Phase 1 Friedreich Ataxia Clinical Trials
3 recruitingPhase 1
What is a Phase 1 trial?
Phase 1 trials test a new treatment in a small group of people for the first time. The primary goal is to evaluate safety, determine a safe dosage range, and identify side effects. These studies typically enroll 20 to 80 participants.
Showing 1–3 of 3 trials
Recruiting
Phase 1
Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia
CardiomyopathiesFriedreich AtaxiaMyocardial Fibrosis+1 more
Weill Medical College of Cornell University25 enrolled1 locationNCT05302271
Recruiting
Phase 1
A Study to Find Out How BIIB141 (Omaveloxolone) is Processed in the Body and to Learn More About Its Safety in Participants With Friedreich's Ataxia Aged 2 to 15 Years Old
Friedreich Ataxia
Biogen35 enrolled1 locationNCT06054893
Recruiting
Phase 1Phase 2
A Multiple Ascending Dose Study of DT-216P2 in Patients With Friedreich's Ataxia
Friedreich Ataxia
Design Therapeutics, Inc.20 enrolled3 locationsNCT06874010