyotonic DystrophyMuscular Dystrophy+6 more
University of Rochester3,000 enrolled1 locationNCT00082108
Recruiting
DMCRN-02-001: Assessing Pediatric Endpoints in DM1
Congenital Myotonic DystrophyCDM
Virginia Commonwealth University50 enrolled5 locationsNCT05224778
Recruiting
Phase 2Phase 3
Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
Congenital Myotonic Dystrophy
AMO Pharma Limited76 enrolled14 locationsNCT05004129