Phase 1 Dyskeratosis Congenita Clinical Trials

2 recruitingPhase 1

What is a Phase 1 trial?

Phase 1 trials test a new treatment in a small group of people for the first time. The primary goal is to evaluate safety, determine a safe dosage range, and identify side effects. These studies typically enroll 20 to 80 participants.

Showing 1–2 of 2 trials

Recruiting

Phase 1

Quercetin Dyskeratosis Congenita (DC)/Telomere Biology Disorders (TBD)

Dyskeratosis CongenitaTelomere Disease

Children's Hospital Medical Center, Cincinnati12 enrolled1 locationNCT07628972

Recruiting

Phase 1

Nucleoside Therapy in Patients With Telomere Biology Disorders

Dyskeratosis CongenitaTelomere Biology DisordersHoyeraal-Hreidarsson Syndrome+4 more

Suneet Agarwal36 enrolled1 locationNCT06817590