Phase 2 Genetic Disease Clinical Trials
2 recruitingPhase 2
What is a Phase 2 trial?
Phase 2 trials evaluate whether a treatment works for a specific condition and further assess its safety. These studies typically enroll several hundred participants and provide preliminary data on effectiveness.
Showing 1–2 of 2 trials
Recruiting
Phase 2
Rifampin in CYP24A1-related Hypercalcemia and Hypercalciuria
Genetic DiseaseIdiopathic Infantile Hypercalcaemia - Severe FormHypercalcemia, Idiopathic, of Infancy+3 more
Children's Hospital of Philadelphia60 enrolled1 locationNCT03301038
Recruiting
Phase 2
Unraveling the Impact of Thalidomide at Diverse Doses in Transfusion Dependent Beta Thalassemia
Genetic DiseaseFetal HemoglobinThalassemia Major
National Institute of Blood and Marrow Transplant (NIBMT), Pakistan54 enrolled1 locationNCT06490627