Phase 2 Crigler-Najjar Syndrome Clinical Trials
2 recruitingPhase 2
What is a Phase 2 trial?
Phase 2 trials evaluate whether a treatment works for a specific condition and further assess its safety. These studies typically enroll several hundred participants and provide preliminary data on effectiveness.
Showing 1–2 of 2 trials
Recruiting
Phase 1Phase 2
Gene Therapy for Crigler Najjar Syndrome Type I (AlphaCN)
Crigler-Najjar Syndrome Type I
Federal State Budget Institution Research Center for Obstetrics, Gynecology and Perinatology Ministry of Healthcare5 enrolled2 locationsNCT06641154
Recruiting
Phase 2
Efficacy and Safety of GNT0003 Following Imlifidase Pre-treatment in Severe Crigler-Najjar Syndrome
Crigler-Najjar Syndrome
Genethon3 enrolled1 locationNCT06518005