DM1 Clinical Trials in La Jolla, California
2 recruitingLa Jolla, California
Showing 1–2 of 2 trials
Recruiting
Phase 3
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
Myotonic DystrophyDM1Steinert Disease+2 more
Dyne Therapeutics150 enrolled19 locationsNCT07486934
Recruiting
Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
Myotonic Dystrophy 1DM1
Virginia Commonwealth University700 enrolled17 locationsNCT03981575