Phase 1 Cystinosis Clinical Trials
3 recruitingPhase 1
What is a Phase 1 trial?
Phase 1 trials test a new treatment in a small group of people for the first time. The primary goal is to evaluate safety, determine a safe dosage range, and identify side effects. These studies typically enroll 20 to 80 participants.
Showing 1–3 of 3 trials
Recruiting
Phase 1Phase 2
DFT383 in Pediatric Participants With Nephropathic Cystinosis
Nephropathic Cystinosis
Novartis Pharmaceuticals30 enrolled4 locationsNCT06910813
Recruiting
Phase 1Phase 2
PK and PD Study of NPI-001 and Cysteamine Bitartrate
Cystinosis
Nacuity Pharmaceuticals, Inc.12 enrolled1 locationNCT05994534
Recruiting
Phase 1Phase 2
Early Trial of Allogeneic Hematopoietic Stem Cell Transplantation for Patients Who Will Receive a Kidney Transplant From the Same Donor
CystinosisCKD Stage 4FSGS+2 more
Alice Bertaina12 enrolled1 locationNCT05508009